[1] Harvard Med Sch, Brigham & Womens Hosp, Dept Neurol, Boston, MA 02115 USA
[2] Leiden Univ, Med Ctr, Dept Neurol, Leiden, Netherlands
[3] Pierre & Marie Curie Univ, Pitie Salpetriere Hosp, Dept Internal Med, Paris, France
[4] Murdoch Univ, IIID, Fiona Stanley Hosp, Perth, WA, Australia
[5] Notre Dame Univ, Perth, WA, Australia
[6] Univ Manchester, Ctr Musculoskeletal Res, NIHR Manchester Musculoskeletal Biomed Res Unit, Manchester, Lancs, England
[7] Novartis Pharmaceut, E Hanover, NJ USA
[8] Novartis Pharma AG, Basel, Switzerland
[9] UCL, Inst Neurol, MRC, Ctr Neuromuscular Dis, London, England