Birth of a New Therapeutic Platform: 47 Years of Adeno-associated Virus Biology From Virus Discovery to Licensed Gene Therapy

被引：16

作者：

Flotte, Terence R. ^{[1
]}

机构：

[1] Univ Massachusetts, Sch Med, Dept Pediat, Gene Therapy Ctr, Worcester, MA USA

来源：

MOLECULAR THERAPY | 2013年 / 21卷 / 11期

关键词：

ADENO-ASSOCIATED VIRUS; LEBER CONGENITAL AMAUROSIS; PHASE-I TRIAL; TRANSMEMBRANE CONDUCTANCE REGULATOR; CYSTIC-FIBROSIS; MESSENGER-RNA; CLINICAL-TRIAL; WILD-TYPE; INTRAMUSCULAR INJECTION; RECOMBINANT PLASMID;

D O I：

10.1038/mt.2013.226

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

引用

页码：1976 / 1981

页数：6

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