CD19-targeted CAR T cells in refractory antisynthetase syndrome

被引:117
作者
Mueller, Fabian [1 ,2 ]
Boeltz, Sebastian [2 ,3 ]
Knitza, Johannes [2 ,3 ]
Aigner, Michael [1 ,2 ]
Voelkl, Simon [1 ,2 ]
Kharboutli, Soraya [1 ,2 ]
Reimann, Hannah [1 ,2 ]
Taubmann, Jule [2 ,3 ]
Kretschmann, Sascha [1 ,2 ]
Roesler, Wolf [1 ,2 ]
Manger, Bernhard [2 ,3 ]
Wacker, Jochen [2 ,3 ]
Mougiakakos, Dimitrios [7 ]
Jabari, Samir [4 ]
Schroeder, Rolf [4 ]
Uder, Michael [5 ,6 ]
Roemer, Frank [5 ,6 ]
Kroenke, Gerhard [2 ,3 ]
Mackensen, Andreas [1 ,2 ]
Schett, Georg [2 ,3 ]
机构
[1] Friedrich Alexander Univ Erlangen Nurnberg, Dept Internal Med 5 Hematol & Oncol, D-91054 Erlangen, Germany
[2] Friedrich Alexander Univ Erlangen Nurnberg, Deutsch Zentrum Immuntherapie, D-91054 Erlangen, Germany
[3] Friedrich Alexander Univ Erlangen Nurnberg, Dept Internal Med 3 Rheumatol & Immunol, D-91054 Erlangen, Germany
[4] Friedrich Alexander Univ Erlangen Nurnberg, Inst Neuropathol, D-91054 Erlangen, Germany
[5] Friedrich Alexander Univ Erlangen Nurnberg, Inst Radiol, D-91054 Erlangen, Germany
[6] Univ Klinikum Erlangen, D-91054 Erlangen, Germany
[7] Otto von Guericke Univ, Dept Hematol & Oncol, Magdeburg, Germany
基金
英国医学研究理事会; 澳大利亚国家健康与医学研究理事会;
关键词
D O I
10.1016/S0140-6736(23)00023-5
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
引用
收藏
页码:815 / 818
页数:4
相关论文
共 9 条
  • [1] Toxicities of chimeric antigen receptor T cells: recognition and management
    Brudno, Jennifer N.
    Kochenderfer, James N.
    [J]. BLOOD, 2016, 127 (26) : 3321 - 3330
  • [2] Influence of Antisynthetase Antibodies Specificities on Antisynthetase Syndrome Clinical Spectrum Time Course
    Cavagna, Lorenzo
    Trallero-Araguas, Ernesto
    Meloni, Federica
    Cavazzana, Ilaria
    Rojas-Serrano, Jorge
    Feist, Eugen
    Zanframundo, Giovanni
    Morandi, Valentina
    Meyer, Alain
    Pereira da Silva, Jose Antonio
    Matos Costa, Carlo Jorge
    Molberg, Oyvind
    Andersson, Helena
    Codullo, Veronica
    Mosca, Marta
    Barsotti, Simone
    Neri, Rossella
    Scire, Carlo
    Govoni, Marcello
    Furini, Federica
    Javier Lopez-Longo, Francisco
    Martinez-Barrio, Julia
    Schneider, Udo
    Lorenz, Hanns-Martin
    Doria, Andrea
    Ghirardello, Anna
    Ortego-Centeno, Norberto
    Confalonieri, Marco
    Tomietto, Paola
    Pipitone, Nicolo
    Rodriguez Cambron, Ana Belen
    Blazquez Canamero, Maria Angeles
    Voll, Reinhard Edmund
    Wendel, Sarah
    Scarpato, Salvatore
    Maurier, Francois
    Limonta, Massimiliano
    Colombelli, Paolo
    Giannini, Margherita
    Geny, Bernard
    Arrigoni, Eugenio
    Bravi, Elena
    Migliorini, Paola
    Mathieu, Alessandro
    Piga, Matteo
    Drott, Ulrich
    Delbrueck, Christiane
    Bauhammer, Jutta
    Cagnotto, Giovanni
    Vancheri, Carlo
    [J]. JOURNAL OF CLINICAL MEDICINE, 2019, 8 (11)
  • [3] Aminoacyl-tRNA Synthetases: On Anti-Synthetase Syndrome and Beyond
    Galindo-Feria, Angeles S.
    Notarnicola, Antonella
    Lundberg, Ingrid E.
    Horuluoglu, Begum
    [J]. FRONTIERS IN IMMUNOLOGY, 2022, 13
  • [4] Idiopathic inflammatory myopathies
    Lundberg, Ingrid E.
    Fujimoto, Manabu
    Vencovsky, Jiri
    Aggarwal, Rohit
    Holmqvist, Marie
    Christopher-Stine, Lisa
    Mammen, Andrew L.
    Miller, Frederick W.
    [J]. NATURE REVIEWS DISEASE PRIMERS, 2021, 7 (01)
  • [5] CD19 CAR T cell therapy effective for systemic lupus erythematosus
    Gelfand, J.
    [J]. JOURNAL OF INVESTIGATIVE DERMATOLOGY, 2023, 143 (01) : 4 - 4
  • [6] CD19-Targeted CAR T Cells in Refractory Systemic Lupus Erythematosus
    Mougiakakos, Dimitrios
    Kroenke, Gerhard
    Voelkl, Simon
    Kretschmann, Sascha
    Aigner, Michael
    Kharboutli, Soraya
    Boeltz, Sebastian
    Manger, Bernhard
    Mackensen, Andreas
    Schett, Georg
    [J]. NEW ENGLAND JOURNAL OF MEDICINE, 2021, 385 (06) : 567 - 569
  • [7] Rituximab in the Treatment of Refractory Adult and Juvenile Dermatomyositis and Adult Polymyositis A Randomized, Placebo-Phase Trial
    Oddis, Chester V.
    Reed, Ann M.
    Aggarwal, Rohit
    Rider, Lisa G.
    Ascherman, Dana P.
    Levesque, Marc C.
    Barohn, Richard J.
    Feldman, Brian M.
    Harris-Love, Michael O.
    Koontz, Diane C.
    Fertig, Noreen
    Kelley, Stephanie S.
    Pryber, Sherrie L.
    Miller, Frederick W.
    Rockette, Howard E.
    [J]. ARTHRITIS AND RHEUMATISM, 2013, 65 (02): : 314 - 324
  • [8] Oddis CV., 2022, ACR OPEN RHEUMATOL, V4, P983, DOI [10.1002/acr2.11493, DOI 10.1002/ACR2.11493]
  • [9] Skeletal muscle provides the immunological micro-milieu for specific plasma cells in anti-synthetase syndrome-associated myositis
    Preusse, Corinna
    Paesler, Barbara
    Nelke, Christopher
    Cengiz, Derya
    Muentefering, Thomas
    Roos, Andreas
    Amelin, Damien
    Allenbach, Yves
    Uruha, Akinori
    Dittmayer, Carsten
    Hentschel, Andreas
    Pawlitzki, Marc
    Hoffmann, Sarah
    Timm, Sara
    Louis, Sarah Leonard
    Dengler, Nora F.
    Wiendl, Heinz
    Lunemann, Jan D.
    Sickmann, Albert
    Hervier, Baptiste
    Meuth, Sven G.
    Schneider, Udo
    Schaenzer, Anne
    Krause, Sabine
    Tomaras, Stylianos
    Feist, Eugen
    Hasseli, Rebecca
    Goebel, Hans-Hilmar
    Gallay, Laure
    Streichenberger, Nathalie
    Benveniste, Olivier
    Stenzel, Werner
    Ruck, Tobias
    [J]. ACTA NEUROPATHOLOGICA, 2022, 144 (02) : 353 - 372