Luspatercept for transfusion-dependent β-thalassemia: time to get real

被引：7
作者：
Musallam, Khaled M. [2 ]
Sheth, Sujit [3 ]
Cappellini, Maria Domenica [4 ]
Kattamis, Antonis [5 ]
Kuo, Kevin H. M. [6 ]
Taher, Ali T. [1 ]
机构：
[1] Amer Univ Beirut, Med Ctr, Dept Internal Med, POB 11-0236, Beirut 11072020, Lebanon
[2] Burjeel Med City, Thalassemia Ctr, Abu Dhabi, U Arab Emirates
[3] Weill Cornell Med, Dept Pediat, Div Hematol & Oncol, New York, NY USA
[4] Univ Milan, Ca Granda Fdn IRCCS Maggiore Policlin Hosp, Dept Clin Sci & Community, Milan, Italy
[5] Natl & Kapodistrian Univ Athens, Dept Pediat 1, Athens, Greece
[6] Univ Toronto, Div Hematol, Toronto, ON, Canada
来源：
THERAPEUTIC ADVANCES IN HEMATOLOGY | 2023年 / 14卷
关键词：
anemia; ineffective erythropoiesis; novel therapy; thalassemia; transfusion; DISEASE;
D O I：
10.1177/20406207231195594
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
引用
收藏
页数：5
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