In Vivo Genetic Eye Disease Correction Using Split AAV-Mediated Adenine Base Editing

被引：0
作者：
Sullivan, Jack [1 ]
Muller, Alissa [2 ,3 ]
Schwarzer, Wibke [2 ,3 ]
Wang, Mantian [2 ,3 ]
Park-Windhol, Cindy [1 ]
Hasler, Pascal [3 ]
Moreau, Pierre-Henri [4 ]
Azoulay, Thierry [5 ]
Janeschitz-Kriegl, Lucas [2 ,3 ]
Szabo, Arnold [6 ]
Scholl, Hendrik P. N. [2 ,3 ]
Roska, Botond [2 ,3 ]
Gyorgy, Bence [2 ,3 ]
Bryson, David I. [1 ]
Ciaramella, Giuseppe [1 ]
机构：
[1] Beam Therapeut, Cambridge, MA USA
[2] Inst Mol & Clin Ophthalmol Basel, Basel, Switzerland
[3] Univ Basel, Dept Ophthalmol, Basel, Switzerland
[4] Univ Strasbourg, SILABE, Niederhausbergen, France
[5] Clin Vet Agoravet, Strasbourg, France
[6] Semmelweis Univ, Dept Anat, Budapest, Hungary
来源：
MOLECULAR THERAPY | 2023年 / 31卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
308
引用
收藏
页码：168 / 168
页数：1
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