共 10 条
[1]
A state-of-the-art review of tamoxifen as a potential therapeutic for duchenne muscular dystrophy
[J].
Botti, Valeria
;
Menzel, Olivier
;
Staedler, Davide
.
FRONTIERS IN PHARMACOLOGY,
2022, 13

Botti, Valeria
论文数: 0 引用数: 0
h-index: 0
机构:
BLACKSWAN Fdn, RE ACT Discovery Inst, Vuarrens, Switzerland BLACKSWAN Fdn, RE ACT Discovery Inst, Vuarrens, Switzerland

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[2]
Safety and efficacy of tamoxifen in boys with Duchenne muscular dystrophy (TAMDMD): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial
[J].
Henzi, Bettina C.
;
Schmidt, Simone
;
Nagy, Sara
;
Rubino-Nacht, Daniela
;
Schaedelin, Sabine
;
Putananickal, Niveditha
;
Stimpson, Georgia
;
Consortium, North Star
;
Amthor, Helge
;
Childs, Anne-Marie
;
Deconinck, Nicolas
;
de Groot, Imelda
;
Horrocks, Iain
;
Opstal, Saskia Houwen-van
;
Laugel, Vincent
;
Lobato, Mercedes Lopez
;
Garrido, Marcos Madruga
;
Osorio, Andres Nascimento
;
Schara-Schmidt, Ulrike
;
Spinty, Stefan
;
von Moers, Arpad
;
Lawrence, Fiona
;
Hafner, Patricia
;
Dorchies, Olivier M.
;
Fischer, Dirk
.
LANCET NEUROLOGY,
2023, 22 (10)
:890-899

Henzi, Bettina C.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Basel, Univ Childrens Hosp Basel, Div Neuropediat & Dev Med, CH-4056 Basel, Switzerland
Univ Freiburg, Fac Med, Med Ctr, Dept Neuropediat & Muscle Disorders, Freiburg, Germany Univ Basel, Univ Childrens Hosp Basel, Div Neuropediat & Dev Med, CH-4056 Basel, Switzerland

Schmidt, Simone
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Basel, Univ Childrens Hosp Basel, Div Neuropediat & Dev Med, CH-4056 Basel, Switzerland Univ Basel, Univ Childrens Hosp Basel, Div Neuropediat & Dev Med, CH-4056 Basel, Switzerland

Nagy, Sara
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Basel, Univ Hosp Basel, Dept Neurol, Basel, Switzerland Univ Basel, Univ Childrens Hosp Basel, Div Neuropediat & Dev Med, CH-4056 Basel, Switzerland

Rubino-Nacht, Daniela
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Basel, Univ Childrens Hosp Basel, Div Neuropediat & Dev Med, CH-4056 Basel, Switzerland Univ Basel, Univ Childrens Hosp Basel, Div Neuropediat & Dev Med, CH-4056 Basel, Switzerland

Schaedelin, Sabine
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Basel, Dept Clin Res, Basel, Switzerland
Univ Hosp Basel, Basel, Switzerland Univ Basel, Univ Childrens Hosp Basel, Div Neuropediat & Dev Med, CH-4056 Basel, Switzerland

Putananickal, Niveditha
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Basel, Univ Childrens Hosp Basel, Div Neuropediat & Dev Med, CH-4056 Basel, Switzerland Univ Basel, Univ Childrens Hosp Basel, Div Neuropediat & Dev Med, CH-4056 Basel, Switzerland

Stimpson, Georgia
论文数: 0 引用数: 0
h-index: 0
机构:
UCL Great Ormond St Inst Child Hlth, Fac Populat Hlth Sci, Dubowitz Neuromuscular Ctr, Dev Neurosci Res & Teaching Dept, London, England Univ Basel, Univ Childrens Hosp Basel, Div Neuropediat & Dev Med, CH-4056 Basel, Switzerland

Consortium, North Star
论文数: 0 引用数: 0
h-index: 0
机构: Univ Basel, Univ Childrens Hosp Basel, Div Neuropediat & Dev Med, CH-4056 Basel, Switzerland

Amthor, Helge
论文数: 0 引用数: 0
h-index: 0
机构:
Hop Raymond Poincare, AP HP Paris Saclay, Serv Neurol & Reanimat Pediat, Garches, France Univ Basel, Univ Childrens Hosp Basel, Div Neuropediat & Dev Med, CH-4056 Basel, Switzerland

Childs, Anne-Marie
论文数: 0 引用数: 0
h-index: 0
机构:
Leeds Teaching Hosp NHS Trust, Leeds, England Univ Basel, Univ Childrens Hosp Basel, Div Neuropediat & Dev Med, CH-4056 Basel, Switzerland

Deconinck, Nicolas
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Libre Bruxelles, Hop Univ Enfants Reine Fabiola, Dept Paediat Neurol, Brussels, Belgium
Univ Libre Bruxelles, Hop Univ Enfants Reine Fabiola, Neuromuscular Reference Ctr, Brussels, Belgium Univ Basel, Univ Childrens Hosp Basel, Div Neuropediat & Dev Med, CH-4056 Basel, Switzerland

de Groot, Imelda
论文数: 0 引用数: 0
h-index: 0
机构:
Radboud Univ Nijmegen, Med Ctr, Donders Inst Brain Cognit & Behav, Dept Rehabil, Nijmegen, Netherlands Univ Basel, Univ Childrens Hosp Basel, Div Neuropediat & Dev Med, CH-4056 Basel, Switzerland

Horrocks, Iain
论文数: 0 引用数: 0
h-index: 0
机构:
Royal Hosp Children, Glasgow, Scotland Univ Basel, Univ Childrens Hosp Basel, Div Neuropediat & Dev Med, CH-4056 Basel, Switzerland

Opstal, Saskia Houwen-van
论文数: 0 引用数: 0
h-index: 0
机构:
Radboud Univ Nijmegen, Med Ctr, Donders Inst Brain Cognit & Behav, Dept Rehabil, Nijmegen, Netherlands Univ Basel, Univ Childrens Hosp Basel, Div Neuropediat & Dev Med, CH-4056 Basel, Switzerland

Laugel, Vincent
论文数: 0 引用数: 0
h-index: 0
机构:
Strasbourg Univ Hosp, Dept Pediat Neurol, Strasbourg, France Univ Basel, Univ Childrens Hosp Basel, Div Neuropediat & Dev Med, CH-4056 Basel, Switzerland

Lobato, Mercedes Lopez
论文数: 0 引用数: 0
h-index: 0
机构:
Hosp Univ Virgen Rocio, Secc Neurol Pediat, Seville, Spain Univ Basel, Univ Childrens Hosp Basel, Div Neuropediat & Dev Med, CH-4056 Basel, Switzerland

Garrido, Marcos Madruga
论文数: 0 引用数: 0
h-index: 0
机构:
Hosp Univ Virgen Rocio, Secc Neurol Pediat, Seville, Spain Univ Basel, Univ Childrens Hosp Basel, Div Neuropediat & Dev Med, CH-4056 Basel, Switzerland

Osorio, Andres Nascimento
论文数: 0 引用数: 0
h-index: 0
机构:
Hosp St Joan de Deu, Dept Neurol, Neuromuscular Unit, Barcelona, Spain
ISCIII, Ctr Biomed Res Network Rare Dis, Barcelona, Spain Univ Basel, Univ Childrens Hosp Basel, Div Neuropediat & Dev Med, CH-4056 Basel, Switzerland

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Spinty, Stefan
论文数: 0 引用数: 0
h-index: 0
机构:
Alder Hey Childrens Hosp, Liverpool, England Univ Basel, Univ Childrens Hosp Basel, Div Neuropediat & Dev Med, CH-4056 Basel, Switzerland

von Moers, Arpad
论文数: 0 引用数: 0
h-index: 0
机构:
DRK Kliniken Berlin Westend, Dept Pediat, Berlin, Germany Univ Basel, Univ Childrens Hosp Basel, Div Neuropediat & Dev Med, CH-4056 Basel, Switzerland

Lawrence, Fiona
论文数: 0 引用数: 0
h-index: 0
机构:
Duchenne UK, London, England Univ Basel, Univ Childrens Hosp Basel, Div Neuropediat & Dev Med, CH-4056 Basel, Switzerland

Hafner, Patricia
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Basel, Univ Childrens Hosp Basel, Div Neuropediat & Dev Med, CH-4056 Basel, Switzerland Univ Basel, Univ Childrens Hosp Basel, Div Neuropediat & Dev Med, CH-4056 Basel, Switzerland

Dorchies, Olivier M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Geneva, Sch Pharmaceut Sci, Geneva, Switzerland
Univ Geneva, Inst Pharmaceut Sci Western Switzerland, Geneva, Switzerland Univ Basel, Univ Childrens Hosp Basel, Div Neuropediat & Dev Med, CH-4056 Basel, Switzerland

Fischer, Dirk
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Basel, Univ Childrens Hosp Basel, Div Neuropediat & Dev Med, CH-4056 Basel, Switzerland Univ Basel, Univ Childrens Hosp Basel, Div Neuropediat & Dev Med, CH-4056 Basel, Switzerland
[3]
Crowdfunding for neuromuscular disease treatment: the ethical implications
[J].
Livingstone, Angus
;
Servais, Laurent
;
Wilkinson, Dominic J. C.
.
LANCET NEUROLOGY,
2021, 20 (10)
:788-789

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Servais, Laurent
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Oxford, MDUK Oxford Neuromuscular Ctr, Dept Paediat, Oxford, England
Univ Hosp Liege, Dept Paediat, Ctr Neuromuscular Dis, Div Child Neurol Reference, Liege, Belgium Univ Oxford, Med Sch, Oxford, England

Wilkinson, Dominic J. C.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Oxford, Fac Philosophy, Oxford Uehiro Ctr Pract Eth, Oxford, England
John Radcliffe Hosp, Newborn Care Unit, Oxford OX1 1PT, England
Murdoch Childrens Res Inst, Melbourne, Vic, Australia Univ Oxford, Med Sch, Oxford, England
[4]
Emerging therapies for Duchenne muscular dystrophy
[J].
Markati, Theodora
;
Oskoui, Maryam
;
Farrar, Michelle A.
;
Duong, Tina
;
Goemans, Nathalie
;
Servais, Laurent
.
LANCET NEUROLOGY,
2022, 21 (09)
:814-829

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Farrar, Michelle A.
论文数: 0 引用数: 0
h-index: 0
机构:
UNSW Sydney, Sch Clin Med, UNSW Med & Hlth, Discipline Paediat, Sydney, NSW, Australia
Sydney Childrens Hosp, Dept Neurol, Randwick, NSW, Australia Univ Oxford, MDUK Oxford Neuromuscular Ctr, Dept Paediat, Oxford OX3 9DU, England

Duong, Tina
论文数: 0 引用数: 0
h-index: 0
机构:
Stanford Univ, Dept Neurol & Neurol Sci, Stanford, CA 94305 USA Univ Oxford, MDUK Oxford Neuromuscular Ctr, Dept Paediat, Oxford OX3 9DU, England

Goemans, Nathalie
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Hosp Leuven, Dept Pediat Neurol, Leuven, Belgium Univ Oxford, MDUK Oxford Neuromuscular Ctr, Dept Paediat, Oxford OX3 9DU, England

Servais, Laurent
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Oxford, MDUK Oxford Neuromuscular Ctr, Dept Paediat, Oxford OX3 9DU, England
Univ Hosp Liege, Div Child Neurol, Reference Ctr Neuromuscular Dis, Dept Pediat, Liege, Belgium
Univ La Citadelle, Liege, Belgium Univ Oxford, MDUK Oxford Neuromuscular Ctr, Dept Paediat, Oxford OX3 9DU, England
[5]
Lessons Learned from Discontinued Clinical Developments in Duchenne Muscular Dystrophy
[J].
Markati, Theodora
;
De Waele, Liesbeth
;
Schara-Schmidt, Urlike
;
Servais, Laurent
.
FRONTIERS IN PHARMACOLOGY,
2021, 12

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De Waele, Liesbeth
论文数: 0 引用数: 0
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机构:
Katholieke Univ Leuven, Dept Dev & Regenerat, Leuven, Belgium
Univ Hosp Leuven, Dept Paediat Neurol, Leuven, Belgium Univ Oxford, MDUK Oxford Neuromuscular Ctr, Dept Paediat, Oxford, England

Schara-Schmidt, Urlike
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Duisburg Essen, Ctr Neuromuscular Dis, Ctr Translat Neuro & Behav Sci, Dept Pediat Neurol, Essen, Germany Univ Oxford, MDUK Oxford Neuromuscular Ctr, Dept Paediat, Oxford, England

Servais, Laurent
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Oxford, MDUK Oxford Neuromuscular Ctr, Dept Paediat, Oxford, England
Univ Hosp Liege, Ctr Hospitaller Reg References Malad Neuromuscula, Reference Ctr Neuromuscular Dis, Dept Pediat,Div Child Neurol, Liege, Belgium Univ Oxford, MDUK Oxford Neuromuscular Ctr, Dept Paediat, Oxford, England
[6]
Assessment of Systemic Delivery of rAAVrh74.MHCK7.micro-dystrophin in Children With Duchenne Muscular Dystrophy A Nonrandomized Controlled Trial
[J].
Mendell, Jerry R.
;
Sahenk, Zarife
;
Lehman, Kelly
;
Nease, Carrie
;
Lowes, Linda P.
;
Miller, Natalie F.
;
Iammarino, Megan A.
;
Alfano, Lindsay N.
;
Nicholl, Amanda
;
Al-Zaidy, Samiah
;
Lewis, Sarah
;
Church, Kathleen
;
Shell, Richard
;
Cripe, Linda H.
;
Potter, Rachael A.
;
Griffin, Danielle A.
;
Pozsgai, Eric
;
Dugar, Ashish
;
Hogan, Mark
;
Rodino-Klapac, Louise R.
.
JAMA NEUROLOGY,
2020, 77 (09)
:1122-1131

Mendell, Jerry R.
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA
Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA
Ohio State Univ, Dept Neurol, Columbus, OH 43210 USA Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA

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Lehman, Kelly
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA
Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA

Nease, Carrie
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA
Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA

Lowes, Linda P.
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA
Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA
Ohio State Univ, Dept Neurol, Columbus, OH 43210 USA Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA

Miller, Natalie F.
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA

Iammarino, Megan A.
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA

Alfano, Lindsay N.
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA

Nicholl, Amanda
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA

Al-Zaidy, Samiah
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA

Lewis, Sarah
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA
Sarepta Therapeut Inc, 215 First St, Cambridge, MA 02142 USA Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA

Church, Kathleen
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA

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Cripe, Linda H.
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA

Potter, Rachael A.
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA
Sarepta Therapeut Inc, 215 First St, Cambridge, MA 02142 USA Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA

Griffin, Danielle A.
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA
Sarepta Therapeut Inc, 215 First St, Cambridge, MA 02142 USA Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA

Pozsgai, Eric
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA
Sarepta Therapeut Inc, 215 First St, Cambridge, MA 02142 USA Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA

Dugar, Ashish
论文数: 0 引用数: 0
h-index: 0
机构:
Sarepta Therapeut Inc, 215 First St, Cambridge, MA 02142 USA Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA

Hogan, Mark
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Dept Radiol Vasc & Intervent Radiol, Columbus, OH USA Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA

Rodino-Klapac, Louise R.
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA
Sarepta Therapeut Inc, 215 First St, Cambridge, MA 02142 USA
Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA Nationwide Childrens Hosp, Abigail Wexner Res Inst, Ctr Gene Therapy, 700 Childrens Dr, Columbus, OH 43205 USA
[7]
Real-world and natural history data for drug evaluation in Duchenne muscular dystrophy: suitability of the North Star Ambulatory Assessment for comparisons with external controls
[J].
Muntoni, Francesco
;
Signorovitch, James
;
Sajeev, Gautam
;
Goemans, Nathalie
;
Wong, Brenda
;
Tian, Cuixia
;
Mercuri, Eugenio
;
Done, Nicolae
;
Wong, Hallee
;
Moss, Jackson
;
Yao, Zhiwen
;
Ward, Susan J.
;
Manzur, Adnan
;
Servais, Laurent
;
Niks, Erik H.
;
Straub, Volker
;
de Groot, Imelda Jm
;
McDonald, Craig
.
NEUROMUSCULAR DISORDERS,
2022, 32 (04)
:271-283

Muntoni, Francesco
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Dubowitz Neuromuscular Ctr, NIHR Great Ormond St Hosp Biomed Res Ctr, Great Ormond St Inst Child Hlth, London, England
Great Ormond St Hosp Trust, London, England UCL, Dubowitz Neuromuscular Ctr, NIHR Great Ormond St Hosp Biomed Res Ctr, Great Ormond St Inst Child Hlth, London, England

Signorovitch, James
论文数: 0 引用数: 0
h-index: 0
机构:
Anal Grp Inc, Boston, MA 02199 USA
Collaborat Trajectory Anal Project, Cambridge, MA 02142 USA UCL, Dubowitz Neuromuscular Ctr, NIHR Great Ormond St Hosp Biomed Res Ctr, Great Ormond St Inst Child Hlth, London, England

Sajeev, Gautam
论文数: 0 引用数: 0
h-index: 0
机构:
Anal Grp Inc, Boston, MA 02199 USA UCL, Dubowitz Neuromuscular Ctr, NIHR Great Ormond St Hosp Biomed Res Ctr, Great Ormond St Inst Child Hlth, London, England

Goemans, Nathalie
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Hosp Leuven, Child Neurol, Leuven, Belgium UCL, Dubowitz Neuromuscular Ctr, NIHR Great Ormond St Hosp Biomed Res Ctr, Great Ormond St Inst Child Hlth, London, England

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Tian, Cuixia
论文数: 0 引用数: 0
h-index: 0
机构:
Cincinnati Childrens Hosp Med Ctr, Cincinnati, OH 45229 USA
Univ Cincinnati, Coll Med, Cincinnati, OH USA UCL, Dubowitz Neuromuscular Ctr, NIHR Great Ormond St Hosp Biomed Res Ctr, Great Ormond St Inst Child Hlth, London, England

Mercuri, Eugenio
论文数: 0 引用数: 0
h-index: 0
机构:
Catholic Univ, Fdn Policlin Gemelli IRCCS, Dept Pediat Neurol, Rome, Italy UCL, Dubowitz Neuromuscular Ctr, NIHR Great Ormond St Hosp Biomed Res Ctr, Great Ormond St Inst Child Hlth, London, England

Done, Nicolae
论文数: 0 引用数: 0
h-index: 0
机构:
Anal Grp Inc, Boston, MA 02199 USA UCL, Dubowitz Neuromuscular Ctr, NIHR Great Ormond St Hosp Biomed Res Ctr, Great Ormond St Inst Child Hlth, London, England

Wong, Hallee
论文数: 0 引用数: 0
h-index: 0
机构:
Anal Grp Inc, Boston, MA 02199 USA UCL, Dubowitz Neuromuscular Ctr, NIHR Great Ormond St Hosp Biomed Res Ctr, Great Ormond St Inst Child Hlth, London, England

Moss, Jackson
论文数: 0 引用数: 0
h-index: 0
机构:
Anal Grp Inc, Boston, MA 02199 USA UCL, Dubowitz Neuromuscular Ctr, NIHR Great Ormond St Hosp Biomed Res Ctr, Great Ormond St Inst Child Hlth, London, England

Yao, Zhiwen
论文数: 0 引用数: 0
h-index: 0
机构:
Anal Grp Inc, Boston, MA 02199 USA UCL, Dubowitz Neuromuscular Ctr, NIHR Great Ormond St Hosp Biomed Res Ctr, Great Ormond St Inst Child Hlth, London, England

Ward, Susan J.
论文数: 0 引用数: 0
h-index: 0
机构:
Collaborat Trajectory Anal Project, Cambridge, MA 02142 USA UCL, Dubowitz Neuromuscular Ctr, NIHR Great Ormond St Hosp Biomed Res Ctr, Great Ormond St Inst Child Hlth, London, England

Manzur, Adnan
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Dubowitz Neuromuscular Ctr, NIHR Great Ormond St Hosp Biomed Res Ctr, Great Ormond St Inst Child Hlth, London, England
Great Ormond St Hosp Trust, London, England UCL, Dubowitz Neuromuscular Ctr, NIHR Great Ormond St Hosp Biomed Res Ctr, Great Ormond St Inst Child Hlth, London, England

Servais, Laurent
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Oxford, CHU & Univ Liege, UK Oxford Neuromuscular Ctr, Oxford, England
CHU, Div Paediat, Neummuscular Ctr Liege, Liege, Belgium
Univ Liege, Liege, Belgium UCL, Dubowitz Neuromuscular Ctr, NIHR Great Ormond St Hosp Biomed Res Ctr, Great Ormond St Inst Child Hlth, London, England

Niks, Erik H.
论文数: 0 引用数: 0
h-index: 0
机构:
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Straub, Volker
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Newcastle Univ, John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, England UCL, Dubowitz Neuromuscular Ctr, NIHR Great Ormond St Hosp Biomed Res Ctr, Great Ormond St Inst Child Hlth, London, England

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Radboud Univ Nijmegen, Donders Ctr Neurosci, Dept Rehabil, Med Ctr, Nijmegen, Netherlands UCL, Dubowitz Neuromuscular Ctr, NIHR Great Ormond St Hosp Biomed Res Ctr, Great Ormond St Inst Child Hlth, London, England

McDonald, Craig
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Univ Calif Davis, Dept Phys Med & Rehabil & Pediat, Sacramento, CA USA UCL, Dubowitz Neuromuscular Ctr, NIHR Great Ormond St Hosp Biomed Res Ctr, Great Ormond St Inst Child Hlth, London, England
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Univ Oxford, Muscular Dystrophy UK Oxford Neuromuscular Ctr, Dept Paediat, Oxford, England Univ Hosp Liege, Ctr References Malad Neuromusculaires, Dept Pediat, Div Child Neurol, Liege, Belgium

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F Hoffmann La Roche Ltd, Grenzacherstr 124, CH-4070 Basel, Switzerland
Sanofi SA, Basel, Switzerland Univ Hosp Liege, Ctr References Malad Neuromusculaires, Dept Pediat, Div Child Neurol, Liege, Belgium

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F Hoffmann La Roche Ltd, Grenzacherstr 124, CH-4070 Basel, Switzerland Univ Hosp Liege, Ctr References Malad Neuromusculaires, Dept Pediat, Div Child Neurol, Liege, Belgium

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F Hoffmann La Roche Ltd, Grenzacherstr 124, CH-4070 Basel, Switzerland
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Hebrew Univ Jerusalem, Pediat Neurol Unit, Hadassah Med Ctr, Fac Med, Jerusalem, Israel Hebrew Univ Jerusalem, Pediat Pulmonol Unit, Hadassah Med Ctr, Fac Med, Jerusalem, Israel

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