Long-term maintenance of response and improved liver health with maralixibat in patients with progressive familial intrahepatic cholestasis (PFIC): data from the MARCH-ON study

被引：0

作者：

Miethke, Alexander ^{[1
]}

Moukarzel, Adib ^{[2
]}

Porta, Gilda ^{[3
]}

Esquer, Joshue Covarrubias ^{[4
]}

Czubkowski, Piotr ^{[5
]}

Ordonez, Felipe ^{[6
]}

Candusso, Manila ^{[7
]}

Aqul, Amal A. ^{[8
]}

Squires, Robert H. ^{[9
]}

Sokal, Etienne ^{[10
]}

D'Agostino, Daniel ^{[11
]}

Baumann, Ulrich ^{[12
]}

D'Antiga, Lorenzo ^{[13
]}

Kasi, Nagraj ^{[14
]}

Laborde, Nolwenn ^{[15
]}

Arikan, Cigdem ^{[16
]}

Lin, Chuan-Hao ^{[17
]}

Gilmour, Susan ^{[18
]}

Mittal, Naveen ^{[19
]}

Chiou, Fang Kuan ^{[20
]}

Horslen, Simon P.

Huber, Wolf-Dietrich ^{[21
]}

Nunes, Tiago ^{[22
]}

Lascau, Anamaria ^{[22
]}

Longpre, Lara ^{[22
]}

Mogul, Douglas ^{[22
]}

Aguilar, Raul ^{[22
]}

Vig, Pamela ^{[22
]}

Hupertz, Vera ^{[23
]}

Gonzalez-Peralta, Regino ^{[24
]}

Ekong, Udeme ^{[25
]}

Hartley, Jane ^{[26
]}

Laverdure, Noemie ^{[27
]}

Ovchinsky, Nadia ^{[28
]}

Thompson, Richard ^{[29
]}

机构：

[1] Cincinnati Childrens Hosp Med Ctr, Cincinnati, OH 45229 USA

[2] St Joseph Univ Hosp, Hotel Dieu France, Beirut, Lebanon

[3] Hosp Sirio Libanes, Sao Paulo, Brazil

[4] Nois Mexico SA CV, Guadalajara, Jalisco, Mexico

[5] Childrens Mem Hlth Inst Gastroenterol, Nutr Disorders & Pediat, Warsaw, Poland

[6] Cardioinfantil Fdn Lacardio, Bogota, Colombia

[7] Osped Pediat Bambino Gesu Irccs, Lazio, Italy

[8] Univ Texas Southwestern Med Ctr Dallas, Dallas, TX USA

[9] Childrens Hosp Pittsburgh, UPMC, Pediat, Pittsburgh, PA USA

[10] Uclouvian, Clin Univ St Luc, Pediat Hepatol, Brussels, Belgium

[11] Hosp Italiano Buenos Aires, Buenos Aires, DF, Argentina

[12] Hannover Med Sch, Pediat Gastroenterol & Hepatol, Hannover, Germany

[13] Hosp Papa Giovanni XXIII, Paediat Hepatol Gastroenterol & Transplantat, Bergamo, Italy

[14] Med Univ South Carolina, Charleston, SC USA

[15] Hop Enfants CHU Toulouse, Toulouse, France

[16] Koc Univ, Sch Med, Istanbul, Turkiye

[17] Childrens Hosp Los Angeles, Los Angeles, CA USA

[18] Univ Alberta, Pediat, Edmonton, AB, Canada

[19] Univ Texas Hlth Sci Ctr San Antonio, San Antonio, TX USA

[20] KK Womens & Childrens Hosp, Singapore, Singapore

[21] Med Univ Vienna, Vienna, Austria

[22] Mirum Pharmaceut Inc, Foster City, CA USA

[23] Cleveland Clin Childrens, Cleveland, OH USA

[24] AdventHlth Children & AdventHlth Transplant Inst, Orlando, FL USA

[25] Medstar Georgetown Univ Hosp, Medstar Georgetown Transplant Inst, Washington, DC USA

[26] Birmingham Women & Childrens Hosp, Birmingham, W Midlands, England

[27] Hosp Civils Lyon, Pediat Hepato Gastroenterol & Nutr Unit, Hop Femme Mere Enfant, Lyon, France

[28] NYU, Grossman Sch Med, New York, NY USA

[29] Kings Coll London, Inst Liver Studies, London, England

来源：

JOURNAL OF HEPATOLOGY | 2023年 / 78卷

关键词：

D O I：

暂无

中图分类号：

R57 [消化系及腹部疾病];

学科分类号：

摘要：

LBP-35

引用

页码：S123 / S123

页数：1