CITRIN MRNA THERAPY IMPROVED METABOLIC AND BEHAVIORAL ABNORMALITIES IN A MOUSE MODEL OF TYPE II CITRULLINEMIA

被引:0
|
作者
Cao, Jingsong [1 ]
Finn, Patrick [1 ]
An, Jeff [1 ]
Guey, Lin [1 ]
Galduroz, Mikel [1 ]
Lukacs, Christine [1 ]
Frassetto, Andrea [1 ]
Sabnis, Staci [2 ,3 ]
Murphy-Benenato, Kerry E. [2 ,3 ]
Kumarasinghe, E. Sathyajith [2 ,3 ]
Salerno, Timothy [2 ,3 ]
Saheki, Takeyori [2 ,3 ]
Martini, Paolo [1 ]
机构
[1] Moderna Therapeut, Rare Dis, Cambridge, MA USA
[2] Moderna Therapeut, Formulat, Cambridge, MA USA
[3] Kagoshima Univ, Dept Mol Oncol, Kagoshima, Japan
关键词
D O I
暂无
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
26
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收藏
页码:222 / 222
页数:1
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