共 50 条
[21]
Turning point of organoid transplantation: first-in-human trial of iPSC-derived retinal organoid grafting in patients with retinitis pigmentosa
[J].
Zhang, Chang-Jun
;
Jin, Zi-Bing
.
SCIENCE CHINA-LIFE SCIENCES,
2024, 67 (05)
:1082-1084

Zhang, Chang-Jun
论文数: 0 引用数: 0
h-index: 0
机构:
Capital Med Univ, Beijing Tongren Hosp, Beijing Inst Ophthalmol, Beijing 100730, Peoples R China Capital Med Univ, Beijing Tongren Hosp, Beijing Inst Ophthalmol, Beijing 100730, Peoples R China

Jin, Zi-Bing
论文数: 0 引用数: 0
h-index: 0
机构:
Capital Med Univ, Beijing Tongren Hosp, Beijing Inst Ophthalmol, Beijing 100730, Peoples R China Capital Med Univ, Beijing Tongren Hosp, Beijing Inst Ophthalmol, Beijing 100730, Peoples R China
[22]
First-in-Human Intravenous Seprehvir in Young Cancer Patients: A Phase 1 Clinical Trial
[J].
Streby, Keri A.
;
Currier, Mark A.
;
Triplet, Melinda
;
Ott, Kristy
;
Dishman, Devon J.
;
Vaughan, Michele R.
;
Ranalli, Mark A.
;
Setty, Bhuvana
;
Skeens, Micah A.
;
Whiteside, Stacy
;
Yeager, Nicholas D.
;
Haworth, Kellie B.
;
Simpson, Kathleen
;
Conner, Joe
;
Cripe, Timothy P.
.
MOLECULAR THERAPY,
2019, 27 (11)
:1930-1938

Streby, Keri A.
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Nationwide Childrens Hosp, Div Hematol Oncol BMT, 700 Childrens Dr, Columbus, OH 43205 USA
Nationwide Childrens Hosp Res Inst, Ctr Childhood Canc & Blood Disorders, Columbus, OH 43205 USA Ohio State Univ, Nationwide Childrens Hosp, Div Hematol Oncol BMT, 700 Childrens Dr, Columbus, OH 43205 USA

Currier, Mark A.
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp Res Inst, Ctr Childhood Canc & Blood Disorders, Columbus, OH 43205 USA Ohio State Univ, Nationwide Childrens Hosp, Div Hematol Oncol BMT, 700 Childrens Dr, Columbus, OH 43205 USA

Triplet, Melinda
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Nationwide Childrens Hosp, Div Hematol Oncol BMT, 700 Childrens Dr, Columbus, OH 43205 USA Ohio State Univ, Nationwide Childrens Hosp, Div Hematol Oncol BMT, 700 Childrens Dr, Columbus, OH 43205 USA

Ott, Kristy
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Nationwide Childrens Hosp, Div Hematol Oncol BMT, 700 Childrens Dr, Columbus, OH 43205 USA Ohio State Univ, Nationwide Childrens Hosp, Div Hematol Oncol BMT, 700 Childrens Dr, Columbus, OH 43205 USA

Dishman, Devon J.
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Nationwide Childrens Hosp, Div Hematol Oncol BMT, 700 Childrens Dr, Columbus, OH 43205 USA Ohio State Univ, Nationwide Childrens Hosp, Div Hematol Oncol BMT, 700 Childrens Dr, Columbus, OH 43205 USA

Vaughan, Michele R.
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Nationwide Childrens Hosp, Div Hematol Oncol BMT, 700 Childrens Dr, Columbus, OH 43205 USA Ohio State Univ, Nationwide Childrens Hosp, Div Hematol Oncol BMT, 700 Childrens Dr, Columbus, OH 43205 USA

Ranalli, Mark A.
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Nationwide Childrens Hosp, Div Hematol Oncol BMT, 700 Childrens Dr, Columbus, OH 43205 USA Ohio State Univ, Nationwide Childrens Hosp, Div Hematol Oncol BMT, 700 Childrens Dr, Columbus, OH 43205 USA

Setty, Bhuvana
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Nationwide Childrens Hosp, Div Hematol Oncol BMT, 700 Childrens Dr, Columbus, OH 43205 USA Ohio State Univ, Nationwide Childrens Hosp, Div Hematol Oncol BMT, 700 Childrens Dr, Columbus, OH 43205 USA

Skeens, Micah A.
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Nationwide Childrens Hosp, Div Hematol Oncol BMT, 700 Childrens Dr, Columbus, OH 43205 USA Ohio State Univ, Nationwide Childrens Hosp, Div Hematol Oncol BMT, 700 Childrens Dr, Columbus, OH 43205 USA

Whiteside, Stacy
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Nationwide Childrens Hosp, Div Hematol Oncol BMT, 700 Childrens Dr, Columbus, OH 43205 USA Ohio State Univ, Nationwide Childrens Hosp, Div Hematol Oncol BMT, 700 Childrens Dr, Columbus, OH 43205 USA

Yeager, Nicholas D.
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Nationwide Childrens Hosp, Div Hematol Oncol BMT, 700 Childrens Dr, Columbus, OH 43205 USA Ohio State Univ, Nationwide Childrens Hosp, Div Hematol Oncol BMT, 700 Childrens Dr, Columbus, OH 43205 USA

Haworth, Kellie B.
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Nationwide Childrens Hosp, Div Hematol Oncol BMT, 700 Childrens Dr, Columbus, OH 43205 USA Ohio State Univ, Nationwide Childrens Hosp, Div Hematol Oncol BMT, 700 Childrens Dr, Columbus, OH 43205 USA

Simpson, Kathleen
论文数: 0 引用数: 0
h-index: 0
机构:
Virttu Biol Ltd, Biocity ML1 5UH, Newhouse, Scotland Ohio State Univ, Nationwide Childrens Hosp, Div Hematol Oncol BMT, 700 Childrens Dr, Columbus, OH 43205 USA

Conner, Joe
论文数: 0 引用数: 0
h-index: 0
机构:
Virttu Biol Ltd, Biocity ML1 5UH, Newhouse, Scotland Ohio State Univ, Nationwide Childrens Hosp, Div Hematol Oncol BMT, 700 Childrens Dr, Columbus, OH 43205 USA

Cripe, Timothy P.
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Nationwide Childrens Hosp, Div Hematol Oncol BMT, 700 Childrens Dr, Columbus, OH 43205 USA
Nationwide Childrens Hosp Res Inst, Ctr Childhood Canc & Blood Disorders, Columbus, OH 43205 USA Ohio State Univ, Nationwide Childrens Hosp, Div Hematol Oncol BMT, 700 Childrens Dr, Columbus, OH 43205 USA
[23]
First-in-human intrathecal gene transfer study for giant axonal neuropathy: Three-year interim evaluation of safety and efficacy
[J].
Bharucha-Goebel, D.
;
Saade, D.
;
Jain, M.
;
Norato, G.
;
Rybin, D.
;
Cheung, K.
;
Waite, M.
;
Paredes, E.
;
Foley, A.
;
Lehky, T.
;
Hu, Y.
;
Del Hoyo, R. Calcedo
;
Chichester, J.
;
Jacobson, S.
;
Nath, A.
;
Charnas, L.
;
Samulski, R.
;
Gray, S.
;
Bonnemann, C.
.
NEUROMUSCULAR DISORDERS,
2020, 30
:S78-S78

Bharucha-Goebel, D.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA
Childrens Natl Hosp, Bethesda, MD USA NIH, Bldg 10, Bethesda, MD 20892 USA

Saade, D.
论文数: 0 引用数: 0
h-index: 0
机构:
NINDS, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Jain, M.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Norato, G.
论文数: 0 引用数: 0
h-index: 0
机构:
NINDS, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Rybin, D.
论文数: 0 引用数: 0
h-index: 0
机构:
Pfizer Inc, Boston, MA USA NIH, Bldg 10, Bethesda, MD 20892 USA

Cheung, K.
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, New York, NY USA NIH, Bldg 10, Bethesda, MD 20892 USA

Waite, M.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Paredes, E.
论文数: 0 引用数: 0
h-index: 0
机构:
NINDS, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Foley, A.
论文数: 0 引用数: 0
h-index: 0
机构:
NINDS, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Lehky, T.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Hu, Y.
论文数: 0 引用数: 0
h-index: 0
机构:
NINDS, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Del Hoyo, R. Calcedo
论文数: 0 引用数: 0
h-index: 0
机构:
Affinia Therapeut, Boston, MA USA NIH, Bldg 10, Bethesda, MD 20892 USA

Chichester, J.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, Philadelphia, PA 19104 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Jacobson, S.
论文数: 0 引用数: 0
h-index: 0
机构:
NINDS, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Nath, A.
论文数: 0 引用数: 0
h-index: 0
机构:
NINDS, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Charnas, L.
论文数: 0 引用数: 0
h-index: 0
机构:
Pfizer Inc, Cambridge, MA USA NIH, Bldg 10, Bethesda, MD 20892 USA

Samulski, R.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ N Carolina, Chapel Hill, NC 27515 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Gray, S.
论文数: 0 引用数: 0
h-index: 0
机构:
UT Southwestern, Dallas, TX USA NIH, Bldg 10, Bethesda, MD 20892 USA

Bonnemann, C.
论文数: 0 引用数: 0
h-index: 0
机构:
NINDS, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA
[24]
First-in-human intrathecal gene transfer study for giant axonal neuropathy: review of safety, immunologic responses and interim analysis of efficacy
[J].
Saade, D.
;
Bharucha-Goebel, D.
;
Jain, M.
;
Waite, M.
;
Norato, G.
;
Cheung, K.
;
Foley, A. R.
;
Soldatos, A.
;
Rybin, D.
;
Lehky, T.
;
Ying, H.
;
Whitehead, M.
;
Del Hoyo, R. Calcedo
;
Jacobson, S.
;
Leibovitch, E.
;
Nath, A.
;
Grieger, J.
;
Samulski, R.
;
Gray, S.
;
Bonnemann, C.
.
NEUROMUSCULAR DISORDERS,
2018, 28
:S91-S92

Saade, D.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Bharucha-Goebel, D.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Jain, M.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Waite, M.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Norato, G.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Cheung, K.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Foley, A. R.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Soldatos, A.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Rybin, D.
论文数: 0 引用数: 0
h-index: 0
机构:
Pfizer, Cambridge, MA USA NIH, Bldg 10, Bethesda, MD 20892 USA

Lehky, T.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Ying, H.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Whitehead, M.
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Natl Hlth, Washington, DC USA NIH, Bldg 10, Bethesda, MD 20892 USA

Del Hoyo, R. Calcedo
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, Philadelphia, PA 19104 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Jacobson, S.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Leibovitch, E.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Nath, A.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Grieger, J.
论文数: 0 引用数: 0
h-index: 0
机构:
Asklepios Biopharmaceut, Chapel Hill, NC USA NIH, Bldg 10, Bethesda, MD 20892 USA

Samulski, R.
论文数: 0 引用数: 0
h-index: 0
机构:
Bamboo Therapeut, Chapel Hill, NC USA NIH, Bldg 10, Bethesda, MD 20892 USA

Gray, S.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Dallas, TX 75390 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Bonnemann, C.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA
[25]
First-in-human clinical trial of transplantation of iPSC-derived NS/PCs in subacute complete spinal cord injury: Study protocol
[J].
Sugai, Keiko
;
Sumida, Miho
;
Shofuda, Tomoko
;
Yamaguchi, Ryo
;
Tamura, Takashi
;
Kohzuki, Tsuneo
;
Abe, Takayuki
;
Shibata, Reo
;
Kamata, Yasuhiro
;
Ito, Shuhei
;
Okubo, Toshiki
;
Tsuji, Osahiko
;
Nori, Satoshi
;
Nagoshi, Narihito
;
Yamanaka, Shinya
;
Kawamata, Shin
;
Kanemura, Yonehiro
;
Nakamura, Masaya
;
Okano, Hideyuki
.
REGENERATIVE THERAPY,
2021, 18
:321-333

Sugai, Keiko
论文数: 0 引用数: 0
h-index: 0
机构:
Keio Univ, Dept Orthopaed Surg, Sch Med, Tokyo, Japan Keio Univ, Dept Orthopaed Surg, Sch Med, Tokyo, Japan

Sumida, Miho
论文数: 0 引用数: 0
h-index: 0
机构:
Natl Hosp Org Osaka Natl Hosp, Dept Biomed Res & Innovat, Inst Clin Res, Osaka, Japan Keio Univ, Dept Orthopaed Surg, Sch Med, Tokyo, Japan

Shofuda, Tomoko
论文数: 0 引用数: 0
h-index: 0
机构:
Natl Hosp Org Osaka Natl Hosp, Dept Biomed Res & Innovat, Inst Clin Res, Osaka, Japan Keio Univ, Dept Orthopaed Surg, Sch Med, Tokyo, Japan

Yamaguchi, Ryo
论文数: 0 引用数: 0
h-index: 0
机构:
Keio Univ, Dept Orthopaed Surg, Sch Med, Tokyo, Japan
Sumitomo Dainippon Pharma Co Ltd, Regenerat & Cellular Med Kobe Ctr, Kobe, Hyogo, Japan Keio Univ, Dept Orthopaed Surg, Sch Med, Tokyo, Japan

Tamura, Takashi
论文数: 0 引用数: 0
h-index: 0
机构:
Fdn Biomed Res & Innovat, R&D Ctr Cell Therapy, Kobe, Hyogo, Japan Keio Univ, Dept Orthopaed Surg, Sch Med, Tokyo, Japan

Kohzuki, Tsuneo
论文数: 0 引用数: 0
h-index: 0
机构:
Keio Univ, Dept Physiol, Sch Med, Tokyo, Japan Keio Univ, Dept Orthopaed Surg, Sch Med, Tokyo, Japan

Abe, Takayuki
论文数: 0 引用数: 0
h-index: 0
机构:
Yokohama City Univ, Sch Data Sci, Yokohama, Kanagawa, Japan
Keio Univ, Clin & Translat Res Ctr, Sch Med, Tokyo, Japan Keio Univ, Dept Orthopaed Surg, Sch Med, Tokyo, Japan

Shibata, Reo
论文数: 0 引用数: 0
h-index: 0
机构:
Keio Univ, Dept Orthopaed Surg, Sch Med, Tokyo, Japan Keio Univ, Dept Orthopaed Surg, Sch Med, Tokyo, Japan

Kamata, Yasuhiro
论文数: 0 引用数: 0
h-index: 0
机构:
Keio Univ, Dept Orthopaed Surg, Sch Med, Tokyo, Japan Keio Univ, Dept Orthopaed Surg, Sch Med, Tokyo, Japan

论文数: 引用数:
h-index:
机构:

Okubo, Toshiki
论文数: 0 引用数: 0
h-index: 0
机构:
Keio Univ, Dept Orthopaed Surg, Sch Med, Tokyo, Japan Keio Univ, Dept Orthopaed Surg, Sch Med, Tokyo, Japan

Tsuji, Osahiko
论文数: 0 引用数: 0
h-index: 0
机构:
Keio Univ, Dept Orthopaed Surg, Sch Med, Tokyo, Japan Keio Univ, Dept Orthopaed Surg, Sch Med, Tokyo, Japan

Nori, Satoshi
论文数: 0 引用数: 0
h-index: 0
机构:
Keio Univ, Dept Orthopaed Surg, Sch Med, Tokyo, Japan Keio Univ, Dept Orthopaed Surg, Sch Med, Tokyo, Japan

论文数: 引用数:
h-index:
机构:

Yamanaka, Shinya
论文数: 0 引用数: 0
h-index: 0
机构:
Kyoto Univ, Ctr IPS Cell Res & Applicat CiRA, Kyoto, Japan
CiRA Fdn CiRA, Kyoto, Japan Keio Univ, Dept Orthopaed Surg, Sch Med, Tokyo, Japan

Kawamata, Shin
论文数: 0 引用数: 0
h-index: 0
机构:
Fdn Biomed Res & Innovat, R&D Ctr Cell Therapy, Kobe, Hyogo, Japan
Riken BDR Kobe, Kobe, Hyogo, Japan Keio Univ, Dept Orthopaed Surg, Sch Med, Tokyo, Japan

Kanemura, Yonehiro
论文数: 0 引用数: 0
h-index: 0
机构:
Natl Hosp Org Osaka Natl Hosp, Dept Biomed Res & Innovat, Inst Clin Res, Osaka, Japan
Natl Hosp Org Osaka Natl Hosp, Dept Neurosurg, Osaka, Japan Keio Univ, Dept Orthopaed Surg, Sch Med, Tokyo, Japan

Nakamura, Masaya
论文数: 0 引用数: 0
h-index: 0
机构:
Keio Univ, Dept Orthopaed Surg, Sch Med, Tokyo, Japan Keio Univ, Dept Orthopaed Surg, Sch Med, Tokyo, Japan

论文数: 引用数:
h-index:
机构:
[26]
First-in-human intrathecal gene transfer study for giant axonal neuropathy: Preliminary review of long-term efficacy and safety
[J].
Bharucha-Goebel, D.
;
Saade, D.
;
Todd, J.
;
Norato, G.
;
Jain, M.
;
Waite, M.
;
Armao, D.
;
Foley, A.
;
Lehky, T.
;
Averion, G.
;
Hu, Y.
;
Mohassel, P.
;
Hoke, A.
;
DeLong, T.
;
Acquaye, N.
;
Hinkley, L.
;
Chichester, J.
;
Mendoza, C.
;
Soldatos, A.
;
Gray, S.
;
Bonnemann, C.
.
NEUROMUSCULAR DISORDERS,
2022, 32
:S94-S94

Bharucha-Goebel, D.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

论文数: 引用数:
h-index:
机构:

Todd, J.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Norato, G.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Jain, M.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Waite, M.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Armao, D.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ N Carolina, Sch Med, Chapel Hill, NC 27515 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Foley, A.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Lehky, T.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Averion, G.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Hu, Y.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Mohassel, P.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Hoke, A.
论文数: 0 引用数: 0
h-index: 0
机构:
Johns Hopkins Sch Med, Bethesda, MD USA NIH, Bldg 10, Bethesda, MD 20892 USA

DeLong, T.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Acquaye, N.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Hinkley, L.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Chichester, J.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, Philadelphia, PA 19104 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Mendoza, C.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Soldatos, A.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA

Gray, S.
论文数: 0 引用数: 0
h-index: 0
机构:
UT Southwestern, Dallas, TX USA NIH, Bldg 10, Bethesda, MD 20892 USA

Bonnemann, C.
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Bldg 10, Bethesda, MD 20892 USA NIH, Bldg 10, Bethesda, MD 20892 USA
[27]
Review of Safety and Interim Analysis of Efficacy in the First in Human Intrathecal Gene Transfer Trial for Giant Axonal Neuropathy
[J].
Saade, Dimah
;
Bharucha-Goebel, Diana
;
Jain, Mina
;
Waite, Melissa
;
Norato, Gina
;
Cheung, Ken
;
Foley, A. Reghan
;
Paredes, Eduardo
;
Soldatos, Ariane
;
Rybin, Denis
;
Lehky, Tanya
;
Charnas, Lawrence
;
Hu, Ying
;
Whitehead, Matthew
;
Nath, Avindra
;
Zein, Wadih
;
Grieger, Josh
;
Samulski, R. Jude
;
Gray, Steven J.
;
Bonnemann, Carsten G.
.
MOLECULAR THERAPY,
2020, 28 (04)
:273-273

Saade, Dimah
论文数: 0 引用数: 0
h-index: 0
机构:
NINDS, Neuromuscular & Neurogenet Disorders Childhood Se, Neurogenet Branch, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA NINDS, Neuromuscular & Neurogenet Disorders Childhood Se, Neurogenet Branch, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA

Bharucha-Goebel, Diana
论文数: 0 引用数: 0
h-index: 0
机构:
NINDS, Neuromuscular & Neurogenet Disorders Childhood Se, Neurogenet Branch, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA
Childrens Natl Hlth Syst, Neurol, Washington, DC USA NINDS, Neuromuscular & Neurogenet Disorders Childhood Se, Neurogenet Branch, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA

Jain, Mina
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Dept Rehabil Med, Ctr Clin, Bethesda, MD 20892 USA NINDS, Neuromuscular & Neurogenet Disorders Childhood Se, Neurogenet Branch, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA

Waite, Melissa
论文数: 0 引用数: 0
h-index: 0
机构:
NIH, Dept Rehabil Med, Ctr Clin, Bethesda, MD 20892 USA NINDS, Neuromuscular & Neurogenet Disorders Childhood Se, Neurogenet Branch, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA

Norato, Gina
论文数: 0 引用数: 0
h-index: 0
机构:
NINDS, Off Biostat, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA NINDS, Neuromuscular & Neurogenet Disorders Childhood Se, Neurogenet Branch, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA

Cheung, Ken
论文数: 0 引用数: 0
h-index: 0
机构:
NINDS, NIH, New York, MD USA
Columbia Univ, Sch Publ Hlth, New York, NY USA NINDS, Neuromuscular & Neurogenet Disorders Childhood Se, Neurogenet Branch, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA

Foley, A. Reghan
论文数: 0 引用数: 0
h-index: 0
机构:
NINDS, Neuromuscular & Neurogenet Disorders Childhood Se, Neurogenet Branch, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA NINDS, Neuromuscular & Neurogenet Disorders Childhood Se, Neurogenet Branch, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA

Paredes, Eduardo
论文数: 0 引用数: 0
h-index: 0
机构:
NINDS, Neuromuscular & Neurogenet Disorders Childhood Se, Neurogenet Branch, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA NINDS, Neuromuscular & Neurogenet Disorders Childhood Se, Neurogenet Branch, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA

Soldatos, Ariane
论文数: 0 引用数: 0
h-index: 0
机构:
NINDS, Pediat Neurol, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA NINDS, Neuromuscular & Neurogenet Disorders Childhood Se, Neurogenet Branch, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA

Rybin, Denis
论文数: 0 引用数: 0
h-index: 0
机构:
Pfizer, Cambridge, MA USA NINDS, Neuromuscular & Neurogenet Disorders Childhood Se, Neurogenet Branch, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA

Lehky, Tanya
论文数: 0 引用数: 0
h-index: 0
机构:
NINDS, Clin Neurophysiol, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA NINDS, Neuromuscular & Neurogenet Disorders Childhood Se, Neurogenet Branch, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA

Charnas, Lawrence
论文数: 0 引用数: 0
h-index: 0
机构:
Pfizer, Cambridge, MA USA NINDS, Neuromuscular & Neurogenet Disorders Childhood Se, Neurogenet Branch, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA

Hu, Ying
论文数: 0 引用数: 0
h-index: 0
机构:
NINDS, Neuromuscular & Neurogenet Disorders Childhood Se, Neurogenet Branch, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA NINDS, Neuromuscular & Neurogenet Disorders Childhood Se, Neurogenet Branch, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA

Whitehead, Matthew
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Natl Hlth Syst, Neuroradiol, Washington, DC USA NINDS, Neuromuscular & Neurogenet Disorders Childhood Se, Neurogenet Branch, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA

Nath, Avindra
论文数: 0 引用数: 0
h-index: 0
机构:
NINDS, Sect Infect Nervous Syst, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA NINDS, Neuromuscular & Neurogenet Disorders Childhood Se, Neurogenet Branch, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA

Zein, Wadih
论文数: 0 引用数: 0
h-index: 0
机构:
NEI, NIH, Bethesda, MD 20892 USA NINDS, Neuromuscular & Neurogenet Disorders Childhood Se, Neurogenet Branch, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA

Grieger, Josh
论文数: 0 引用数: 0
h-index: 0
机构:
AskBio, Res Triangle Pk, NC USA NINDS, Neuromuscular & Neurogenet Disorders Childhood Se, Neurogenet Branch, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA

Samulski, R. Jude
论文数: 0 引用数: 0
h-index: 0
机构:
UNC, Chapel Hill, NC USA NINDS, Neuromuscular & Neurogenet Disorders Childhood Se, Neurogenet Branch, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA

Gray, Steven J.
论文数: 0 引用数: 0
h-index: 0
机构:
UT Southwestern Med Ctr, Dallas, TX USA NINDS, Neuromuscular & Neurogenet Disorders Childhood Se, Neurogenet Branch, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA

Bonnemann, Carsten G.
论文数: 0 引用数: 0
h-index: 0
机构:
NINDS, Neuromuscular & Neurogenet Disorders Childhood Se, Neurogenet Branch, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA NINDS, Neuromuscular & Neurogenet Disorders Childhood Se, Neurogenet Branch, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA
[28]
An open-label, first-in-human, phase I trial of the safety and efficacy of daily PCLX-001.
[J].
Sangha, Randeep S.
;
Sehn, Laurie Helen
;
Kuruvilla, John
;
Weickert, Michael
;
Mackey, John Robert
;
Berthiaume, Luc G.
.
JOURNAL OF CLINICAL ONCOLOGY,
2020, 38 (15)

Sangha, Randeep S.
论文数: 0 引用数: 0
h-index: 0
机构: Cross Canc Inst, Edmonton, AB, Canada

Sehn, Laurie Helen
论文数: 0 引用数: 0
h-index: 0
机构: Cross Canc Inst, Edmonton, AB, Canada

Kuruvilla, John
论文数: 0 引用数: 0
h-index: 0
机构: Cross Canc Inst, Edmonton, AB, Canada

Weickert, Michael
论文数: 0 引用数: 0
h-index: 0
机构: Cross Canc Inst, Edmonton, AB, Canada

Mackey, John Robert
论文数: 0 引用数: 0
h-index: 0
机构: Cross Canc Inst, Edmonton, AB, Canada

Berthiaume, Luc G.
论文数: 0 引用数: 0
h-index: 0
机构: Cross Canc Inst, Edmonton, AB, Canada
[29]
Safety and efficacy of bronchoscopic cryospray therapy for refractory or unexplained chronic cough: Preclinical investigations and first-in-human trial
[J].
Huang, Junfeng
;
Lin, Jinsheng
;
Zhong, Shuxin
;
Chen, Difei
;
Fang, Liman
;
Chen, Ruchong
;
Li, Shiyue
.
RESPIROLOGY,
2024, 29
:25-26

Huang, Junfeng
论文数: 0 引用数: 0
h-index: 0
机构:
Guangzhou Med Univ, Affiliated Hosp 1, Natl Clin Res Ctr Resp Dis,State Key Lab Resp Dis, Natl Ctr Resp Med,Guangzhou Inst Resp Hlth,Dept R, Guangzhou, Peoples R China Guangzhou Med Univ, Affiliated Hosp 1, Natl Clin Res Ctr Resp Dis,State Key Lab Resp Dis, Natl Ctr Resp Med,Guangzhou Inst Resp Hlth,Dept R, Guangzhou, Peoples R China

Lin, Jinsheng
论文数: 0 引用数: 0
h-index: 0
机构:
Guangzhou Med Univ, Affiliated Hosp 1, Natl Clin Res Ctr Resp Dis,State Key Lab Resp Dis, Natl Ctr Resp Med,Guangzhou Inst Resp Hlth,Dept R, Guangzhou, Peoples R China Guangzhou Med Univ, Affiliated Hosp 1, Natl Clin Res Ctr Resp Dis,State Key Lab Resp Dis, Natl Ctr Resp Med,Guangzhou Inst Resp Hlth,Dept R, Guangzhou, Peoples R China

Zhong, Shuxin
论文数: 0 引用数: 0
h-index: 0
机构:
Guangzhou Med Univ, Affiliated Hosp 1, Natl Clin Res Ctr Resp Dis,State Key Lab Resp Dis, Natl Ctr Resp Med,Guangzhou Inst Resp Hlth,Dept R, Guangzhou, Peoples R China Guangzhou Med Univ, Affiliated Hosp 1, Natl Clin Res Ctr Resp Dis,State Key Lab Resp Dis, Natl Ctr Resp Med,Guangzhou Inst Resp Hlth,Dept R, Guangzhou, Peoples R China

Chen, Difei
论文数: 0 引用数: 0
h-index: 0
机构:
Guangzhou Med Univ, Affiliated Hosp 1, Natl Clin Res Ctr Resp Dis,State Key Lab Resp Dis, Natl Ctr Resp Med,Guangzhou Inst Resp Hlth,Dept R, Guangzhou, Peoples R China Guangzhou Med Univ, Affiliated Hosp 1, Natl Clin Res Ctr Resp Dis,State Key Lab Resp Dis, Natl Ctr Resp Med,Guangzhou Inst Resp Hlth,Dept R, Guangzhou, Peoples R China

Fang, Liman
论文数: 0 引用数: 0
h-index: 0
机构:
Guangzhou Med Univ, Affiliated Hosp 1, Natl Clin Res Ctr Resp Dis,State Key Lab Resp Dis, Natl Ctr Resp Med,Guangzhou Inst Resp Hlth,Dept R, Guangzhou, Peoples R China Guangzhou Med Univ, Affiliated Hosp 1, Natl Clin Res Ctr Resp Dis,State Key Lab Resp Dis, Natl Ctr Resp Med,Guangzhou Inst Resp Hlth,Dept R, Guangzhou, Peoples R China

Chen, Ruchong
论文数: 0 引用数: 0
h-index: 0
机构:
Guangzhou Med Univ, Affiliated Hosp 1, Natl Clin Res Ctr Resp Dis,State Key Lab Resp Dis, Natl Ctr Resp Med,Guangzhou Inst Resp Hlth,Dept R, Guangzhou, Peoples R China Guangzhou Med Univ, Affiliated Hosp 1, Natl Clin Res Ctr Resp Dis,State Key Lab Resp Dis, Natl Ctr Resp Med,Guangzhou Inst Resp Hlth,Dept R, Guangzhou, Peoples R China

Li, Shiyue
论文数: 0 引用数: 0
h-index: 0
机构:
Guangzhou Med Univ, Affiliated Hosp 1, Natl Clin Res Ctr Resp Dis,State Key Lab Resp Dis, Natl Ctr Resp Med,Guangzhou Inst Resp Hlth,Dept R, Guangzhou, Peoples R China Guangzhou Med Univ, Affiliated Hosp 1, Natl Clin Res Ctr Resp Dis,State Key Lab Resp Dis, Natl Ctr Resp Med,Guangzhou Inst Resp Hlth,Dept R, Guangzhou, Peoples R China
[30]
Results from a first-in-human trial of a novel vascular sealant
[J].
Florek, Hans-Joachim
;
Brunkwall, Jan
;
Orend, Karl-Heinz
;
Handley, Ian
;
Pribble, John
;
Dieck, Ronald
.
FRONTIERS IN SURGERY,
2015, 2

Florek, Hans-Joachim
论文数: 0 引用数: 0
h-index: 0
机构:
Helios Kliniken Frietal, Dept Vasc Surg, Freital, Germany Helios Kliniken Frietal, Dept Vasc Surg, Freital, Germany

论文数: 引用数:
h-index:
机构:

Orend, Karl-Heinz
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Ulm, Dept Thorac & Vasc Surg, Ulm, Germany Helios Kliniken Frietal, Dept Vasc Surg, Freital, Germany

Handley, Ian
论文数: 0 引用数: 0
h-index: 0
机构:
Tenaxis Med Inc, Mountain View, CA USA Helios Kliniken Frietal, Dept Vasc Surg, Freital, Germany

Pribble, John
论文数: 0 引用数: 0
h-index: 0
机构:
Med Co, 1144 Eastlake Ave East,Suite 700, Seattle, WA 98109 USA Helios Kliniken Frietal, Dept Vasc Surg, Freital, Germany

Dieck, Ronald
论文数: 0 引用数: 0
h-index: 0
机构:
Tenaxis Med Inc, Mountain View, CA USA Helios Kliniken Frietal, Dept Vasc Surg, Freital, Germany