Dystrophin as a biochemical outcome measure in Duchenne muscular dystrophy clinical trials

被引:0
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作者
Sardone, V. [1 ]
Ellis, M. [2 ]
Torelli, S. [1 ]
Feng, L. [1 ]
Chambers, D. [1 ]
Ricotti, V. [1 ]
Domingos, J. Pisco [1 ]
Phadke, R. [1 ,3 ]
Sewry, C. A. [3 ]
Morgan, J. [1 ]
Muntoni, F. [1 ]
机构
[1] UCL Inst Child Hlth, Dubowitz Neuromuscular Ctr, London, England
[2] UCL Inst Neurol, Dept Neurodegenerat Dis, London, England
[3] Great Ormond St Hosp Sick Children, London, England
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R74 [神经病学与精神病学];
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P41
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页码:S16 / S16
页数:1
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