Development of a Self-Complementary AAV.U7snRNA Vector for Efficient Dystrophin Exon 53 Skipping

被引：0
|
作者：
Qian, Randolph [1 ]
Foltz, Steven J. [1 ]
Jin, Lan [1 ]
Chen, Ting [1 ]
Qiao, Chunping [1 ]
Elliott, Kirk W. [1 ]
Hafiz, Ikram [1 ]
Yang, Jason [1 ]
Karumuthil-Melethil, Subha [1 ]
Bruder, Joseph T. [1 ]
Danos, Olivier F. [1 ]
Liu, Ye [1 ]
机构：
[1] REGENXBIO, Res Early Dev, Rockville, MD USA
来源：
MOLECULAR THERAPY | 2023年 / 31卷 / 04期
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D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
1565
引用
收藏
页码：736 / 736
页数：1
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