CRISPR-Cas9 Gene Editing for Sickle Cell Disease and β-Thalassemia

被引：55

作者：

Meisel, Roland ^{[1
]}

机构：

[1] Heinrich Heine Univ, Dusseldorf, Germany

来源：

NEW ENGLAND JOURNAL OF MEDICINE | 2021年 / 384卷 / 23期

关键词：

BCL11A;

D O I：

10.1056/NEJMc2103481

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

引用

页数：1

共 3 条

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[3] Bcl11a Deficiency Leads to Hematopoietic Stem Cell Defects with an Aging-like Phenotype [J].

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