共 5 条
[1]
Genome editing with CRISPR-Cas nucleases, base editors, transposases and prime editors
[J].
Anzalone, Andrew V.
;
Koblan, Luke W.
;
Liu, David R.
.
NATURE BIOTECHNOLOGY,
2020, 38 (07)
:824-844

Anzalone, Andrew V.
论文数: 0 引用数: 0
h-index: 0
机构:
Broad Inst MIT & Harvard, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA
Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA
Harvard Univ, Howard Hughes Med Inst, Cambridge, MA 02138 USA Broad Inst MIT & Harvard, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA

Koblan, Luke W.
论文数: 0 引用数: 0
h-index: 0
机构:
Broad Inst MIT & Harvard, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA
Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA
Harvard Univ, Howard Hughes Med Inst, Cambridge, MA 02138 USA Broad Inst MIT & Harvard, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA

Liu, David R.
论文数: 0 引用数: 0
h-index: 0
机构:
Broad Inst MIT & Harvard, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA
Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA
Harvard Univ, Howard Hughes Med Inst, Cambridge, MA 02138 USA Broad Inst MIT & Harvard, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA
[2]
Programmable base editing of A.T to G.C in genomic DNA without DNA cleavage
[J].
Gaudelli, Nicole M.
;
Komor, Alexis C.
;
Rees, Holly A.
;
Packer, Michael S.
;
Badran, Ahmed H.
;
Bryson, David I.
;
Liu, David R.
.
NATURE,
2017, 551 (7681)
:464-+

Gaudelli, Nicole M.
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA
Harvard Univ, Howard Hughes Med Inst, Cambridge, MA 02138 USA
Broad Inst MIT & Harvard, Cambridge, MA 02142 USA Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA

Komor, Alexis C.
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA
Harvard Univ, Howard Hughes Med Inst, Cambridge, MA 02138 USA
Broad Inst MIT & Harvard, Cambridge, MA 02142 USA
Univ Calif San Diego, Dept Chem & Biochem, La Jolla, CA 92093 USA Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA

Rees, Holly A.
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA
Harvard Univ, Howard Hughes Med Inst, Cambridge, MA 02138 USA
Broad Inst MIT & Harvard, Cambridge, MA 02142 USA Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA

Packer, Michael S.
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA
Harvard Univ, Howard Hughes Med Inst, Cambridge, MA 02138 USA
Broad Inst MIT & Harvard, Cambridge, MA 02142 USA
Beam Therapeut, 675 West Kendall St, Cambridge, MA 02139 USA Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA

Badran, Ahmed H.
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA
Harvard Univ, Howard Hughes Med Inst, Cambridge, MA 02138 USA
Broad Inst MIT & Harvard, Cambridge, MA 02142 USA Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA

Bryson, David I.
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA
Harvard Univ, Howard Hughes Med Inst, Cambridge, MA 02138 USA
Broad Inst MIT & Harvard, Cambridge, MA 02142 USA
Beam Therapeut, 675 West Kendall St, Cambridge, MA 02139 USA Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA

Liu, David R.
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA
Harvard Univ, Howard Hughes Med Inst, Cambridge, MA 02138 USA
Broad Inst MIT & Harvard, Cambridge, MA 02142 USA Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA
[3]
Efficacy and Safety of an Investigational Single-Course CRISPR Base-Editing Therapy Targeting PCSK9 in Nonhuman Primate and Mouse Models
[J].
Lee, Richard G.
;
Mazzola, Anne Marie
;
Braun, Maurine C.
;
Platt, Colin
;
Vafai, Scott B.
;
Kathiresan, Sekar
;
Rohde, Ellen
;
Bellinger, Andrew M.
;
Khera, Amit, V
.
CIRCULATION,
2023, 147 (03)
:242-253

Lee, Richard G.
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Boston, MA USA Verve Therapeut, Boston, MA USA

Mazzola, Anne Marie
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Boston, MA USA Verve Therapeut, Boston, MA USA

Braun, Maurine C.
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Boston, MA USA Verve Therapeut, Boston, MA USA

Platt, Colin
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Boston, MA USA Verve Therapeut, Boston, MA USA

Vafai, Scott B.
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Boston, MA USA Verve Therapeut, Boston, MA USA

Kathiresan, Sekar
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Boston, MA USA Verve Therapeut, Boston, MA USA

Rohde, Ellen
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Boston, MA USA Verve Therapeut, Boston, MA USA

Bellinger, Andrew M.
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Boston, MA USA Verve Therapeut, Boston, MA USA

Khera, Amit, V
论文数: 0 引用数: 0
h-index: 0
机构:
Verve Therapeut, Boston, MA USA Verve Therapeut, Boston, MA USA
[4]
Two Phase 3 Trials of Inclisiran in Patients with Elevated LDL Cholesterol
[J].
Ray, Kausik K.
;
Wright, R. Scott
;
Kallend, David
;
Koenig, Wolfgang
;
Leiter, Lawrence A.
;
Raal, Frederick J.
;
Bisch, Jenna A.
;
Richardson, Tara
;
Jaros, Mark
;
Wijngaard, Peter L. J.
;
Kastelein, John J. P.
.
NEW ENGLAND JOURNAL OF MEDICINE,
2020, 382 (16)
:1507-1519

Ray, Kausik K.
论文数: 0 引用数: 0
h-index: 0
机构:
Imperial Coll London, Imperial Ctr Cardiovasc Dis Prevent, Dept Primary Care & Publ Hlth, Reynolds Bldg,St Dunstans Rd, London W6 8RP, England Imperial Coll London, Imperial Ctr Cardiovasc Dis Prevent, Dept Primary Care & Publ Hlth, Reynolds Bldg,St Dunstans Rd, London W6 8RP, England

Wright, R. Scott
论文数: 0 引用数: 0
h-index: 0
机构:
Mayo Clin, Dept Cardiol, Rochester, MN USA Imperial Coll London, Imperial Ctr Cardiovasc Dis Prevent, Dept Primary Care & Publ Hlth, Reynolds Bldg,St Dunstans Rd, London W6 8RP, England

Kallend, David
论文数: 0 引用数: 0
h-index: 0
机构:
Medicines Co, Zurich, Switzerland Imperial Coll London, Imperial Ctr Cardiovasc Dis Prevent, Dept Primary Care & Publ Hlth, Reynolds Bldg,St Dunstans Rd, London W6 8RP, England

Koenig, Wolfgang
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Munich, Deutsch Herzzentrum Munchen, Munich, Germany
Partner Site Munich Heart Alliance, Deutsch Zentrum Herz Kreislauf Forsch, German Ctr Cardiovasc Res, Munich, Germany
Univ Ulm, Inst Epidemiol & Med Biometry, Ulm, Germany Imperial Coll London, Imperial Ctr Cardiovasc Dis Prevent, Dept Primary Care & Publ Hlth, Reynolds Bldg,St Dunstans Rd, London W6 8RP, England

Leiter, Lawrence A.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Toronto, Li Ka Shing Knowledge Inst, St Michaels Hosp, Toronto, ON, Canada Imperial Coll London, Imperial Ctr Cardiovasc Dis Prevent, Dept Primary Care & Publ Hlth, Reynolds Bldg,St Dunstans Rd, London W6 8RP, England

Raal, Frederick J.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Witwatersrand, Dept Med, Fac Hlth Sci, Johannesburg, South Africa Imperial Coll London, Imperial Ctr Cardiovasc Dis Prevent, Dept Primary Care & Publ Hlth, Reynolds Bldg,St Dunstans Rd, London W6 8RP, England

Bisch, Jenna A.
论文数: 0 引用数: 0
h-index: 0
机构:
Medicines Co, Parsippany, NJ USA Imperial Coll London, Imperial Ctr Cardiovasc Dis Prevent, Dept Primary Care & Publ Hlth, Reynolds Bldg,St Dunstans Rd, London W6 8RP, England

Richardson, Tara
论文数: 0 引用数: 0
h-index: 0
机构:
Medicines Co, Parsippany, NJ USA Imperial Coll London, Imperial Ctr Cardiovasc Dis Prevent, Dept Primary Care & Publ Hlth, Reynolds Bldg,St Dunstans Rd, London W6 8RP, England

Jaros, Mark
论文数: 0 引用数: 0
h-index: 0
机构:
Summit Analyt, Denver, CO USA Imperial Coll London, Imperial Ctr Cardiovasc Dis Prevent, Dept Primary Care & Publ Hlth, Reynolds Bldg,St Dunstans Rd, London W6 8RP, England

Wijngaard, Peter L. J.
论文数: 0 引用数: 0
h-index: 0
机构:
Medicines Co, Parsippany, NJ USA Imperial Coll London, Imperial Ctr Cardiovasc Dis Prevent, Dept Primary Care & Publ Hlth, Reynolds Bldg,St Dunstans Rd, London W6 8RP, England

Kastelein, John J. P.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Amsterdam, Dept Vasc Med, Acad Med Ctr, Amsterdam, Netherlands Imperial Coll London, Imperial Ctr Cardiovasc Dis Prevent, Dept Primary Care & Publ Hlth, Reynolds Bldg,St Dunstans Rd, London W6 8RP, England
[5]
Sabatine MS, 2017, NEW ENGL J MED, V376, P1713, DOI [10.4997/JRCPE.2017.212, 10.1056/NEJMoa1615664]