LONG-TERM SAFETY AND EFFECTIVENESS OF CANAKINUMAB IN CRYOPYRIN-ASSOCIATED PERIODIC SYNDROMES (CAPS)-4-YEARS DATA FROM THE RELIANCE REGISTRY

被引:0
作者
Kuemmerle-Deschner, J. B. [1 ]
Kortus-Goetze, B. [2 ]
Schuetz, C. [3 ]
Oommen, P. [4 ]
Janda, A. [5 ]
Rech, J. [6 ,7 ,8 ]
Weller-Heinemann, F. [9 ]
Kallinich, T. [10 ,11 ]
Pankow, A. [12 ]
Horneff, G. [13 ]
Foeldvari, I. [14 ]
Wasiliew, P. [1 ]
Borte, M. [15 ]
Fiene, M. [16 ]
Meier, F. [17 ,18 ,19 ]
Krickau, T. [20 ]
Andreica, I. [21 ]
Weber-Arden, J. [22 ]
Blank, N. [23 ]
机构
[1] Univ Hosp Tuebingen, Div Pediat Rheumatol & autoinflammat reference Ct, Dept Pediat, Tubingen, Germany
[2] Univ Hosp Giessen & Marburg, Div Nephrol, Dept Internal Med, Marburg, Germany
[3] Tech Univ Dresden, Univ Hosp Carl Gustav Carus, Dept Paediat, Dresden, Germany
[4] Heinrich Heine Univ Duesseldorf, Fac Med, Dept Pediat Oncol, Ctr Child & Adolescent Hlth, Dusseldorf, Germany
[5] Univ Med Ctr Ulm, Dept Pediat & Adolescent Med, Ulm, Germany
[6] Ctr Rare Dis Erlangen ZSEER, Erlangen, Germany
[7] Deutsch Zentrum Immuntherapie DZI, Erlangen, Germany
[8] Univ Hosp Erlangen, Dept Rheumatol & Immunol, Erlangen, Germany
[9] Prof Hess Childrens Hosp, Div Pediat Rheumatol, Bremen, Germany
[10] Charite Univ Med Berlin, Dept Pediat Resp Med Immunol & Crit Care Med, Berlin, Germany
[11] Deutsch Rheuma Forschungszentrum DRFZ, Inst Leibniz Assoc Berlin, Berlin, Germany
[12] Charite Univ Med Berlin, Dept Rheumatol & Clin Immunol, Berlin, Germany
[13] Asklepios Kinderklin Sankt Augustin, Dept Pediat, St Augustin, Germany
[14] Hamburg Ctr Pediat & Adolescence Rheumatol, Pediat & Adolescence Rheumatol, Hamburg, Germany
[15] Univ Leipzig, Acad Teaching Hosp, Hosp Children & Adolescents, St Georg Hosp, Leipzig, Germany
[16] Rheumatol Ctr Greifswald, Rheumatol, Greifswald, Germany
[17] Fraunhofer Inst Translat Med & Pharmacol ITMP, Translat Med & Pharmacol, Frankfurt, Germany
[18] Goethe Univ Hosp, Frankfurt, Germany
[19] Goethe Univ Frankfurt, Dept Gen Pharmacol & Toxicol, Frankfurt, Germany
[20] Friedrich Alexander Univ Erlangen Nuernberg FAU, Pediat, Erlangen, Germany
[21] Ruhr Univ Bochum, Rheumazentrum Ruhrgebiet, Bochum, Germany
[22] Novartis Pharma GmbH, Immunol, Nurnberg, Germany
[23] Univ Hosp, Div Rheumatol, Dept Internal Med, Heidelberg, Germany
关键词
Real-world evidence; Rare/orphan diseases; Innate immunity;
D O I
10.1136/annrheumdis-2023-eular.6040
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
OP0252
引用
收藏
页码:167 / 167
页数:1
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