Treatment of Infantile-Onset Pompe Disease in a Rat Model with Muscle-Directed AAV Gene Therapy

被引：0

作者：

Garcia, Miquel ^{[1
]}

Munoz, Sergio ^{[1
]}

Bertolin, Joan ^{[1
]}

Jimenez, Veronica ^{[1
]}

Jaen, Maria Luisa ^{[1
]}

Pujol, Anna ^{[1
]}

Vila, Laia ^{[1
]}

Sacristan, Victor ^{[1
]}

Barbon, Elena ^{[2
]}

Ronzitti, Giuseppe ^{[2
]}

El Andari, Jihad ^{[3
]}

Tulalamba, Warut ^{[4
]}

Pham, Quang Hong ^{[5
]}

Ruberte, Jesus ^{[6
]}

Vandendriessche, Thierry C. ^{[4
]}

Chuah, Marinee K. L. ^{[7
]}

Grimm, Dirk ^{[3
]}

Mingozzi, Federico ^{[2
]}

Bosch, Fatima ^{[1
]}

机构：

[1] Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy CBATEG, Bellaterra, Spain

[2] INTEGRARE, GENETHON, Evry, France

[3] Univ Heidelberg Hosp, Heidelberg, Germany

[4] Free Univ Brussels VUB, Brussels, Belgium

[5] Free Univ Brussels VUB, Brusels, Belgium

[6] Univ Autonoma Barcelona, Sch Vet Med, Dept Anim Hlth & Anat, Bellaterra, Spain

[7] Free Univ Brussels, VUB, Brussels, Belgium

来源：

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D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

1678

引用

页码：785 / 785

页数：1