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SAFETY AND TOLERABILITY CHARACTERIZATION OF MARALIXIBAT IN INFANTS WITH ALGS FROM 2 MONTHS OF AGE: INTERIM RESULTS FROM THE RISE STUDY
被引:0
|作者:
Gonzales, Emmanuel
[1
,2
]
Jankowska, Irena
[3
]
Horslen, Simon P.
[4
]
Ekong, Udeme
[5
]
Rosenthal, Philip
[6
]
Sokal, Etienne
[7
]
Lin, Chuan-Hao
[8
]
Garner, Will
[9
]
Elliott, Jilliann
[9
]
Nunes, Tiago
[9
]
Thompson, Richard J.
[10
]
机构:
[1] Univ Paris Saclay, Inserm Umr 1193, Hepatinov, Orsay, France
[2] Univ Paris Saclay, Hop Bicetre, AP HP, Ctr Reference Natl Atresie Voies Biliaires & Chol, Le Kremlin Bicetre, France
[3] Childrens Mem Hlth Inst, Gastroenterol Hepatol Nutr Disorders & Paediat, Warsaw, Poland
[4] UPMC Childrens Hosp Pittsburgh, Pediat, Pittsburgh, PA USA
[5] Medstar Georgetown Univ Hosp, Medstar Georgetown Transplant Inst, Washington, DC USA
[6] Univ Calif San Francisco, Div Pediat Gastroenterol Hepatol & Nutr, Pediat, San Francisco, CA USA
[7] Clin Univ St Luc, Uclouvian, Pediat Hepatol, Brussels, Belgium
[8] Childrens Hosp Angeles, Los Angeles, CA USA
[9] Mirum Pharmaceut Inc, Foster City, CA USA
[10] Kings Coll London, Inst Liver Studies, London, England
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D O I:
暂无
中图分类号:
R57 [消化系及腹部疾病];
学科分类号:
摘要:
5021
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页码:E135 / E135
页数:1
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