Enzyme replacement therapy for lysosomal storage disorders

被引：1
|
作者：
Keutzer, Joan [1 ]
Yee, John [2 ]
机构：
[1] Genzyme Corp, LSD Sci Affairs, Cambridge, MA 02142 USA
[2] Genzyme Corp, LSD Global Med Affairs, Cambridge, MA USA
来源：
HUMAN GENE THERAPY | 2008年 / 19卷 / 08期
关键词：
D O I：
10.1089/hum.2008.0714
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
引用
收藏
页码：857 / 857
页数：1
相关论文
共 50 条
  • [31] Maximizing the therapeutic potential of enzyme replacement therapy for lysosomal storage diseases
    Gieselmann, V.
    INTERNATIONAL JOURNAL OF CLINICAL PHARMACOLOGY AND THERAPEUTICS, 2009, 47 (12) : 707 - 708
  • [32] Enzyme replacement therapy versus substrate deprivation in the treatment of lysosomal disorders
    Aerts, J. M.
    CHEMISTRY AND PHYSICS OF LIPIDS, 2008, 154 : S19 - S19
  • [33] Delayed infusion reactions associated with enzyme replacement therapies for lysosomal storage disorders
    Utz, Jeanine
    Doyen, Colleen
    Whitley, Chester B.
    MOLECULAR GENETICS AND METABOLISM, 2008, 93 (02) : S40 - S40
  • [34] Non-inhibitory antibodies impede lysosomal storage reduction in enzyme replacement therapy of a lysosomal storage disease
    Matzner, U.
    Matthes, F.
    Herbst, E.
    Luellmann-Rauch, R.
    Weigelt, C.
    Andersson, C.
    Eistrup, C.
    Fogh, J.
    Gieselmann, V
    JOURNAL OF INHERITED METABOLIC DISEASE, 2007, 30 : 124 - 124
  • [35] Role of the Lactide:Glycolide Ratio in PLGA Nanoparticle Stability and Release under Lysosomal Conditions for Enzyme Replacement Therapy of Lysosomal Storage Disorders
    del Moral, Maria
    Loeck, Maximilian
    Muntimadugu, Eameema
    Vives, Guillem
    Pham, Vy
    Pfeifer, Peter
    Battaglia, Giuseppe
    Muro, Silvia
    Andrianov, Alexander K.
    JOURNAL OF FUNCTIONAL BIOMATERIALS, 2023, 14 (09)
  • [36] Hypersensitivity reaction during enzyme replacement therapy in lysosomal storage disorders. A systematic review of desensitization strategies
    Spataro, Federico
    Carlucci, Palma
    Loverre, Teresa
    Macchia, Luigi
    Di Bona, Danilo
    PEDIATRIC ALLERGY AND IMMUNOLOGY, 2023, 34 (06)
  • [37] Hypersensitivity reaction during enzyme replacement therapy in lysosomal storage disorders: a systematic review of desensitization strategies Reply
    Spataro, Federico
    Carlucci, Palma
    PEDIATRIC ALLERGY AND IMMUNOLOGY, 2024, 35 (08)
  • [38] Engineering memory T cells as a platform for long-term enzyme replacement therapy in lysosomal storage disorders
    Kleinboehl, Evan W.
    Laoharawee, Kanut
    Jensen, Jacob D.
    Peterson, Joseph J.
    Slipek, Nicholas J.
    Wick, Bryce J.
    Johnson, Matthew J.
    Webber, Beau R.
    Moriarity, Branden S.
    MOLECULAR THERAPY, 2024, 32 (11) : 3865 - 3878
  • [39] Therapy for Lysosomal Storage Disorders
    Beck, Michael
    IUBMB LIFE, 2010, 62 (01) : 33 - 40
  • [40] Enzyme therapy for the lysosomal storage disorders: principles, patents, practice and prospects
    Pastores, GM
    EXPERT OPINION ON THERAPEUTIC PATENTS, 2003, 13 (08) : 1157 - 1172
12345