SAFETY AND TOLERABILITY CHARACTERIZATION OF MARALIXIBAT IN INFANTS WITH ALGS FROM 2 MONTHS OF AGE: INTERIM RESULTS FROM THE RISE STUDY

被引：0
|
作者：
Gonzales, Emmanuel [1 ,2 ]
Jankowska, Irena [3 ]
Horslen, Simon P. [4 ]
Ekong, Udeme [5 ]
Rosenthal, Philip [6 ]
Sokal, Etienne [7 ]
Lin, Chuan-Hao [8 ]
Garner, Will [9 ]
Elliott, Jilliann [9 ]
Nunes, Tiago [9 ]
Thompson, Richard J. [10 ]
机构：
[1] Univ Paris Saclay, Inserm Umr 1193, Hepatinov, Orsay, France
[2] Univ Paris Saclay, Hop Bicetre, AP HP, Ctr Reference Natl Atresie Voies Biliaires & Chol, Le Kremlin Bicetre, France
[3] Childrens Mem Hlth Inst, Gastroenterol Hepatol Nutr Disorders & Paediat, Warsaw, Poland
[4] UPMC Childrens Hosp Pittsburgh, Pediat, Pittsburgh, PA USA
[5] Medstar Georgetown Univ Hosp, Medstar Georgetown Transplant Inst, Washington, DC USA
[6] Univ Calif San Francisco, Div Pediat Gastroenterol Hepatol & Nutr, Pediat, San Francisco, CA USA
[7] Clin Univ St Luc, Uclouvian, Pediat Hepatol, Brussels, Belgium
[8] Childrens Hosp Angeles, Los Angeles, CA USA
[9] Mirum Pharmaceut Inc, Foster City, CA USA
[10] Kings Coll London, Inst Liver Studies, London, England
来源：
HEPATOLOGY | 2023年 / 77卷 / 05期
关键词：
D O I：
暂无
中图分类号：
R57 [消化系及腹部疾病];
学科分类号：
摘要：
5021
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收藏
页码：E135 / E135
页数：1
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