Intravital imaging of muscle damage and response to therapy in a model of Pompe disease

被引：3

作者：

Meena, Naresh K. ^{[1
]}

Ng, Yeap ^{[2
,3
]}

Randazzo, Davide ^{[4
]}

Weigert, Roberto ^{[2
,3
,7
]}

Puertollano, Rosa ^{[1
,6
]}

Raben, Nina ^{[1
,5
]}

机构：

[1] NHLBI, Cell & Dev Biol Ctr, NIH, Bethesda, MD USA

[2] NCI, Intravital Microscopy Core, Ctr Canc Res, NIH, Bethesda, MD USA

[3] NCI, Lab Cellular & Mol Biol, Ctr Canc Res, NIH, Bethesda, MD USA

[4] NIAMSD, Light Imaging Sect, Off Sci & Technol, NIH, Bethesda, MD USA

[5] NHLBI, NIH, 50 South Dr,Room 3533, Bethesda, MD 20892 USA

[6] NHLBI, NIH, 50 South Dr,Room 3537, Bethesda, MD 20892 USA

[7] NCI, CCR, NIH, Bldg 37,Room 2050-B, Bethesda, MD 20892 USA

来源：

CLINICAL AND TRANSLATIONAL MEDICINE | 2024年 / 14卷 / 03期

基金：

美国国家卫生研究院;

关键词：

D O I：

10.1002/ctm2.1561

中图分类号：

R73 [肿瘤学];

学科分类号：

100214 ;

摘要：

引用

页数：6

共 10 条

[1] Evaluating Cell Metabolism Through Autofluorescence Imaging of NAD(P)H and FAD [J].

Kolenc, Olivia I. ;

Quinn, Kyle P. .

ANTIOXIDANTS & REDOX SIGNALING, 2019, 30 (06) :875-889

[2] Defects in calcium homeostasis and mitochondria can be reversed in Pompe disease [J].

Lim, Jeong-A ;

Li, Lishu ;

Kakhlon, Or ;

Myerowitz, Rachel ;

Raben, Nina .

AUTOPHAGY, 2015, 11 (02) :385-402

[3] AAV-mediated delivery of secreted acid a-glucosidase with enhanced uptake corrects neuromuscular pathology in Pompe mice [J].

Meena, Naresh K. ;

Randazzo, Davide ;

Raben, Nina ;

Puertollano, Rosa .

JCI INSIGHT, 2023, 8 (16)

[4] Pompe Disease: New Developments in an Old Lysosomal Storage Disorder [J].

Meena, Naresh K. ;

Raben, Nina .

BIOMOLECULES, 2020, 10 (09) :1-19

[5] Enzyme Replacement Therapy Can Reverse Pathogenic Cascade in Pompe Disease [J].

Meena, Naresh Kumar ;

Ralston, Evelyn ;

Raben, Nina ;

Puertollano, Rosa .

MOLECULAR THERAPY-METHODS & CLINICAL DEVELOPMENT, 2020, 18 :199-214

[6] In Vivo Tissue-wide Synchronization of Mitochondrial Metabolic Oscillations [J].

Porat-Shliom, Natalie ;

Chen, Yun ;

Tora, Muhibullah ;

Shitara, Akiko ;

Masedunskas, Andrius ;

Weigert, Roberto .

CELL REPORTS, 2014, 9 (02) :514-521

[7]

Scheele CLGJ, 2022, NAT REV METHOD PRIME, V2, DOI 10.1038/s43586-022-00168-w

[8] Correction of oxidative stress enhances enzyme replacement therapy in Pompe disease [J].

Tarallo, Antonietta ;

Damiano, Carla ;

Strollo, Sandra ;

Minopoli, Nadia ;

Indrieri, Alessia ;

Polishchuk, Elena ;

Zappa, Francesca ;

Nusco, Edoardo ;

Fecarotta, Simona ;

Porto, Caterina ;

Coletta, Marcella ;

Iacono, Roberta ;

Moracci, Marco ;

Polishchuk, Roman ;

Medina, Diego Luis ;

Imbimbo, Paola ;

Monti, Daria Maria ;

De Matteis, Maria Antonietta ;

Parenti, Giancarlo .

EMBO MOLECULAR MEDICINE, 2021, 13 (11)

[9] Imaging cell biology in live animals: Ready for prime time [J].

Weigert, Roberto ;

Porat-Shliom, Natalie ;

Amornphimoltham, Panomwat .

JOURNAL OF CELL BIOLOGY, 2013, 201 (07) :969-979

[10] Improved efficacy of a next-generation ERT in murine Pompe disease [J].

Xu, Su ;

Lun, Yi ;

Frascella, Michelle ;

Garcia, Anadina ;

Soska, Rebecca ;

Nair, Anju ;

Ponery, Abdul S. ;

Schilling, Adriane ;

Feng, Jessie ;

Tuske, Steven ;

Della Valle, Maria Cecilia ;

Martina, Jose A. ;

Ralston, Evelyn ;

Gotschall, Russell ;

Valenzano, Kenneth J. ;

Puertollano, Rosa ;

Do, Hung, V ;

Raben, Nina ;

Khanna, Richie .

JCI INSIGHT, 2019, 4 (05)

← 1 →