VERVE-101: a promising CRISPR-based gene editing therapy that reduces LDL-C and PCSK9 levels in HeFH patients

被引：18

作者：

Horie, Takahiro ^{[1
]}

Ono, Koh ^{[1
]}

机构：

[1] Kyoto Univ, Grad Sch Med, Dept Cardiovasc Med, 54 Kawahara Cho,Sakyo Ku, Kyoto 6068507, Japan

来源：

EUROPEAN HEART JOURNAL-CARDIOVASCULAR PHARMACOTHERAPY | 2024年 / 10卷 / 02期

关键词：

D O I：

10.1093/ehjcvp/pvad103

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

引用

页码：89 / 90

页数：2

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[4] Two Phase 3 Trials of Inclisiran in Patients with Elevated LDL Cholesterol [J].

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[5]

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