[1] King Faisal Specialist Hosp & Res Ctr, Jeddah, Saudi Arabia
[2] Univ Paris Cite, Necker Enfants Malades Hosp, AP HP, Paris, France
[3] Univ Estadual Campinas, UNICAMP, Hematol & Hemotherapy Ctr, Sch Med, Campinas, Brazil
[4] Univ South Carolina, PRISMA Hlth Comprehens Sickle Cell Dis Program, Sch Med, Greenville, SC USA
[5] Heidelberg Univ, Hopp Childrens Canc Ctr Heidelberg KiTZ, Heidelberg, Germany
[6] Univ Toronto, Hosp Sick Children, Toronto, ON, Canada
[7] Ipsos Healthcare, London, England
[8] Guys & St Thomas NHS Fdn Trust, Evelina London Childrens Hosp, London, England