CRISPR/Cas9 Strategy for Correcting ELANE Mutations and Restoring Neutrophil Differentiation in Severe Congenital Neutropenia: Insights from Patient-Derived iPSCs

被引：0
|
作者：
Rydzynska, Zuzanna [1 ]
Grzela, Dawid [1 ,2 ]
Linder, Monika I. [3 ]
Dobrewa, Weronika [1 ]
Urbanska, Zuzanna [1 ]
Pawlik, Bartlomiej [1 ]
Krzyzanowski, Damian [1 ,2 ]
Mazurek, Maciej [1 ]
Janczar, Szymon [1 ]
Madzio, Joanna [1 ]
Mlynarski, Wojciech [1 ]
机构：
[1] Med Univ Lodz, Dept Pediat Oncol & Hematol, Lodz, Poland
[2] Polish Acad Sci, Inst Med Biol, Lodz, Poland
[3] Ludwig Maximilians Univ Munchen, Dr von Hauner Childrens Hosp, Dept Pediat, Munich, Germany
来源：
BLOOD | 2023年 / 142卷
关键词：
D O I：
10.1182/blood-2023-188759
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
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页数：3
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