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Efficacy and Safety of a Single Dose of Exagamglogene Autotemcel for Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease
被引:0
作者:
Frangoul, Haydar
[1
]
Locatelli, Franco
[2
]
Corbacioglu, Selim
[3
]
De La Fuente, Josu
[4
]
Wall, Donna
[5
]
Cappellini, Maria Domenica
[6
]
de Montalembert, Mariane
[7
]
Kattamis, Antonis
[8
]
Lobitz, Stephan
[9
]
Rondelli, Damiano
[10
]
Sheth, Sujit
[11
]
Steinberg, Martin
[12
]
Walters, Mark
[13
]
Bobruff, Yael
[14
]
Simard, Chris
[14
]
Song, Yang
[14
]
Zhang, Lanju
[14
]
Sharma, Anjali
[15
]
Imren, Suzan
[14
]
Hobbs, Bill
[14
]
Grupp, Stephan A.
[16
]
机构:
[1] Childrens Hosp TriStar Centennial, Nashville, TN USA
[2] Uni Rome, Rome, Italy
[3] Uni Regensburg, Regensburg, Germany
[4] Imperial Coll London, St Albans, England
[5] Hosp Sick Children, Toronto, ON, Canada
[6] Uni Milan, Milan, Italy
[7] Uni Paris, Paris, France
[8] Uni Athens, Athens, Greece
[9] Gemeinschaftsklinikum Mittelrhein, Koblenz, Germany
[10] Uni Ill Chicago, Chicago, IL USA
[11] Weill Cornell Med, New York, NY USA
[12] BU Sch Med, Boston, MA USA
[13] UCSF Benioff Childrens Hosp, Oakland, CA USA
[14] Vertex Pharmaceut, Boston, MA USA
[15] CRISPR Therapeut, Cambridge, MA USA
[16] Uni Penn, Perelman Sch Med, Philadelphia, PA USA
关键词:
D O I:
暂无
中图分类号:
Q81 [生物工程学(生物技术)];
Q93 [微生物学];
学科分类号:
071005 ;
0836 ;
090102 ;
100705 ;
摘要:
1
引用
收藏
页码:1 / 1
页数:1
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