共 55 条
[1]
Gene Therapy for Immunodeficiency Due to Adenosine Deaminase Deficiency.
[J].
Aiuti, Alessandro
;
Cattaneo, Federica
;
Galimberti, Stefania
;
Benninghoff, Ulrike
;
Cassani, Barbara
;
Callegaro, Luciano
;
Scaramuzza, Samantha
;
Andolfi, Grazia
;
Mirolo, Massimiliano
;
Brigida, Immacolata
;
Tabucchi, Antonella
;
Carlucci, Filippo
;
Eibl, Martha
;
Aker, Memet
;
Slavin, Shimon
;
Al-Mousa, Hamoud
;
Al Ghonaium, Abdulaziz
;
Ferster, Alina
;
Duppenthaler, Andrea
;
Notarangelo, Luigi
;
Wintergerst, Uwe
;
Buckley, Rebecca H.
;
Bregni, Marco
;
Marktel, Sarah
;
Valsecchi, Maria Grazia
;
Rossi, Paolo
;
Ciceri, Fabio
;
Miniero, Roberto
;
Bordignon, Claudio
;
Roncarolo, Maria-Grazia
.
NEW ENGLAND JOURNAL OF MEDICINE,
2009, 360 (05)
:447-458

Aiuti, Alessandro
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy
Univ Roma Tor Vergata, Rome, Italy Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy

Cattaneo, Federica
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy
Ist Sci San Raffaele, I-20132 Milan, Italy Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy

论文数: 引用数:
h-index:
机构:

Benninghoff, Ulrike
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy

Cassani, Barbara
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy

Callegaro, Luciano
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy

论文数: 引用数:
h-index:
机构:

Andolfi, Grazia
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy

Mirolo, Massimiliano
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy

Brigida, Immacolata
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy

Tabucchi, Antonella
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Siena, I-53100 Siena, Italy Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy

论文数: 引用数:
h-index:
机构:

Eibl, Martha
论文数: 0 引用数: 0
h-index: 0
机构:
Immunol Tagesklin, Vienna, Austria Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy

Aker, Memet
论文数: 0 引用数: 0
h-index: 0
机构:
Hadassah Univ Hosp, IL-91120 Jerusalem, Israel Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy

Slavin, Shimon
论文数: 0 引用数: 0
h-index: 0
机构:
Hadassah Univ Hosp, IL-91120 Jerusalem, Israel Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy

Al-Mousa, Hamoud
论文数: 0 引用数: 0
h-index: 0
机构:
King Faisal Specialist Hosp & Res Ctr, Riyadh 11211, Saudi Arabia Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy

Al Ghonaium, Abdulaziz
论文数: 0 引用数: 0
h-index: 0
机构:
King Faisal Specialist Hosp & Res Ctr, Riyadh 11211, Saudi Arabia Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy

Ferster, Alina
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Libre Bruxelles, Hop Univ Enfants Reine Fabiola, Brussels, Belgium Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy

Duppenthaler, Andrea
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Childrens Hosp, Bern, Switzerland Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy

Notarangelo, Luigi
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Sch Med, Childrens Hosp, Boston, MA 02115 USA Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy

Wintergerst, Uwe
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Kinderklin Munchen, Munich, Germany Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy

Buckley, Rebecca H.
论文数: 0 引用数: 0
h-index: 0
机构:
Duke Univ, Med Ctr, Durham, NC USA Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy

Bregni, Marco
论文数: 0 引用数: 0
h-index: 0
机构:
Osped San Giuseppe, Milan, Italy Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy

Marktel, Sarah
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy

Valsecchi, Maria Grazia
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Milano Bicocca, Milan, Italy Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy

Rossi, Paolo
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Roma Tor Vergata, Rome, Italy
Childrens Hosp Bambino Gesu, Rome, Italy Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy

Ciceri, Fabio
论文数: 0 引用数: 0
h-index: 0
机构: Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy

Miniero, Roberto
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Turin, Turin, Italy Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy

Bordignon, Claudio
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Vita Salute San Raffaele, Milan, Italy
MolMed, Milan, Italy Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy

Roncarolo, Maria-Grazia
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy
Univ Vita Salute San Raffaele, Milan, Italy Univ Milano Bicocca, HSR TIGET, I-20132 Milan, Italy
[2]
Lentiviral Hematopoietic Stem Cell Gene Therapy Benefits Metachromatic Leukodystrophy
[J].
Biffi, Alessandra
;
Montini, Eugenio
;
Lorioli, Laura
;
Cesani, Martina
;
Fumagalli, Francesca
;
Plati, Tiziana
;
Baldoli, Cristina
;
Martino, Sabata
;
Calabria, Andrea
;
Canale, Sabrina
;
Benedicenti, Fabrizio
;
Vallanti, Giuliana
;
Biasco, Luca
;
Leo, Simone
;
Kabbara, Nabil
;
Zanetti, Gianluigi
;
Rizzo, William B.
;
Mehta, Nalini A. L.
;
Cicalese, Maria Pia
;
Casiraghi, Miriam
;
Boelens, Jaap J.
;
Del Carro, Ubaldo
;
Dow, David J.
;
Schmidt, Manfred
;
Assanelli, Andrea
;
Neduva, Victor
;
Di Serio, Clelia
;
Stupka, Elia
;
Gardner, Jason
;
von Kalle, Christof
;
Bordignon, Claudio
;
Ciceri, Fabio
;
Rovelli, Attilio
;
Roncarolo, Maria Grazia
;
Aiuti, Alessandro
;
Sessa, Maria
;
Naldini, Luigi
.
SCIENCE,
2013, 341 (6148)
:864-U58

Biffi, Alessandra
论文数: 0 引用数: 0
h-index: 0
机构:
Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Montini, Eugenio
论文数: 0 引用数: 0
h-index: 0
机构:
Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Lorioli, Laura
论文数: 0 引用数: 0
h-index: 0
机构:
Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Cesani, Martina
论文数: 0 引用数: 0
h-index: 0
机构:
Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Fumagalli, Francesca
论文数: 0 引用数: 0
h-index: 0
机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Plati, Tiziana
论文数: 0 引用数: 0
h-index: 0
机构:
Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Baldoli, Cristina
论文数: 0 引用数: 0
h-index: 0
机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Martino, Sabata
论文数: 0 引用数: 0
h-index: 0
机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Calabria, Andrea
论文数: 0 引用数: 0
h-index: 0
机构:
Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Canale, Sabrina
论文数: 0 引用数: 0
h-index: 0
机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Benedicenti, Fabrizio
论文数: 0 引用数: 0
h-index: 0
机构:
Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Vallanti, Giuliana
论文数: 0 引用数: 0
h-index: 0
机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Biasco, Luca
论文数: 0 引用数: 0
h-index: 0
机构:
Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Leo, Simone
论文数: 0 引用数: 0
h-index: 0
机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Kabbara, Nabil
论文数: 0 引用数: 0
h-index: 0
机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Zanetti, Gianluigi
论文数: 0 引用数: 0
h-index: 0
机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Rizzo, William B.
论文数: 0 引用数: 0
h-index: 0
机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Mehta, Nalini A. L.
论文数: 0 引用数: 0
h-index: 0
机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Cicalese, Maria Pia
论文数: 0 引用数: 0
h-index: 0
机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Casiraghi, Miriam
论文数: 0 引用数: 0
h-index: 0
机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Boelens, Jaap J.
论文数: 0 引用数: 0
h-index: 0
机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Del Carro, Ubaldo
论文数: 0 引用数: 0
h-index: 0
机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Dow, David J.
论文数: 0 引用数: 0
h-index: 0
机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Schmidt, Manfred
论文数: 0 引用数: 0
h-index: 0
机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Assanelli, Andrea
论文数: 0 引用数: 0
h-index: 0
机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Neduva, Victor
论文数: 0 引用数: 0
h-index: 0
机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Di Serio, Clelia
论文数: 0 引用数: 0
h-index: 0
机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Stupka, Elia
论文数: 0 引用数: 0
h-index: 0
机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Gardner, Jason
论文数: 0 引用数: 0
h-index: 0
机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

von Kalle, Christof
论文数: 0 引用数: 0
h-index: 0
机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Bordignon, Claudio
论文数: 0 引用数: 0
h-index: 0
机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Ciceri, Fabio
论文数: 0 引用数: 0
h-index: 0
机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Rovelli, Attilio
论文数: 0 引用数: 0
h-index: 0
机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Roncarolo, Maria Grazia
论文数: 0 引用数: 0
h-index: 0
机构:
Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Aiuti, Alessandro
论文数: 0 引用数: 0
h-index: 0
机构:
Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Sessa, Maria
论文数: 0 引用数: 0
h-index: 0
机构: Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy

Naldini, Luigi
论文数: 0 引用数: 0
h-index: 0
机构:
Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy TIGET, I-20132 Milan, Italy
[3]
Broad T-Cell Receptor Repertoire in T-Lymphocytes Derived from Human Induced Pluripotent Stem Cells
[J].
Chang, Chia-Wei
;
Lai, Yi-Shin
;
Lamb, Lawrence S., Jr.
;
Townes, Tim M.
.
PLOS ONE,
2014, 9 (05)

Chang, Chia-Wei
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Alabama Birmingham, Sch Med, Dept Biochem & Mol Genet, Birmingham, AL 35205 USA
Univ Alabama Birmingham, Sch Dent, Dept Biochem & Mol Genet, Birmingham, AL 35294 USA
Univ Alabama Birmingham, Sch Med, UAB Stem Cell Inst, Birmingham, AL USA
Univ Alabama Birmingham, Sch Dent, UAB Stem Cell Inst, Birmingham, AL 35294 USA Univ Alabama Birmingham, Sch Med, Dept Biochem & Mol Genet, Birmingham, AL 35205 USA

Lai, Yi-Shin
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Alabama Birmingham, Sch Med, Dept Biochem & Mol Genet, Birmingham, AL 35205 USA
Univ Alabama Birmingham, Sch Dent, Dept Biochem & Mol Genet, Birmingham, AL 35294 USA
Univ Alabama Birmingham, Sch Med, UAB Stem Cell Inst, Birmingham, AL USA
Univ Alabama Birmingham, Sch Dent, UAB Stem Cell Inst, Birmingham, AL 35294 USA Univ Alabama Birmingham, Sch Med, Dept Biochem & Mol Genet, Birmingham, AL 35205 USA

Lamb, Lawrence S., Jr.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Alabama Birmingham, Sch Med, Dept Med, Birmingham, AL USA
Univ Alabama Birmingham, Sch Dent, Dept Med, Birmingham, AL 35294 USA
Univ Alabama Birmingham, Sch Med, Cell Therapy Lab, Birmingham, AL USA
Univ Alabama Birmingham, Sch Dent, Cell Therapy Lab, Birmingham, AL 35294 USA Univ Alabama Birmingham, Sch Med, Dept Biochem & Mol Genet, Birmingham, AL 35205 USA

Townes, Tim M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Alabama Birmingham, Sch Med, Dept Biochem & Mol Genet, Birmingham, AL 35205 USA
Univ Alabama Birmingham, Sch Dent, Dept Biochem & Mol Genet, Birmingham, AL 35294 USA
Univ Alabama Birmingham, Sch Med, UAB Stem Cell Inst, Birmingham, AL USA
Univ Alabama Birmingham, Sch Dent, UAB Stem Cell Inst, Birmingham, AL 35294 USA Univ Alabama Birmingham, Sch Med, Dept Biochem & Mol Genet, Birmingham, AL 35205 USA
[4]
Polycistronic Lentiviral Vector for "Hit and Run'' Reprogramming of Adult Skin Fibroblasts to Induced Pluripotent Stem Cells
[J].
Chang, Chia-Wei
;
Lai, Yi-Shin
;
Pawlik, Kevin M.
;
Liu, Kaimao
;
Sun, Chiao-Wang
;
Li, Chao
;
Schoeb, Trenton R.
;
Townes, Tim M.
.
STEM CELLS,
2009, 27 (05)
:1042-1049

Chang, Chia-Wei
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Alabama Birmingham, Sch Med, Dept Biochem & Mol Genet, Birmingham, AL USA
Univ Alabama Birmingham, Sch Dent, Dept Biochem & Mol Genet, Birmingham, AL 35294 USA Univ Alabama Birmingham, Sch Med, Dept Biochem & Mol Genet, Birmingham, AL USA

Lai, Yi-Shin
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Alabama Birmingham, Sch Med, Dept Biochem & Mol Genet, Birmingham, AL USA
Univ Alabama Birmingham, Sch Dent, Dept Biochem & Mol Genet, Birmingham, AL 35294 USA Univ Alabama Birmingham, Sch Med, Dept Biochem & Mol Genet, Birmingham, AL USA

Pawlik, Kevin M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Alabama Birmingham, Sch Med, Dept Biochem & Mol Genet, Birmingham, AL USA
Univ Alabama Birmingham, Sch Dent, Dept Biochem & Mol Genet, Birmingham, AL 35294 USA Univ Alabama Birmingham, Sch Med, Dept Biochem & Mol Genet, Birmingham, AL USA

Liu, Kaimao
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Alabama Birmingham, Sch Med, Dept Biochem & Mol Genet, Birmingham, AL USA
Univ Alabama Birmingham, Sch Dent, Dept Biochem & Mol Genet, Birmingham, AL 35294 USA Univ Alabama Birmingham, Sch Med, Dept Biochem & Mol Genet, Birmingham, AL USA

Sun, Chiao-Wang
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Alabama Birmingham, Sch Med, Dept Biochem & Mol Genet, Birmingham, AL USA
Univ Alabama Birmingham, Sch Dent, Dept Biochem & Mol Genet, Birmingham, AL 35294 USA Univ Alabama Birmingham, Sch Med, Dept Biochem & Mol Genet, Birmingham, AL USA

Li, Chao
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Alabama Birmingham, Sch Med, Dept Biochem & Mol Genet, Birmingham, AL USA
Univ Alabama Birmingham, Sch Dent, Dept Biochem & Mol Genet, Birmingham, AL 35294 USA Univ Alabama Birmingham, Sch Med, Dept Biochem & Mol Genet, Birmingham, AL USA

Schoeb, Trenton R.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Alabama Birmingham, Sch Med, Dept Genet, Birmingham, AL USA
Univ Alabama Birmingham, Sch Dent, Dept Genet, Birmingham, AL 35294 USA Univ Alabama Birmingham, Sch Med, Dept Biochem & Mol Genet, Birmingham, AL USA

Townes, Tim M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Alabama Birmingham, Sch Med, Dept Biochem & Mol Genet, Birmingham, AL USA
Univ Alabama Birmingham, Sch Dent, Dept Biochem & Mol Genet, Birmingham, AL 35294 USA Univ Alabama Birmingham, Sch Med, Dept Biochem & Mol Genet, Birmingham, AL USA
[5]
Multiplex Genome Engineering Using CRISPR/Cas Systems
[J].
Cong, Le
;
Ran, F. Ann
;
Cox, David
;
Lin, Shuailiang
;
Barretto, Robert
;
Habib, Naomi
;
Hsu, Patrick D.
;
Wu, Xuebing
;
Jiang, Wenyan
;
Marraffini, Luciano A.
;
Zhang, Feng
.
SCIENCE,
2013, 339 (6121)
:819-823

Cong, Le
论文数: 0 引用数: 0
h-index: 0
机构:
Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA
MIT, Dept Biol Engn, Dept Brain & Cognit Sci, McGovern Inst Brain Res, Cambridge, MA 02139 USA
Harvard Univ, Sch Med, Program Biol & Biomed Sci, Boston, MA 02115 USA Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA

Ran, F. Ann
论文数: 0 引用数: 0
h-index: 0
机构:
Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA
MIT, Dept Biol Engn, Dept Brain & Cognit Sci, McGovern Inst Brain Res, Cambridge, MA 02139 USA
Harvard Univ, Dept Mol & Cellular Biol, Cambridge, MA 02138 USA Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA

论文数: 引用数:
h-index:
机构:

Lin, Shuailiang
论文数: 0 引用数: 0
h-index: 0
机构:
Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA
MIT, Dept Biol Engn, Dept Brain & Cognit Sci, McGovern Inst Brain Res, Cambridge, MA 02139 USA
Tsinghua Univ, Sch Life Sci, Beijing 100084, Peoples R China Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA

Barretto, Robert
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Coll Phys & Surg, Dept Biochem & Mol Biophys, New York, NY 10032 USA Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA

Habib, Naomi
论文数: 0 引用数: 0
h-index: 0
机构:
Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA
MIT, Dept Biol Engn, Dept Brain & Cognit Sci, McGovern Inst Brain Res, Cambridge, MA 02139 USA Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA

Hsu, Patrick D.
论文数: 0 引用数: 0
h-index: 0
机构:
Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA
MIT, Dept Biol Engn, Dept Brain & Cognit Sci, McGovern Inst Brain Res, Cambridge, MA 02139 USA
Harvard Univ, Dept Mol & Cellular Biol, Cambridge, MA 02138 USA Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA

Wu, Xuebing
论文数: 0 引用数: 0
h-index: 0
机构:
MIT, Computat & Syst Biol Grad Program, Cambridge, MA 02139 USA
MIT, Koch Inst Integrat Canc Res, Cambridge, MA 02139 USA Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA

Jiang, Wenyan
论文数: 0 引用数: 0
h-index: 0
机构:
Rockefeller Univ, Bacteriol Lab, New York, NY 10065 USA Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA

Marraffini, Luciano A.
论文数: 0 引用数: 0
h-index: 0
机构:
Rockefeller Univ, Bacteriol Lab, New York, NY 10065 USA Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA

Zhang, Feng
论文数: 0 引用数: 0
h-index: 0
机构:
Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA
MIT, Dept Biol Engn, Dept Brain & Cognit Sci, McGovern Inst Brain Res, Cambridge, MA 02139 USA Broad Inst MIT & Harvard, Cambridge Ctr 7, Cambridge, MA 02142 USA
[6]
Identifying a High Fraction of the Human Genome to be under Selective Constraint Using GERP plus
[J].
Davydov, Eugene V.
;
Goode, David L.
;
Sirota, Marina
;
Cooper, Gregory M.
;
Sidow, Arend
;
Batzoglou, Serafim
.
PLOS COMPUTATIONAL BIOLOGY,
2010, 6 (12)

Davydov, Eugene V.
论文数: 0 引用数: 0
h-index: 0
机构:
Stanford Univ, Dept Comp Sci, Stanford, CA 94305 USA Stanford Univ, Dept Comp Sci, Stanford, CA 94305 USA

Goode, David L.
论文数: 0 引用数: 0
h-index: 0
机构:
Stanford Univ, Dept Genet, Sch Med, Stanford, CA 94305 USA Stanford Univ, Dept Comp Sci, Stanford, CA 94305 USA

论文数: 引用数:
h-index:
机构:

Cooper, Gregory M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Washington, Dept Genome Sci, Seattle, WA 98195 USA
Univ Washington, Howard Hughes Med Inst, Seattle, WA 98195 USA Stanford Univ, Dept Comp Sci, Stanford, CA 94305 USA

Sidow, Arend
论文数: 0 引用数: 0
h-index: 0
机构:
Stanford Univ, Dept Genet, Sch Med, Stanford, CA 94305 USA
Stanford Univ, Sch Med, Dept Pathol, Stanford, CA 94305 USA Stanford Univ, Dept Comp Sci, Stanford, CA 94305 USA

Batzoglou, Serafim
论文数: 0 引用数: 0
h-index: 0
机构:
Stanford Univ, Dept Comp Sci, Stanford, CA 94305 USA Stanford Univ, Dept Comp Sci, Stanford, CA 94305 USA
[7]
T-cell potential and development in vitro:: the OP9-DL1 approach
[J].
de Pooter, Rene
;
Zuniga-Pflucker, Juan Carlos
.
CURRENT OPINION IN IMMUNOLOGY,
2007, 19 (02)
:163-168

de Pooter, Rene
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Toronto, Dept Immunol, Sunnybrook Res Inst, Toronto, ON M4N 3M5, Canada Univ Toronto, Dept Immunol, Sunnybrook Res Inst, Toronto, ON M4N 3M5, Canada

Zuniga-Pflucker, Juan Carlos
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Toronto, Dept Immunol, Sunnybrook Res Inst, Toronto, ON M4N 3M5, Canada Univ Toronto, Dept Immunol, Sunnybrook Res Inst, Toronto, ON M4N 3M5, Canada
[8]
Comparative and Functional Evaluation of In Vitro Generated to Ex Vivo CD8 T Cells
[J].
Dervovic, Dzana D.
;
Ciofani, Maria
;
Kianizad, Korosh
;
Zuniga-Pfluecker, Juan Carlos
.
JOURNAL OF IMMUNOLOGY,
2012, 189 (07)
:3411-3420

Dervovic, Dzana D.
论文数: 0 引用数: 0
h-index: 0
机构:
Sunnybrook Res Inst, Toronto, ON M4N 3M5, Canada
Univ Toronto, Dept Immunol, Toronto, ON M4N 3M5, Canada Sunnybrook Res Inst, Toronto, ON M4N 3M5, Canada

Ciofani, Maria
论文数: 0 引用数: 0
h-index: 0
机构:
Sunnybrook Res Inst, Toronto, ON M4N 3M5, Canada
Univ Toronto, Dept Immunol, Toronto, ON M4N 3M5, Canada Sunnybrook Res Inst, Toronto, ON M4N 3M5, Canada

Kianizad, Korosh
论文数: 0 引用数: 0
h-index: 0
机构:
Sunnybrook Res Inst, Toronto, ON M4N 3M5, Canada
Univ Toronto, Dept Immunol, Toronto, ON M4N 3M5, Canada Sunnybrook Res Inst, Toronto, ON M4N 3M5, Canada

Zuniga-Pfluecker, Juan Carlos
论文数: 0 引用数: 0
h-index: 0
机构:
Sunnybrook Res Inst, Toronto, ON M4N 3M5, Canada
Univ Toronto, Dept Immunol, Toronto, ON M4N 3M5, Canada Sunnybrook Res Inst, Toronto, ON M4N 3M5, Canada
[9]
Eynon EE, 1999, J IMMUNOL, V162, P1448
[10]
Update on gene therapy for adenosine deaminase-deficient severe combined immunodeficiency
[J].
Ferrua, Francesca
;
Brigida, Immacolata
;
Aiuti, Alessandro
.
CURRENT OPINION IN ALLERGY AND CLINICAL IMMUNOLOGY,
2010, 10 (06)
:551-556

Ferrua, Francesca
论文数: 0 引用数: 0
h-index: 0
机构:
San Raffaele Telethon Inst Gene Therapy, I-20132 Milan, Italy
Ist Sci San Raffaele, Pediat Immunohematol & Bone Marrow Transplantat U, I-20132 Milan, Italy San Raffaele Telethon Inst Gene Therapy, I-20132 Milan, Italy

Brigida, Immacolata
论文数: 0 引用数: 0
h-index: 0
机构:
San Raffaele Telethon Inst Gene Therapy, I-20132 Milan, Italy San Raffaele Telethon Inst Gene Therapy, I-20132 Milan, Italy

Aiuti, Alessandro
论文数: 0 引用数: 0
h-index: 0
机构:
San Raffaele Telethon Inst Gene Therapy, I-20132 Milan, Italy
Ist Sci San Raffaele, Pediat Immunohematol & Bone Marrow Transplantat U, I-20132 Milan, Italy
Univ Roma Tor Vergata, Childrens Hosp Bambino Gesu, Dept Pediat, Rome, Italy San Raffaele Telethon Inst Gene Therapy, I-20132 Milan, Italy