CRISPR-Cas9-mediated exon skipping as a cardioprotective strategy in Duchenne muscular dystrophy

被引：2

作者：

Wilton-Clark, Harry ^{[1
]}

Yokota, Toshifumi ^{[1
]}

机构：

[1] Univ Alberta, Dept Med Genet, Edmonton, AB, Canada

来源：

MOLECULAR THERAPY-METHODS & CLINICAL DEVELOPMENT | 2023年 / 30卷

关键词：

D O I：

10.1016/j.omtm.2023.08.013

中图分类号：

R-3 [医学研究方法]; R3 [基础医学];

学科分类号：

1001 ;

摘要：

引用

页码：500 / 501

页数：2

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