Directed evolution of a family of AAV capsid variants enabling potent muscle-directed gene delivery across species

被引：0
作者：
Tabebordbar, S. [1 ]
Lagerborg, K. [2 ]
Ye, S. [2 ]
Stanton, A. [2 ]
King, E. [2 ]
Tellez, L. [2 ]
Krunnfusz, A. [2 ]
Tavakoli, S. [3 ]
Widrick, J. [4 ]
Messemer, K. [3 ]
Troiano, E. [4 ]
Moghadaszadeh, B. [4 ]
Peacker, B. [3 ]
Leacock, K. [3 ]
Horwitz, N. [3 ]
Beggs, A. [4 ]
Wagers, A. [3 ]
Sabeti, P. [2 ]
机构：
[1] Kate Therapeut, San Diego, CA USA
[2] Broad Inst, Cambridge, MA USA
[3] Harvard Univ, Cambridge, MA 02138 USA
[4] Boston Childrens Hosp, Boston, MA USA
来源：
NEUROMUSCULAR DISORDERS | 2022年 / 32卷
关键词：
D O I：
10.1016/j.nmd.2022.07.225
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
I.11
引用
收藏
页码：S96 / S96
页数：1
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