Personalized CFTR modulator therapy for G85E and N1303K homozygous patients with cystic fibrosis

被引：0
|
作者：
Eva, Steinke [1 ,2 ,3 ,4 ]
Simon, Graeber Y. [1 ,2 ,3 ,4 ]
Anita, Balazs [1 ,2 ,3 ]
Niklas, Ziegahn [1 ,2 ,3 ]
Tihomir, Rubil [1 ,2 ,3 ]
Linus, Piehler [1 ,2 ]
Marika, Drescher [1 ,2 ,3 ]
Constanze, Vitzthum [1 ,2 ,3 ]
Kathrin, Seidel [1 ,2 ,3 ]
Alexander, Rohrbach [1 ,2 ,3 ]
Julia, Duerr [1 ,2 ]
Marcus, Mall A. [1 ,2 ,3 ,4 ]
Mirjam, Stahl [1 ,2 ,3 ,4 ]
机构：
[1] Charite Univ Med Berlin, Dept Pediat Resp Med Immunol & Crit Care Med, Berlin, Germany
[2] Cyst Fibrosis Ctr, Berlin, Germany
[3] German Ctr Lung Res DZL, Associated partner site, Berlin, Germany
[4] Berlin Inst Hlth Charite, Berlin, Germany
来源：
KLINISCHE PADIATRIE | 2023年 / 235卷 / 02期
关键词：
D O I：
10.1055/s-0043-1761542
中图分类号：
R72 [儿科学];
学科分类号：
100202 ;
摘要：
P32
引用
收藏
页码：119 / 119
页数：1
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