CITRIN MRNA THERAPY IMPROVED METABOLIC AND BEHAVIORAL ABNORMALITIES IN A MOUSE MODEL OF TYPE II CITRULLINEMIA

被引：0
|
作者：
Cao, Jingsong [1 ]
Finn, Patrick [1 ]
An, Jeff [1 ]
Guey, Lin [1 ]
Galduroz, Mikel [1 ]
Lukacs, Christine [1 ]
Frassetto, Andrea [1 ]
Sabnis, Staci [2 ,3 ]
Murphy-Benenato, Kerry E. [2 ,3 ]
Kumarasinghe, E. Sathyajith [2 ,3 ]
Salerno, Timothy [2 ,3 ]
Saheki, Takeyori [2 ,3 ]
Martini, Paolo [1 ]
机构：
[1] Moderna Therapeut, Rare Dis, Cambridge, MA USA
[2] Moderna Therapeut, Formulat, Cambridge, MA USA
[3] Kagoshima Univ, Dept Mol Oncol, Kagoshima, Japan
来源：
MOLECULAR GENETICS AND METABOLISM | 2018年 / 123卷 / 03期
关键词：
D O I：
暂无
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
26
引用
收藏
页码：222 / 222
页数：1
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