[1] St Jude Childrens Res Hosp, Memphis, TN USA
[2] TriStar Centennial, Sarah Cannon Res Inst, Childrens Hosp, Nashville, TN USA
[3] Columbia Univ, Div Hematol Oncol, Dept Med, New York, NY USA
[4] Vertex Pharmaceut, Boston, MA USA
[5] Childrens Hosp Philadelphia, Div Oncol, Philadelphia, PA USA