ASO drug Qalsody (tofersen) targets amyotrophic lateral sclerosis

被引:9
作者
Jin, Jing [1 ]
Zhong, Xiao-bo [1 ]
机构
[1] Univ Connecticut, Sch Pharm, Dept Pharmaceut Sci, Storrs, CT 06269 USA
基金
美国国家卫生研究院;
关键词
ANTISENSE OLIGONUCLEOTIDE TOFERSEN; TRIAL;
D O I
10.1016/j.tips.2023.08.008
中图分类号
R9 [药学];
学科分类号
1007 ;
摘要
引用
收藏
页码:1043 / 1044
页数:2
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