A meditation on accelerating the development of small molecule medicines targeting RNA

被引：1
作者：
Yang, Xueyi [1 ]
Childs-Disney, Jessica L. [1 ]
Disney, Matthew D. [1 ]
机构：
[1] Scripps Res Inst, Dept Chem, La Jolla, CA 92037 USA
来源：
EXPERT OPINION ON DRUG DISCOVERY | 2023年 / 18卷 / 02期
基金：
美国国家卫生研究院;
关键词：
Drug design; genetically defined disease; precision medicine; RNA; small molecules; SPINAL MUSCULAR-ATROPHY; PHENOTYPE; SEQUENCE; DISEASE; RESCUE;
D O I：
10.1080/17460441.2022.2084528
中图分类号：
R9 [药学];
学科分类号：
1007 ;
摘要：
引用
收藏
页码：115 / 117
页数：3
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