共 5 条
[1]
[Anonymous], 2020, ASGR1 AS REC 1
[2]
Phase 3 Trial of RNAi Therapeutic Givosiran for Acute Intermittent Porphyria
[J].
Balwani, Manisha
;
Sardh, Eliane
;
Ventura, Paolo
;
Peiro, Paula Aguilera
;
Rees, David C.
;
Stoelzel, Ulrich
;
Bissell, D. Montgomery
;
Bonkovsky, Herbert L.
;
Windyga, Jerzy
;
Anderson, Karl E.
;
Parker, Charles
;
Silver, Samuel M.
;
Keel, Sioban B.
;
Wang, Jiaan-Der
;
Stein, Penelope E.
;
Harper, Pauline
;
Vassiliou, Daphne
;
Wang, Bruce
;
Phillips, John
;
Ivanova, Aneta
;
Langendonk, Janneke G.
;
Kauppinen, Raili
;
Minder, Elisabeth
;
Horie, Yutaka
;
Penz, Craig
;
Chen, Jihong
;
Liu, Shangbin
;
Ko, John J.
;
Sweetser, Marianne T.
;
Garg, Pushkal
;
Vaishnaw, Akshay
;
Kim, Jae B.
;
Simon, Amy R.
;
Gouya, Laurent
.
NEW ENGLAND JOURNAL OF MEDICINE,
2020, 382 (24)
:2289-2301

Balwani, Manisha
论文数: 0 引用数: 0
h-index: 0
机构:
Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

Sardh, Eliane
论文数: 0 引用数: 0
h-index: 0
机构:
Karolinska Univ Hosp, Karolinska Inst, Ctr Inherited Metab Dis, Porphyria Ctr Sweden, Stockholm, Sweden Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

Ventura, Paolo
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Modena & Reggio Emilia, Internal Med Unit, Dept Surg & Med Sci Children & Adults, Modena, Italy Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

Peiro, Paula Aguilera
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Barcelona, Hosp Clin Barcelona, Barcelona, Spain Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

Rees, David C.
论文数: 0 引用数: 0
h-index: 0
机构:
Kings Coll London, Kings Coll Hosp, London, England Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

Stoelzel, Ulrich
论文数: 0 引用数: 0
h-index: 0
机构:
Klinikum Chemnitz, Chemnitz, Germany Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

Bissell, D. Montgomery
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif San Francisco, Ctr Liver, San Francisco, CA 94143 USA
Univ Calif San Francisco, Porphyria Ctr, San Francisco, CA 94143 USA Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

Bonkovsky, Herbert L.
论文数: 0 引用数: 0
h-index: 0
机构:
Wake Forest Univ, North Carolina Baptist Med Ctr, Sect Gastroenterol & Hepatol, Winston Salem, NC 27101 USA Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

Windyga, Jerzy
论文数: 0 引用数: 0
h-index: 0
机构:
Inst Hematol & Transfus Med, Dept Hemostat Disorders & Internal Med, Warsaw, Poland Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

Anderson, Karl E.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Med Branch, Galveston, TX 77555 USA Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

Parker, Charles
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Utah, Salt Lake City, UT USA Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

Silver, Samuel M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Michigan, Ann Arbor, MI 48109 USA Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

Keel, Sioban B.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Washington, Dept Med, Div Hematol, Seattle, WA 98195 USA Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

Wang, Jiaan-Der
论文数: 0 引用数: 0
h-index: 0
机构:
Taichung Vet Gen Hosp, Ctr Rare Dis & Hemophilia, Taichung, Taiwan Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

Stein, Penelope E.
论文数: 0 引用数: 0
h-index: 0
机构:
Kings Coll London, Kings Coll Hosp, London, England Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

Harper, Pauline
论文数: 0 引用数: 0
h-index: 0
机构:
Karolinska Univ Hosp, Karolinska Inst, Ctr Inherited Metab Dis, Porphyria Ctr Sweden, Stockholm, Sweden Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

Vassiliou, Daphne
论文数: 0 引用数: 0
h-index: 0
机构:
Karolinska Univ Hosp, Karolinska Inst, Ctr Inherited Metab Dis, Porphyria Ctr Sweden, Stockholm, Sweden Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

Wang, Bruce
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif San Francisco, Ctr Liver, San Francisco, CA 94143 USA
Univ Calif San Francisco, Porphyria Ctr, San Francisco, CA 94143 USA Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

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Ivanova, Aneta
论文数: 0 引用数: 0
h-index: 0
机构:
St Ivan Rilski Univ Hosp, Sofia, Bulgaria Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

Langendonk, Janneke G.
论文数: 0 引用数: 0
h-index: 0
机构:
Erasmus MC, Univ Med Ctr Rotterdam, Ctr Lysosomal & Metab Dis, Dept Internal Med,Porphyria Ctr Rotterdam, Rotterdam, Netherlands Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

Kauppinen, Raili
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Hosp Helsinki, Dept Med, Helsinki, Finland Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

Minder, Elisabeth
论文数: 0 引用数: 0
h-index: 0
机构:
Stadtspital Triemli, Zurich, Switzerland Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

Horie, Yutaka
论文数: 0 引用数: 0
h-index: 0
机构:
Tottori Univ, Sch Med, Tottori, Japan Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

Penz, Craig
论文数: 0 引用数: 0
h-index: 0
机构:
Alnylam Pharmaceut, Cambridge, MA USA Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

Chen, Jihong
论文数: 0 引用数: 0
h-index: 0
机构:
Alnylam Pharmaceut, Cambridge, MA USA Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

Liu, Shangbin
论文数: 0 引用数: 0
h-index: 0
机构:
Alnylam Pharmaceut, Cambridge, MA USA Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

Ko, John J.
论文数: 0 引用数: 0
h-index: 0
机构:
Alnylam Pharmaceut, Cambridge, MA USA Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

Sweetser, Marianne T.
论文数: 0 引用数: 0
h-index: 0
机构:
Alnylam Pharmaceut, Cambridge, MA USA Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

Garg, Pushkal
论文数: 0 引用数: 0
h-index: 0
机构:
Alnylam Pharmaceut, Cambridge, MA USA Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

Vaishnaw, Akshay
论文数: 0 引用数: 0
h-index: 0
机构:
Alnylam Pharmaceut, Cambridge, MA USA Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

Kim, Jae B.
论文数: 0 引用数: 0
h-index: 0
机构:
Alnylam Pharmaceut, Cambridge, MA USA Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

Simon, Amy R.
论文数: 0 引用数: 0
h-index: 0
机构:
Alnylam Pharmaceut, Cambridge, MA USA Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, New York, NY 10029 USA

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[3]
Porphyria and kidney diseases
[J].
Pallet, Nicolas
;
Karras, Alexandre
;
Thervet, Eric
;
Gouya, Laurent
;
Karim, Zoubida
;
Puy, Herve
.
CLINICAL KIDNEY JOURNAL,
2018, 11 (02)
:191-197

论文数: 引用数:
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Karras, Alexandre
论文数: 0 引用数: 0
h-index: 0
机构:
Ctr Univ St Peres, INSERM, U1147, Paris, France
Univ Paris 05, Paris, France
Hop Europeen Georges Pompidou, AP HP, Serv Nephrol, Paris, France Ctr Univ St Peres, INSERM, U1147, Paris, France

Thervet, Eric
论文数: 0 引用数: 0
h-index: 0
机构:
Ctr Univ St Peres, INSERM, U1147, Paris, France
Univ Paris 05, Paris, France
Hop Europeen Georges Pompidou, AP HP, Serv Nephrol, Paris, France Ctr Univ St Peres, INSERM, U1147, Paris, France

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[4]
SAITOH S, 2018, PLOS ONE
[5]
Dynamic changes in Bach1 expression in the kidney of rhabdomyolysis-associated acute kidney injury
[J].
Yamaoka, Masakazu
;
Shimizu, Hiroko
;
Takahashi, Toru
;
Omori, Emiko
;
Morimatsu, Hiroshi
.
PLOS ONE,
2017, 12 (07)

Yamaoka, Masakazu
论文数: 0 引用数: 0
h-index: 0
机构:
Okayama Univ, Dept Anesthesiol & Resuscitol, Med Sch, Okayama, Japan Okayama Univ, Dept Anesthesiol & Resuscitol, Med Sch, Okayama, Japan

Shimizu, Hiroko
论文数: 0 引用数: 0
h-index: 0
机构:
Okayama Univ, Dept Anesthesiol & Resuscitol, Med Sch, Okayama, Japan Okayama Univ, Dept Anesthesiol & Resuscitol, Med Sch, Okayama, Japan

Takahashi, Toru
论文数: 0 引用数: 0
h-index: 0
机构:
Okayama Prefectural Univ, Dept Fac Hlth & Welf Sci, Okayama, Japan Okayama Univ, Dept Anesthesiol & Resuscitol, Med Sch, Okayama, Japan

Omori, Emiko
论文数: 0 引用数: 0
h-index: 0
机构:
Okayama Univ, Dept Anesthesiol & Resuscitol, Med Sch, Okayama, Japan Okayama Univ, Dept Anesthesiol & Resuscitol, Med Sch, Okayama, Japan

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