Liver-Directed Lentiviral Gene Therapy for ARC Syndrome

被引：0
|
作者：
Cozmescu, Andrei Claudiu [1 ,2 ]
Touramanidou, Loukia [1 ]
Gurung, Sonam [1 ]
Perocheau, Dany [1 ]
Counsell, John R. [3 ]
Karda, Rajvinder [4 ]
Waddington, Simon [4 ]
Baruteau, Julien [1 ,2 ,5 ]
Gissen, Paul [1 ,2 ,5 ]
机构：
[1] UCL, Great Ormond St Inst Child Hlth, London, England
[2] NIHR Great Ormond St Hosp Biomed Res Ctr, London, England
[3] UCL, Div Surg & Intervent Sci, Res Dept Targeted Intervent, London, England
[4] UCL, EGA Inst Womens Hlth, London, England
[5] Great Ormond St Hosp Children NHS Fdn Trust, Metab Med, London, England
来源：
MOLECULAR THERAPY | 2023年 / 31卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
70
引用
收藏
页码：37 / 37
页数：1
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