Persistence of the treatment effect of idebenone in Leber's hereditary optic neuropathy

被引:136
作者
Klopstock, T. [1 ]
Metz, G. [2 ]
Yu-Wai-Man, P. [3 ,4 ,5 ]
Buechner, B. [1 ]
Gallenmueller, C. [1 ]
Bailie, M. [3 ,4 ,5 ]
Nwali, N. [3 ,4 ,5 ]
Griffiths, P. G. [3 ,4 ,5 ]
von Livonius, B. [6 ]
Reznicek, L. [6 ]
Rouleau, J. [7 ]
Coppard, N. [2 ]
Meier, T. [2 ]
Chinnery, P. F. [3 ,4 ,5 ]
机构
[1] Univ Munich, Friedrich Baur Inst, Dept Neurol, D-80336 Munich, Germany
[2] Santhera Pharmaceut, CH-4410 Liestal, Switzerland
[3] Newcastle Upon Tyne Fdn Hosp NHS Fdn Trust, Dept Neurol, Newcastle Upon Tyne NE1 4LP, Tyne & Wear, England
[4] Newcastle Upon Tyne Fdn Hosp NHS Fdn Trust, Dept Ophthalmol, Newcastle Upon Tyne NE1 4LP, Tyne & Wear, England
[5] Newcastle Univ, Inst Med Genet, Newcastle Upon Tyne NE1 3BZ, Tyne & Wear, England
[6] Univ Munich, Dept Ophthalmol, D-80336 Munich, Germany
[7] CHUM, Dept Ophthalmol, Montreal, PQ H2L 4M1, Canada
基金
英国医学研究理事会; 英国惠康基金;
关键词
PATIENT;
D O I
10.1093/brain/aws279
中图分类号
R74 [神经病学与精神病学];
学科分类号
摘要
引用
收藏
页数:5
相关论文
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