AAV Gene Therapy for Autosomal Dominant Optic Atrophy Caused by Mutation in the Opa1 Gene

被引：0
作者：
Stupay, Rachel M. [1 ]
Cascone, Alyna [1 ]
Padegimas, Linas [2 ]
Wille, Paul T. [1 ]
Kevany, Brian M. [3 ]
机构：
[1] Abeona Therapeut, Product Dev, Cleveland, OH USA
[2] Forge Biol, Grove City, OH USA
[3] Abeona Therapeut, Cleveland, OH USA
来源：
MOLECULAR THERAPY | 2023年 / 31卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
1478
引用
收藏
页码：696 / 697
页数：2
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