SAFETY AND TOLERABILITY CHARACTERIZATION OF MARALIXIBAT IN INFANTS WITH ALGS FROM 2 MONTHS OF AGE: INTERIM RESULTS FROM THE RISE STUDY

被引：0

作者：

Gonzales, Emmanuel ^{[1
,2
]}

Jankowska, Irena ^{[3
]}

Horslen, Simon P. ^{[4
]}

Ekong, Udeme ^{[5
]}

Rosenthal, Philip ^{[6
]}

Sokal, Etienne ^{[7
]}

Lin, Chuan-Hao ^{[8
]}

Garner, Will ^{[9
]}

Elliott, Jilliann ^{[9
]}

Nunes, Tiago ^{[9
]}

Thompson, Richard J. ^{[10
]}

机构：

[1] Univ Paris Saclay, Inserm Umr 1193, Hepatinov, Orsay, France

[2] Univ Paris Saclay, Hop Bicetre, AP HP, Ctr Reference Natl Atresie Voies Biliaires & Chol, Le Kremlin Bicetre, France

[3] Childrens Mem Hlth Inst, Gastroenterol Hepatol Nutr Disorders & Paediat, Warsaw, Poland

[4] UPMC Childrens Hosp Pittsburgh, Pediat, Pittsburgh, PA USA

[5] Medstar Georgetown Univ Hosp, Medstar Georgetown Transplant Inst, Washington, DC USA

[6] Univ Calif San Francisco, Div Pediat Gastroenterol Hepatol & Nutr, Pediat, San Francisco, CA USA

[7] Clin Univ St Luc, Uclouvian, Pediat Hepatol, Brussels, Belgium

[8] Childrens Hosp Angeles, Los Angeles, CA USA

[9] Mirum Pharmaceut Inc, Foster City, CA USA

[10] Kings Coll London, Inst Liver Studies, London, England

来源：

HEPATOLOGY | 2023年 / 77卷 / 05期

关键词：

D O I：

暂无

中图分类号：

R57 [消化系及腹部疾病];

学科分类号：

摘要：

5021

引用

页码：E135 / E135

页数：1

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