EFFECT OF RNAI ON CARDIOMYOPATHY AND POLYNEUROPATHY OUTCOMES IN PATIENTS WITH V122I VARIANT HEREDITARY TRANSTHYRETIN-MEDIATED (HATTR OR ATTRV) AMYLOIDOSIS
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作者:
Sperry, Brett Wesley
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St Lukes Mid Amer Heart Inst, Kansas City, MO USASt Lukes Mid Amer Heart Inst, Kansas City, MO USA
Sperry, Brett Wesley
[1
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Quan, Dianna
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St Lukes Mid Amer Heart Inst, Kansas City, MO USASt Lukes Mid Amer Heart Inst, Kansas City, MO USA
Quan, Dianna
[1
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Mauricio, Elizabeth
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St Lukes Mid Amer Heart Inst, Kansas City, MO USASt Lukes Mid Amer Heart Inst, Kansas City, MO USA
Mauricio, Elizabeth
[1
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Small, Roy S.
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St Lukes Mid Amer Heart Inst, Kansas City, MO USASt Lukes Mid Amer Heart Inst, Kansas City, MO USA
Small, Roy S.
[1
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Ananthasubramaniam, Karthikeyan
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St Lukes Mid Amer Heart Inst, Kansas City, MO USASt Lukes Mid Amer Heart Inst, Kansas City, MO USA
Ananthasubramaniam, Karthikeyan
[1
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Egolum, Ugochukwu Onyibo
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St Lukes Mid Amer Heart Inst, Kansas City, MO USASt Lukes Mid Amer Heart Inst, Kansas City, MO USA
Egolum, Ugochukwu Onyibo
[1
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Roblin, Steven
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St Lukes Mid Amer Heart Inst, Kansas City, MO USASt Lukes Mid Amer Heart Inst, Kansas City, MO USA
Roblin, Steven
[1
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Yureneva, Elena
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St Lukes Mid Amer Heart Inst, Kansas City, MO USASt Lukes Mid Amer Heart Inst, Kansas City, MO USA
Yureneva, Elena
[1
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Chou, Lin-Na
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St Lukes Mid Amer Heart Inst, Kansas City, MO USASt Lukes Mid Amer Heart Inst, Kansas City, MO USA
Chou, Lin-Na
[1
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Jay, Patrick
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St Lukes Mid Amer Heart Inst, Kansas City, MO USASt Lukes Mid Amer Heart Inst, Kansas City, MO USA
Jay, Patrick
[1
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Capocelli, Kelley
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St Lukes Mid Amer Heart Inst, Kansas City, MO USASt Lukes Mid Amer Heart Inst, Kansas City, MO USA
Capocelli, Kelley
[1
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Freimer, Miriam
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St Lukes Mid Amer Heart Inst, Kansas City, MO USASt Lukes Mid Amer Heart Inst, Kansas City, MO USA
Freimer, Miriam
[1
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[1] St Lukes Mid Amer Heart Inst, Kansas City, MO USA
机构:
Univ Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, FranceUniv Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, France
Adams, David
Tournev, Ivailo L.
论文数: 0引用数: 0
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机构:
Med Univ, Univ Hosp Aleksandrovska, Dept Neurol, Clin Nervous Dis, Sofia, Bulgaria
New Bulgarian Univ, Dept Cognit Sci, Sofia, BulgariaUniv Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, France
Tournev, Ivailo L.
Taylor, Mark S.
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机构:
Univ Sydney, Dept Clin Immunol & Allergy, Westmead Hosp, Sydney, NSW, Australia
Univ Sydney, Westmead Clin Sch, Sydney, NSW, AustraliaUniv Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, France
Taylor, Mark S.
Coelho, Teresa
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机构:
Ctr Hosp Univ Porto, Hosp Santo Antonio, Porto, PortugalUniv Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, France
Coelho, Teresa
Plante-Bordeneuve, Violaine
论文数: 0引用数: 0
h-index: 0
机构:
Univ Paris Est Creteil, CHU Henri Mondor, APHP, Neurol Amyloid Network, Creteil, FranceUniv Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, France
Plante-Bordeneuve, Violaine
Berk, John L.
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h-index: 0
机构:
Boston Univ, Boston Med Ctr, Boston, MA USAUniv Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, France
Berk, John L.
Gonzalez-Duarte, Alejandra
论文数: 0引用数: 0
h-index: 0
机构:
Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoUniv Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, France
Gonzalez-Duarte, Alejandra
Gillmore, Julian D.
论文数: 0引用数: 0
h-index: 0
机构:
UCL, Royal Free Hosp, Natl Amyloidosis Ctr, London, EnglandUniv Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, France
Gillmore, Julian D.
Low, Soon-Chai
论文数: 0引用数: 0
h-index: 0
机构:
Univ Malaya, Dept Med, Div Neurol, Med Ctr, Kuala Lumpur, MalaysiaUniv Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, France
Low, Soon-Chai
Sekijima, Yoshiki
论文数: 0引用数: 0
h-index: 0
机构:
Shinshu Univ, Dept Med Neurol & Rheumatol, Sch Med, Matsumoto, Nagano, JapanUniv Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, France
Sekijima, Yoshiki
Obici, Laura
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机构:
IRCCS Fdn Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, ItalyUniv Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, France
Obici, Laura
Chen, Chongshu
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h-index: 0
机构:
Alnylam Pharmaceut, Cambridge, MA USAUniv Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, France
Chen, Chongshu
Badri, Prajakta
论文数: 0引用数: 0
h-index: 0
机构:
Alnylam Pharmaceut, Cambridge, MA USAUniv Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, France
Badri, Prajakta
Arum, Seth M.
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h-index: 0
机构:
Alnylam Pharmaceut, Cambridge, MA USAUniv Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, France
Arum, Seth M.
Vest, John
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h-index: 0
机构:
Alnylam Pharmaceut, Cambridge, MA USAUniv Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, France
Vest, John
Polydefkis, Michael
论文数: 0引用数: 0
h-index: 0
机构:
Johns Hopkins Univ, Sch Med, Dept Neurol, Baltimore, MD 21205 USAUniv Paris Saclay, CHU Bicetre, APHP, Neurol Dept, Le Kremlin Bicetre, France
Polydefkis, Michael
AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS,
2023,
30
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