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- [3] OUTCOME MEASURES FOR DUCHENNE MUSCULAR DYSTROPHY: IMPLICATIONS FOR TRIALS JOURNAL OF NEUROLOGY NEUROSURGERY AND PSYCHIATRY, 2017, 88 : A63 - A63
- [8] Cumulative jerk as an outcome measure in nonambulatory Duchenne muscular dystrophy BRAIN & DEVELOPMENT, 2019, 41 (09): : 796 - 802
- [9] Clinical trials of exon skipping in Duchenne muscular dystrophy EXPERT OPINION ON ORPHAN DRUGS, 2017, 5 (09): : 683 - 690
- [10] Outcome measures in Duchenne muscular dystrophy: sensitivity to change, clinical meaningfulness, and implications for clinical trials DEVELOPMENTAL MEDICINE AND CHILD NEUROLOGY, 2018, 60 (02): : 117 - 117