共 50 条
- [41] CRISPR-Cas9-mediated base-editing screening in mice identifies DND1 amino acids that are critical for primordial germ cell developmentNATURE CELL BIOLOGY, 2018, 20 (11) : 1315 - +Li, Qing论文数: 0 引用数: 0 h-index: 0机构: Univ Chinese Acad Sci, Chinese Acad Sci, Shanghai Inst Biochem & Cell Biol,CAS Ctr Excelle, State Key Lab Cell Biol,Shanghai Key Lab Mol Andr, Shanghai, Peoples R China Univ Chinese Acad Sci, Chinese Acad Sci, Shanghai Inst Biochem & Cell Biol,CAS Ctr Excelle, State Key Lab Cell Biol,Shanghai Key Lab Mol Andr, Shanghai, Peoples R ChinaLi, Yanjing论文数: 0 引用数: 0 h-index: 0机构: Univ Chinese Acad Sci, Chinese Acad Sci,Shanghai Sci Res Ctr, Shanghai Inst Biochem & Cell Biol,Natl Ctr Prot S, CAS Ctr Excellence Mol Cell Sci,State Key Lab Mol, Shanghai, Peoples R China Univ Chinese Acad Sci, Chinese Acad Sci, Shanghai Inst Biochem & Cell Biol,CAS Ctr Excelle, State Key Lab Cell Biol,Shanghai Key Lab Mol Andr, Shanghai, Peoples R ChinaYang, Suming论文数: 0 引用数: 0 h-index: 0机构: Univ Chinese Acad Sci, Chinese Acad Sci, Shanghai Inst Biochem & Cell Biol,CAS Ctr Excelle, State Key Lab Cell Biol,Shanghai Key Lab Mol Andr, Shanghai, Peoples R China Univ Chinese Acad Sci, Chinese Acad Sci, Shanghai Inst Biochem & Cell Biol,CAS Ctr Excelle, State Key Lab Cell Biol,Shanghai Key Lab Mol Andr, Shanghai, Peoples R ChinaHuang, Shuo论文数: 0 引用数: 0 h-index: 0机构: Shanghai Tech Univ, Sch Life Sci & Technol, Shanghai, Peoples R China Univ Chinese Acad Sci, Chinese Acad Sci, Shanghai Inst Biochem & Cell Biol,CAS Ctr Excelle, State Key Lab Cell Biol,Shanghai Key Lab Mol Andr, Shanghai, Peoples R ChinaYan, Meng论文数: 0 引用数: 0 h-index: 0机构: Univ Chinese Acad Sci, Chinese Acad Sci, Shanghai Inst Biochem & Cell Biol,CAS Ctr Excelle, State Key Lab Cell Biol,Shanghai Key Lab Mol Andr, Shanghai, Peoples R China Univ Chinese Acad Sci, Chinese Acad Sci, Shanghai Inst Biochem & Cell Biol,CAS Ctr Excelle, State Key Lab Cell Biol,Shanghai Key Lab Mol Andr, Shanghai, Peoples R ChinaDing, Yifu论文数: 0 引用数: 0 h-index: 0机构: Univ Chinese Acad Sci, Chinese Acad Sci, Shanghai Inst Biochem & Cell Biol,CAS Ctr Excelle, State Key Lab Cell Biol,Shanghai Key Lab Mol Andr, Shanghai, Peoples R China Univ Chinese Acad Sci, Chinese Acad Sci, Shanghai Inst Biochem & Cell Biol,CAS Ctr Excelle, State Key Lab Cell Biol,Shanghai Key Lab Mol Andr, Shanghai, Peoples R ChinaTang, Wei论文数: 0 引用数: 0 h-index: 0机构: Univ Chinese Acad Sci, Shanghai Inst Biochem & Cell Biol, Chinese Acad Sci, Anim Core Facil, Shanghai, Peoples R China Univ Chinese Acad Sci, Chinese Acad Sci, Shanghai Inst Biochem & Cell Biol,CAS Ctr Excelle, State Key Lab Cell Biol,Shanghai Key Lab Mol Andr, Shanghai, Peoples R ChinaLou, Xiwen论文数: 0 引用数: 0 h-index: 0机构: Univ Chinese Acad Sci, Chinese Acad Sci,Shanghai Sci Res Ctr, Shanghai Inst Biochem & Cell Biol,Natl Ctr Prot S, CAS Ctr Excellence Mol Cell Sci,State Key Lab Mol, Shanghai, Peoples R China Univ Chinese Acad Sci, Chinese Acad Sci, Shanghai Inst Biochem & Cell Biol,CAS Ctr Excelle, State Key Lab Cell Biol,Shanghai Key Lab Mol Andr, Shanghai, Peoples R ChinaYin, Qi论文数: 0 引用数: 0 h-index: 0机构: Univ Chinese Acad Sci, Chinese Acad Sci, Shanghai Inst Biochem & Cell Biol,CAS Ctr Excelle, State Key Lab Cell Biol,Shanghai Key Lab Mol Andr, Shanghai, Peoples R China Univ Chinese Acad Sci, Chinese Acad Sci, Shanghai Inst Biochem & Cell Biol,CAS Ctr Excelle, State Key Lab Cell Biol,Shanghai Key Lab Mol Andr, Shanghai, Peoples R ChinaSun, Zhanfei论文数: 0 引用数: 0 h-index: 0机构: Shanghai Tech Univ, Sch Life Sci & Technol, Shanghai, Peoples R China Univ Chinese Acad Sci, Chinese Acad Sci, Shanghai Inst Biochem & Cell Biol,CAS Ctr Excelle, State Key Lab Cell Biol,Shanghai Key Lab Mol Andr, Shanghai, Peoples R ChinaLu, Lei论文数: 0 引用数: 0 h-index: 0机构: Univ Chinese Acad Sci, Chinese Acad Sci, Shanghai Inst Biochem & Cell Biol,CAS Ctr Excelle, State Key Lab Cell Biol,Shanghai Key Lab Mol Andr, Shanghai, Peoples R China Fudan Univ, Inst Reprod & Dev, Hosp & Inst Obstet & Gynecol,Sch Life Sci, State Key Lab Genet Engn,Collaborat Innovat Ctr G, Shanghai, Peoples R China Univ Chinese Acad Sci, Chinese Acad Sci, Shanghai Inst Biochem & Cell Biol,CAS Ctr Excelle, State Key Lab Cell Biol,Shanghai Key Lab Mol Andr, Shanghai, Peoples R ChinaShi, Huijuan论文数: 0 引用数: 0 h-index: 0机构: Shanghai Inst Planned Parenthood Res, Natl Populat & Family Planning Comm, Key Lab Contracept Drugs & Devices, Shanghai, Peoples R China Univ Chinese Acad Sci, Chinese Acad Sci, Shanghai Inst Biochem & Cell Biol,CAS Ctr Excelle, State Key Lab Cell Biol,Shanghai Key Lab Mol Andr, Shanghai, Peoples R ChinaWang, Hongyan论文数: 0 引用数: 0 h-index: 0机构: Fudan Univ, Inst Reprod & Dev, Hosp & Inst Obstet & Gynecol,Sch Life Sci, State Key Lab Genet Engn,Collaborat Innovat Ctr G, Shanghai, Peoples R China Univ Chinese Acad Sci, Chinese Acad Sci, Shanghai Inst Biochem & Cell Biol,CAS Ctr Excelle, State Key Lab Cell Biol,Shanghai Key Lab Mol Andr, Shanghai, Peoples R ChinaChen, Yong论文数: 0 引用数: 0 h-index: 0机构: Univ Chinese Acad Sci, Chinese Acad Sci,Shanghai Sci Res Ctr, Shanghai Inst Biochem & Cell Biol,Natl Ctr Prot S, CAS Ctr Excellence Mol Cell Sci,State Key Lab Mol, Shanghai, Peoples R China Univ Chinese Acad Sci, Chinese Acad Sci, Shanghai Inst Biochem & Cell Biol,CAS Ctr Excelle, State Key Lab Cell Biol,Shanghai Key Lab Mol Andr, Shanghai, Peoples R ChinaLi, Jinsong论文数: 0 引用数: 0 h-index: 0机构: Univ Chinese Acad Sci, Chinese Acad Sci, Shanghai Inst Biochem & Cell Biol,CAS Ctr Excelle, State Key Lab Cell Biol,Shanghai Key Lab Mol Andr, Shanghai, Peoples R China Shanghai Tech Univ, Sch Life Sci & Technol, Shanghai, Peoples R China Univ Chinese Acad Sci, Chinese Acad Sci, Shanghai Inst Biochem & Cell Biol,CAS Ctr Excelle, State Key Lab Cell Biol,Shanghai Key Lab Mol Andr, Shanghai, Peoples R China
- [42] The pAblo<bold><middle dot></bold>pCasso self-curing vector toolset for unconstrained cytidine and adenine base-editing in Gram-negative bacteriaNUCLEIC ACIDS RESEARCH, 2024, 52 (04) : E19Kozaeva, Ekaterina论文数: 0 引用数: 0 h-index: 0机构: Tech Univ Denmark, Novo Nord Fdn Ctr Biosustainabil, DK-2800 Lyngby, Denmark Tech Univ Denmark, Novo Nord Fdn Ctr Biosustainabil, DK-2800 Lyngby, DenmarkNielsen, Zacharias S.论文数: 0 引用数: 0 h-index: 0机构: Tech Univ Denmark, Novo Nord Fdn Ctr Biosustainabil, DK-2800 Lyngby, Denmark Tech Univ Denmark, Novo Nord Fdn Ctr Biosustainabil, DK-2800 Lyngby, DenmarkNieto-Dominguez, Manuel论文数: 0 引用数: 0 h-index: 0机构: Tech Univ Denmark, Novo Nord Fdn Ctr Biosustainabil, DK-2800 Lyngby, Denmark Tech Univ Denmark, Novo Nord Fdn Ctr Biosustainabil, DK-2800 Lyngby, DenmarkNikel, Pablo, I论文数: 0 引用数: 0 h-index: 0机构: Tech Univ Denmark, Novo Nord Fdn Ctr Biosustainabil, DK-2800 Lyngby, Denmark Tech Univ Denmark, Novo Nord Fdn Ctr Biosustainabil, DK-2800 Lyngby, Denmark
- [43] SPLICER: a highly efficient base editing toolbox that enables in vivo therapeutic exon skippingNATURE COMMUNICATIONS, 2024, 15 (01)Miskalis, Angelo论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Grainger Coll Engn, Dept Bioengn, Urbana, IL 61801 USA Univ Illinois, Grainger Coll Engn, Dept Bioengn, Urbana, IL 61801 USAShirguppe, Shraddha论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Grainger Coll Engn, Dept Bioengn, Urbana, IL 61801 USA Univ Illinois, Grainger Coll Engn, Dept Bioengn, Urbana, IL 61801 USAWinter, Jackson论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Grainger Coll Engn, Dept Bioengn, Urbana, IL 61801 USA Univ Illinois, Grainger Coll Engn, Dept Bioengn, Urbana, IL 61801 USAElias, Gianna论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Grainger Coll Engn, Dept Bioengn, Urbana, IL 61801 USA Univ Illinois, Grainger Coll Engn, Dept Bioengn, Urbana, IL 61801 USASwami, Devyani论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Grainger Coll Engn, Dept Bioengn, Urbana, IL 61801 USA Univ Illinois, Grainger Coll Engn, Dept Bioengn, Urbana, IL 61801 USANambiar, Ananthan论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Grainger Coll Engn, Dept Bioengn, Urbana, IL 61801 USA Univ Illinois, Carl R Woese Inst Genom Biol, Urbana, IL 61801 USA Univ Illinois, Grainger Coll Engn, Dept Bioengn, Urbana, IL 61801 USAStilger, Michelle论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Grainger Coll Engn, Dept Bioengn, Urbana, IL 61801 USA Univ Illinois, Grainger Coll Engn, Dept Bioengn, Urbana, IL 61801 USAWoods, Wendy S.论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Grainger Coll Engn, Dept Bioengn, Urbana, IL 61801 USA Univ Illinois, Grainger Coll Engn, Dept Bioengn, Urbana, IL 61801 USAGosstola, Nicholas论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Grainger Coll Engn, Dept Bioengn, Urbana, IL 61801 USA Univ Illinois, Carl R Woese Inst Genom Biol, Urbana, IL 61801 USA Univ Illinois, Grainger Coll Engn, Dept Bioengn, Urbana, IL 61801 USAGapinske, Michael论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Grainger Coll Engn, Dept Bioengn, Urbana, IL 61801 USA Univ Illinois, Grainger Coll Engn, Dept Bioengn, Urbana, IL 61801 USAZeballos, Alejandra论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Grainger Coll Engn, Dept Bioengn, Urbana, IL 61801 USA Univ Illinois, Grainger Coll Engn, Dept Bioengn, Urbana, IL 61801 USAMoore, Hayden论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Grainger Coll Engn, Dept Bioengn, Urbana, IL 61801 USA Univ Illinois, Grainger Coll Engn, Dept Bioengn, Urbana, IL 61801 USAMaslov, Sergei论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Grainger Coll Engn, Dept Bioengn, Urbana, IL 61801 USA Univ Illinois, Carl R Woese Inst Genom Biol, Urbana, IL 61801 USA Univ Illinois, Grainger Coll Engn, Dept Bioengn, Urbana, IL 61801 USAGaj, Thomas论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Grainger Coll Engn, Dept Bioengn, Urbana, IL 61801 USA Univ Illinois, Carl R Woese Inst Genom Biol, Urbana, IL 61801 USA Univ Illinois, Grainger Coll Engn, Dept Bioengn, Urbana, IL 61801 USAPerez-Pinera, Pablo论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Grainger Coll Engn, Dept Bioengn, Urbana, IL 61801 USA Univ Illinois, Carl R Woese Inst Genom Biol, Urbana, IL 61801 USA Univ Illinois, Carle Illinois Coll Med, Dept Biomed & Translat Sci, Urbana, IL 61801 USA Univ Illinois, Canc Ctr Illinois, Urbana, IL 61801 USA Univ Illinois, Dept Mol & Integrat Physiol, Urbana, IL 61801 USA Univ Illinois, Grainger Coll Engn, Dept Bioengn, Urbana, IL 61801 USA
- [44] Precise in vivo functional analysis of DNA variants with base editing using ACEofBASEs target predictionELIFE, 2022, 11Cornean, Alex论文数: 0 引用数: 0 h-index: 0机构: Heidelberg Univ, Ctr Organismal Studies, Heidelberg, Germany Heidelberg Biosci Int Grad Sch HBIGS, Heidelberg, Germany Heidelberg Univ, Ctr Organismal Studies, Heidelberg, GermanyGierten, Jakob论文数: 0 引用数: 0 h-index: 0机构: Heidelberg Univ, Ctr Organismal Studies, Heidelberg, Germany Univ Hosp Heidelberg, Dept Pediat Cardiol, Heidelberg, Germany DZHK German Ctr Cardiovasc Res, Heidelberg, Germany Heidelberg Univ, Ctr Organismal Studies, Heidelberg, GermanyWelz, Bettina论文数: 0 引用数: 0 h-index: 0机构: Heidelberg Univ, Ctr Organismal Studies, Heidelberg, Germany Heidelberg Biosci Int Grad Sch HBIGS, Heidelberg, Germany DZHK German Ctr Cardiovasc Res, Heidelberg, Germany Heidelberg Univ, Ctr Organismal Studies, Heidelberg, GermanyLuis Mateo, Juan论文数: 0 引用数: 0 h-index: 0机构: Univ Oviedo, Dept Comp Sci, Oviedo, Spain Heidelberg Univ, Ctr Organismal Studies, Heidelberg, GermanyThumberger, Thomas论文数: 0 引用数: 0 h-index: 0机构: Heidelberg Univ, Ctr Organismal Studies, Heidelberg, Germany Heidelberg Univ, Ctr Organismal Studies, Heidelberg, Germany论文数: 引用数: h-index:机构:
- [45] In vivo adenine base editing of PCSK9 in macaques reduces LDL cholesterol levelsNATURE BIOTECHNOLOGY, 2021, 39 (08) : 949 - 957Rothgangl, Tanja论文数: 0 引用数: 0 h-index: 0机构: Univ Zurich, Inst Pharmacol & Toxicol, Zurich, Switzerland Univ Zurich, Inst Pharmacol & Toxicol, Zurich, SwitzerlandDennis, Melissa K.论文数: 0 引用数: 0 h-index: 0机构: Acuitas Therapeut Inc, Vancouver, BC, Canada Univ Zurich, Inst Pharmacol & Toxicol, Zurich, SwitzerlandLin, Paulo J. C.论文数: 0 引用数: 0 h-index: 0机构: Acuitas Therapeut Inc, Vancouver, BC, Canada Univ Zurich, Inst Pharmacol & Toxicol, Zurich, SwitzerlandOka, Rurika论文数: 0 引用数: 0 h-index: 0机构: Princess Maxima Ctr Pediat Oncol, Oncode Inst, Utrecht, Netherlands Univ Zurich, Inst Pharmacol & Toxicol, Zurich, SwitzerlandWitzigmann, Dominik论文数: 0 引用数: 0 h-index: 0机构: Univ Zurich, Inst Pharmacol & Toxicol, Zurich, Switzerland Univ Zurich, Inst Pharmacol & Toxicol, Zurich, Switzerland论文数: 引用数: h-index:机构:Qi, Weihong论文数: 0 引用数: 0 h-index: 0机构: Univ Zurich, ETH Zurich, Funct Genom Ctr Zurich, Zurich, Switzerland Univ Zurich, Inst Pharmacol & Toxicol, Zurich, SwitzerlandHruzova, Martina论文数: 0 引用数: 0 h-index: 0机构: Swiss Fed Inst Technol, Dept Biol, Inst Mol Hlth Sci, Zurich, Switzerland Univ Zurich, Inst Pharmacol & Toxicol, Zurich, Switzerland论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:Borrelli, Costanza论文数: 0 引用数: 0 h-index: 0机构: Swiss Fed Inst Technol, Dept Biosyst Sci & Engn, Zurich, Switzerland Univ Zurich, Inst Pharmacol & Toxicol, Zurich, SwitzerlandEgli, Sabina论文数: 0 引用数: 0 h-index: 0机构: Univ Zurich, Inst Pharmacol & Toxicol, Zurich, Switzerland Univ Zurich, Inst Pharmacol & Toxicol, Zurich, SwitzerlandFrey, Nina论文数: 0 引用数: 0 h-index: 0机构: Swiss Fed Inst Technol, Dept Biol, Inst Mol Hlth Sci, Zurich, Switzerland Univ Zurich, Inst Pharmacol & Toxicol, Zurich, SwitzerlandBakker, Noelle论文数: 0 引用数: 0 h-index: 0机构: Univ Zurich, Inst Pharmacol & Toxicol, Zurich, Switzerland Univ Zurich, Inst Pharmacol & Toxicol, Zurich, SwitzerlandWalker, John A., II论文数: 0 引用数: 0 h-index: 0机构: Synthego Corp, Redwood City, CA USA Univ Zurich, Inst Pharmacol & Toxicol, Zurich, SwitzerlandKadina, Anastasia P.论文数: 0 引用数: 0 h-index: 0机构: Synthego Corp, Redwood City, CA USA Univ Zurich, Inst Pharmacol & Toxicol, Zurich, SwitzerlandVictorov, Denis V.论文数: 0 引用数: 0 h-index: 0机构: Synthego Corp, Redwood City, CA USA Univ Zurich, Inst Pharmacol & Toxicol, Zurich, SwitzerlandPacesa, Martin论文数: 0 引用数: 0 h-index: 0机构: Univ Zurich, Dept Biochem, Zurich, Switzerland Univ Zurich, Inst Pharmacol & Toxicol, Zurich, SwitzerlandKreutzer, Susanne论文数: 0 引用数: 0 h-index: 0机构: Univ Zurich, ETH Zurich, Funct Genom Ctr Zurich, Zurich, Switzerland Swiss Fed Inst Technol, Genome Engn & Measurement Lab, Zurich, Switzerland Univ Zurich, Inst Pharmacol & Toxicol, Zurich, SwitzerlandKontarakis, Zacharias论文数: 0 引用数: 0 h-index: 0机构: Univ Zurich, ETH Zurich, Funct Genom Ctr Zurich, Zurich, Switzerland Swiss Fed Inst Technol, Genome Engn & Measurement Lab, Zurich, Switzerland Univ Zurich, Inst Pharmacol & Toxicol, Zurich, SwitzerlandMoor, Andreas论文数: 0 引用数: 0 h-index: 0机构: Swiss Fed Inst Technol, Dept Biosyst Sci & Engn, Zurich, Switzerland Univ Zurich, Inst Pharmacol & Toxicol, Zurich, SwitzerlandJinek, Martin论文数: 0 引用数: 0 h-index: 0机构: Univ Zurich, Dept Biochem, Zurich, Switzerland Univ Zurich, Inst Pharmacol & Toxicol, Zurich, SwitzerlandWeissman, Drew论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Dept Med, Philadelphia, PA 19104 USA Univ Zurich, Inst Pharmacol & Toxicol, Zurich, SwitzerlandStoffel, Markus论文数: 0 引用数: 0 h-index: 0机构: Swiss Fed Inst Technol, Dept Biol, Inst Mol Hlth Sci, Zurich, Switzerland Univ Zurich, Inst Pharmacol & Toxicol, Zurich, Switzerlandvan Boxtel, Ruben论文数: 0 引用数: 0 h-index: 0机构: Princess Maxima Ctr Pediat Oncol, Oncode Inst, Utrecht, Netherlands Univ Zurich, Inst Pharmacol & Toxicol, Zurich, SwitzerlandHolden, Kevin论文数: 0 引用数: 0 h-index: 0机构: Synthego Corp, Redwood City, CA USA Univ Zurich, Inst Pharmacol & Toxicol, Zurich, SwitzerlandPardi, Norbert论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Dept Med, Philadelphia, PA 19104 USA Univ Zurich, Inst Pharmacol & Toxicol, Zurich, SwitzerlandThoeny, Beat论文数: 0 引用数: 0 h-index: 0机构: Univ Childrens Hosp Zurich, Div Metab & Childrens Res Ctr, Zurich, Switzerland Zurich Ctr Integrat Human Physiol, Zurich, Switzerland Neurosci Ctr Zurich, Zurich, Switzerland Univ Zurich, Inst Pharmacol & Toxicol, Zurich, SwitzerlandHaeberle, Johannes论文数: 0 引用数: 0 h-index: 0机构: Univ Childrens Hosp Zurich, Div Metab & Childrens Res Ctr, Zurich, Switzerland Zurich Ctr Integrat Human Physiol, Zurich, Switzerland Univ Zurich, Inst Mol Life Sci, Zurich, Switzerland Univ Zurich, Inst Pharmacol & Toxicol, Zurich, SwitzerlandTam, Ying K.论文数: 0 引用数: 0 h-index: 0机构: Acuitas Therapeut Inc, Vancouver, BC, Canada Univ Zurich, Inst Pharmacol & Toxicol, Zurich, SwitzerlandSemple, Sean C.论文数: 0 引用数: 0 h-index: 0机构: Acuitas Therapeut Inc, Vancouver, BC, Canada Univ Zurich, Inst Pharmacol & Toxicol, Zurich, SwitzerlandSchwank, Gerald论文数: 0 引用数: 0 h-index: 0机构: Univ Zurich, Inst Pharmacol & Toxicol, Zurich, Switzerland Swiss Fed Inst Technol, Dept Biol, Inst Mol Hlth Sci, Zurich, Switzerland Univ Zurich, Inst Pharmacol & Toxicol, Zurich, Switzerland
- [46] In vivo base editing of Angptl3 via lipid nanoparticles to treat cardiovascular diseaseMOLECULAR THERAPY NUCLEIC ACIDS, 2025, 36 (02):Khirallah, Jennifer论文数: 0 引用数: 0 h-index: 0机构: Tufts Univ, Dept Biomed Engn, Medford, MA 02155 USA Tufts Univ, Dept Biomed Engn, Medford, MA 02155 USABloomer, Hanan论文数: 0 引用数: 0 h-index: 0机构: Tufts Univ, Dept Biomed Engn, Medford, MA 02155 USA Tufts Univ, Sch Med, Boston, MA 02111 USA Tufts Univ, Grad Sch Biomed Sci, Boston, MA 02111 USA Tufts Univ, Dept Biomed Engn, Medford, MA 02155 USAWich, Douglas论文数: 0 引用数: 0 h-index: 0机构: Tufts Univ, Dept Biomed Engn, Medford, MA 02155 USA Tufts Univ, Dept Biomed Engn, Medford, MA 02155 USAHuang, Changfeng论文数: 0 引用数: 0 h-index: 0机构: Tufts Univ, Dept Biomed Engn, Medford, MA 02155 USA Tufts Univ, Dept Biomed Engn, Medford, MA 02155 USAWorkman, J. Noah论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, Dept Genet Med, Baltimore, MD 21205 USA Tufts Univ, Dept Biomed Engn, Medford, MA 02155 USALi, Yamin论文数: 0 引用数: 0 h-index: 0机构: Tufts Univ, Dept Biomed Engn, Medford, MA 02155 USA Tufts Univ, Dept Biomed Engn, Medford, MA 02155 USANewby, Gregory A.论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, Dept Genet Med, Baltimore, MD 21205 USA Johns Hopkins Univ, Dept Biomed Engn, Baltimore, MD 21218 USA Broad Inst MIT & Harvard, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA Harvard Univ, Howard Hughes Med Inst, Cambridge, MA 02138 USA Tufts Univ, Dept Biomed Engn, Medford, MA 02155 USALiu, David R.论文数: 0 引用数: 0 h-index: 0机构: Broad Inst MIT & Harvard, Merkin Inst Transformat Technol Healthcare, Cambridge, MA 02142 USA Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA 02138 USA Harvard Univ, Howard Hughes Med Inst, Cambridge, MA 02138 USA Tufts Univ, Dept Biomed Engn, Medford, MA 02155 USA论文数: 引用数: h-index:机构:
- [47] In vivo cytidine base editing of hepatocytes without detectable off-target mutations in RNA and DNANATURE BIOMEDICAL ENGINEERING, 2021, 5 (02) : 179 - 189论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:Hall, Jonathan论文数: 0 引用数: 0 h-index: 0机构: Swiss Fed Inst Technol, Inst Pharmaceut Sci, Zurich, Switzerland Swiss Fed Inst Technol, Inst Mol Hlth Sci, Dept Biol, Zurich, SwitzerlandRehrauer, Hubert论文数: 0 引用数: 0 h-index: 0机构: Univ Zurich, ETH Zurich, Funct Genom Ctr Zurich, Zurich, Switzerland Swiss Fed Inst Technol, Inst Mol Hlth Sci, Dept Biol, Zurich, Switzerlandvan Boxtel, Ruben论文数: 0 引用数: 0 h-index: 0机构: Princess Maxima Ctr Pediat Oncol, Oncode Inst, Utrecht, Netherlands Swiss Fed Inst Technol, Inst Mol Hlth Sci, Dept Biol, Zurich, SwitzerlandTam, Ying K.论文数: 0 引用数: 0 h-index: 0机构: Acuitas Therapeut, Vancouver, BC, Canada Swiss Fed Inst Technol, Inst Mol Hlth Sci, Dept Biol, Zurich, SwitzerlandSchwank, Gerald论文数: 0 引用数: 0 h-index: 0机构: Swiss Fed Inst Technol, Inst Mol Hlth Sci, Dept Biol, Zurich, Switzerland Univ Zurich, Inst Pharmacol & Toxicol, Zurich, Switzerland Swiss Fed Inst Technol, Inst Mol Hlth Sci, Dept Biol, Zurich, Switzerland
- [48] Cytosine base editing inhibits hepatitis B virus replication and reduces HBsAg expression in vitro and in vivoMOLECULAR THERAPY NUCLEIC ACIDS, 2024, 35 (01):Smekalova, Elena M.论文数: 0 引用数: 0 h-index: 0机构: Beam Therapeut, Cambridge, MA 02142 USA Beam Therapeut, Cambridge, MA 02142 USAMartinez, Maria G.论文数: 0 引用数: 0 h-index: 0机构: INSERM, Canc Res Ctr Lyon, CNRS, U1052,UMR 5286, F-69008 Lyon, France Univ Lyon, UMR S1052, UCBL, F-69008 Lyon, France Hepatol Inst Lyon, F-69008 Lyon, France Beam Therapeut, Cambridge, MA 02142 USACombe, Emmanuel论文数: 0 引用数: 0 h-index: 0机构: INSERM, Canc Res Ctr Lyon, CNRS, U1052,UMR 5286, F-69008 Lyon, France Univ Lyon, UMR S1052, UCBL, F-69008 Lyon, France Hepatol Inst Lyon, F-69008 Lyon, France Beam Therapeut, Cambridge, MA 02142 USAKumar, Anuj论文数: 0 引用数: 0 h-index: 0机构: INSERM, Canc Res Ctr Lyon, CNRS, U1052,UMR 5286, F-69008 Lyon, France Univ Lyon, UMR S1052, UCBL, F-69008 Lyon, France Hepatol Inst Lyon, F-69008 Lyon, France Beam Therapeut, Cambridge, MA 02142 USADejene, Selam论文数: 0 引用数: 0 h-index: 0机构: Beam Therapeut, Cambridge, MA 02142 USA Beam Therapeut, Cambridge, MA 02142 USALeboeuf, Dominique论文数: 0 引用数: 0 h-index: 0机构: Beam Therapeut, Cambridge, MA 02142 USA Beam Therapeut, Cambridge, MA 02142 USAChen, Chao-Ying论文数: 0 引用数: 0 h-index: 0机构: Beam Therapeut, Cambridge, MA 02142 USA Beam Therapeut, Cambridge, MA 02142 USADorkin, J. Robert论文数: 0 引用数: 0 h-index: 0机构: Beam Therapeut, Cambridge, MA 02142 USA Beam Therapeut, Cambridge, MA 02142 USAShuang, Lan Shuan论文数: 0 引用数: 0 h-index: 0机构: Beam Therapeut, Cambridge, MA 02142 USA Beam Therapeut, Cambridge, MA 02142 USAKieft, Sarah论文数: 0 引用数: 0 h-index: 0机构: Beam Therapeut, Cambridge, MA 02142 USA Beam Therapeut, Cambridge, MA 02142 USAYoung, Lauren论文数: 0 引用数: 0 h-index: 0机构: Beam Therapeut, Cambridge, MA 02142 USA Beam Therapeut, Cambridge, MA 02142 USABarrera, Luis Alberto论文数: 0 引用数: 0 h-index: 0机构: Beam Therapeut, Cambridge, MA 02142 USA Beam Therapeut, Cambridge, MA 02142 USAPacker, Michael S.论文数: 0 引用数: 0 h-index: 0机构: Beam Therapeut, Cambridge, MA 02142 USA Beam Therapeut, Cambridge, MA 02142 USACiaramella, Giuseppe论文数: 0 引用数: 0 h-index: 0机构: Beam Therapeut, Cambridge, MA 02142 USA Beam Therapeut, Cambridge, MA 02142 USATestoni, Barbara论文数: 0 引用数: 0 h-index: 0机构: INSERM, Canc Res Ctr Lyon, CNRS, U1052,UMR 5286, F-69008 Lyon, France Univ Lyon, UMR S1052, UCBL, F-69008 Lyon, France Hepatol Inst Lyon, F-69008 Lyon, France Beam Therapeut, Cambridge, MA 02142 USAGregoire, Francine论文数: 0 引用数: 0 h-index: 0机构: Beam Therapeut, Cambridge, MA 02142 USA Beam Therapeut, Cambridge, MA 02142 USAZoulim, Fabien论文数: 0 引用数: 0 h-index: 0机构: INSERM, Canc Res Ctr Lyon, CNRS, U1052,UMR 5286, F-69008 Lyon, France Univ Lyon, UMR S1052, UCBL, F-69008 Lyon, France Hepatol Inst Lyon, F-69008 Lyon, France Hosp Civils Lyon HCL, Hepatol Dept, F-69004 Lyon, France INSERM, Canc Res Ctr Lyon CRCL, U1052, 151 Cours Albert Thomas, F-69003 Lyon, France Beam Therapeut, Cambridge, MA 02142 USA
- [49] In Vivo Base Editing of Scn5a Rescues Type 3 Long QT Syndrome in MiceCIRCULATION, 2024, 149 (04) : 317 - 329Qi, Man论文数: 0 引用数: 0 h-index: 0机构: Chinese Acad Med Sci, Fuwai Hosp, Shenzhen Key Lab Cardiovasc Dis, Shenzhen, Peoples R China Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, Natl Ctr Cardiovasc Dis, Key Lab Pluripotent Stem Cells Cardiac Repair & Re, Beijing, Peoples R China Chinese Peoples Liberat Army Gen Hosp, Coll Pulm & Crit Care Med, Beijing Key Lab OTIR, Beijing, Peoples R China Chinese Peoples Liberat Army Gen Hosp, Dept Cardiol, Beijing, Peoples R China Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, State Key Lab Cardiovasc Dis, Natl Ctr Cardiovasc Dis, Beijing 100037, Peoples R ChinaMa, Shuhong论文数: 0 引用数: 0 h-index: 0机构: Chinese Acad Med Sci & Peking Union Med Coll, Natl Ctr Cardiovasc Dis, State Key Lab Cardiovasc Dis, Fuwai Hosp, Beijing 100037, Peoples R China Chinese Acad Med Sci, Fuwai Hosp, Shenzhen Key Lab Cardiovasc Dis, Shenzhen, Peoples R China Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, Natl Ctr Cardiovasc Dis, Key Lab Pluripotent Stem Cells Cardiac Repair & Re, Beijing, Peoples R China Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, State Key Lab Cardiovasc Dis, Natl Ctr Cardiovasc Dis, Beijing 100037, Peoples R ChinaLiu, Jingtong论文数: 0 引用数: 0 h-index: 0机构: Fudan Univ, Zhongshan Hosp, Sch Life Sci, State Key Lab Genet Engn, Shanghai, Peoples R China Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, State Key Lab Cardiovasc Dis, Natl Ctr Cardiovasc Dis, Beijing 100037, Peoples R ChinaLiu, Xujie论文数: 0 引用数: 0 h-index: 0机构: Chinese Acad Med Sci, Fuwai Hosp, Shenzhen Key Lab Cardiovasc Dis, Shenzhen, Peoples R China Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, Natl Ctr Cardiovasc Dis, Key Lab Pluripotent Stem Cells Cardiac Repair & Re, Beijing, Peoples R China Fuwai Cent China Hosp, Natl Ctr Cardiovasc Dis, Natl Hlth Commiss Key Lab Cardiovasc Regenerat Med, Cent China Branch, Zhengzhou, Peoples R China Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, State Key Lab Cardiovasc Dis, Natl Ctr Cardiovasc Dis, Beijing 100037, Peoples R ChinaWei, Jingjing论文数: 0 引用数: 0 h-index: 0机构: Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, Natl Ctr Cardiovasc Dis, Key Lab Pluripotent Stem Cells Cardiac Repair & Re, Beijing, Peoples R China Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, State Key Lab Cardiovasc Dis, Natl Ctr Cardiovasc Dis, Beijing 100037, Peoples R ChinaLu, Wen-Jing论文数: 0 引用数: 0 h-index: 0机构: Capital Med Univ, Beijing Anzhen Hosp, Minist Educ, Beijing Lab Cardiovasc Precis Med,Key Lab Biomed E, Beijing, Peoples R China Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, State Key Lab Cardiovasc Dis, Natl Ctr Cardiovasc Dis, Beijing 100037, Peoples R ChinaZhang, Siyao论文数: 0 引用数: 0 h-index: 0机构: Capital Med Univ, Beijing Anzhen Hosp, Minist Educ, Beijing Lab Cardiovasc Precis Med,Key Lab Biomed E, Beijing, Peoples R China Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, State Key Lab Cardiovasc Dis, Natl Ctr Cardiovasc Dis, Beijing 100037, Peoples R ChinaChang, Yun论文数: 0 引用数: 0 h-index: 0机构: Chinese Acad Med Sci, Fuwai Hosp, Shenzhen Key Lab Cardiovasc Dis, Shenzhen, Peoples R China Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, Natl Ctr Cardiovasc Dis, Key Lab Pluripotent Stem Cells Cardiac Repair & Re, Beijing, Peoples R China Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, State Key Lab Cardiovasc Dis, Natl Ctr Cardiovasc Dis, Beijing 100037, Peoples R ChinaZhang, Yongshuai论文数: 0 引用数: 0 h-index: 0机构: Chinese Acad Med Sci, Fuwai Hosp, Shenzhen Key Lab Cardiovasc Dis, Shenzhen, Peoples R China Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, Natl Ctr Cardiovasc Dis, Key Lab Pluripotent Stem Cells Cardiac Repair & Re, Beijing, Peoples R China Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, State Key Lab Cardiovasc Dis, Natl Ctr Cardiovasc Dis, Beijing 100037, Peoples R ChinaZhong, Kejia论文数: 0 引用数: 0 h-index: 0机构: Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, Natl Ctr Cardiovasc Dis, Key Lab Pluripotent Stem Cells Cardiac Repair & Re, Beijing, Peoples R China Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, State Key Lab Cardiovasc Dis, Natl Ctr Cardiovasc Dis, Beijing 100037, Peoples R ChinaYan, Yuting论文数: 0 引用数: 0 h-index: 0机构: Chinese Acad Med Sci, Fuwai Hosp, Shenzhen Key Lab Cardiovasc Dis, Shenzhen, Peoples R China Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, Natl Ctr Cardiovasc Dis, Key Lab Pluripotent Stem Cells Cardiac Repair & Re, Beijing, Peoples R China Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, State Key Lab Cardiovasc Dis, Natl Ctr Cardiovasc Dis, Beijing 100037, Peoples R ChinaZhu, Min论文数: 0 引用数: 0 h-index: 0机构: Chinese Acad Med Sci, Fuwai Hosp, Shenzhen Key Lab Cardiovasc Dis, Shenzhen, Peoples R China Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, Natl Ctr Cardiovasc Dis, Key Lab Pluripotent Stem Cells Cardiac Repair & Re, Beijing, Peoples R China Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, State Key Lab Cardiovasc Dis, Natl Ctr Cardiovasc Dis, Beijing 100037, Peoples R ChinaSong, Yabing论文数: 0 引用数: 0 h-index: 0机构: Tsinghua Univ, Sch Life Sci, Beijing, Peoples R China Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, State Key Lab Cardiovasc Dis, Natl Ctr Cardiovasc Dis, Beijing 100037, Peoples R ChinaChen, Yundai论文数: 0 引用数: 0 h-index: 0机构: Chinese Peoples Liberat Army Gen Hosp, Dept Cardiol, Beijing, Peoples R China Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, State Key Lab Cardiovasc Dis, Natl Ctr Cardiovasc Dis, Beijing 100037, Peoples R ChinaHao, Guoliang论文数: 0 引用数: 0 h-index: 0机构: Henan Acad Innovat Med Sci, Zhengzhou, Peoples R China Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, State Key Lab Cardiovasc Dis, Natl Ctr Cardiovasc Dis, Beijing 100037, Peoples R ChinaWang, Jianbin论文数: 0 引用数: 0 h-index: 0机构: Tsinghua Univ, Sch Life Sci, Beijing, Peoples R China Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, State Key Lab Cardiovasc Dis, Natl Ctr Cardiovasc Dis, Beijing 100037, Peoples R ChinaWang, Li论文数: 0 引用数: 0 h-index: 0机构: Chinese Acad Med Sci, Fuwai Hosp, Shenzhen Key Lab Cardiovasc Dis, Shenzhen, Peoples R China Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, Natl Ctr Cardiovasc Dis, Key Lab Pluripotent Stem Cells Cardiac Repair & Re, Beijing, Peoples R China Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, State Key Lab Cardiovasc Dis, Natl Ctr Cardiovasc Dis, Beijing 100037, Peoples R ChinaLee, Andrew S.论文数: 0 引用数: 0 h-index: 0机构: Shenzhen Bay Lab, Inst Canc Res, Shenzhen, Peoples R China Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, State Key Lab Cardiovasc Dis, Natl Ctr Cardiovasc Dis, Beijing 100037, Peoples R ChinaChen, Xiangbo论文数: 0 引用数: 0 h-index: 0机构: Floor 3,Bldg B,Transfer Innovat Bldg, Hangzhou, Zhejiang, Peoples R China Hangzhou Rongze Biotechnol Grp Co Ltd, Hangzhou, Peoples R China Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, State Key Lab Cardiovasc Dis, Natl Ctr Cardiovasc Dis, Beijing 100037, Peoples R ChinaWang, Yongming论文数: 0 引用数: 0 h-index: 0机构: Fudan Univ, Zhongshan Hosp, Sch Life Sci, State Key Lab Genet Engn, Shanghai 200438, Peoples R China Fudan Univ, Zhongshan Hosp, Sch Life Sci, State Key Lab Genet Engn, Shanghai, Peoples R China Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, State Key Lab Cardiovasc Dis, Natl Ctr Cardiovasc Dis, Beijing 100037, Peoples R ChinaLan, Feng论文数: 0 引用数: 0 h-index: 0机构: Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, State Key Lab Cardiovasc Dis, Natl Ctr Cardiovasc Dis, Beijing 100037, Peoples R China Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, Natl Ctr Cardiovasc Dis, Key Lab Pluripotent Stem Cells Cardiac Repair & Re, Beijing, Peoples R China Fuwai Cent China Hosp, Natl Ctr Cardiovasc Dis, Natl Hlth Commiss Key Lab Cardiovasc Regenerat Med, Cent China Branch, Zhengzhou, Peoples R China Capital Med Univ, Beijing Anzhen Hosp, Minist Educ, Beijing Lab Cardiovasc Precis Med,Key Lab Biomed E, Beijing, Peoples R China Chinese Acad Med Sci & Peking Union Med Coll, Fuwai Hosp, State Key Lab Cardiovasc Dis, Natl Ctr Cardiovasc Dis, Beijing 100037, Peoples R China
- [50] A base editing strategy using mRNA-LNPs for in vivo correction of the most frequent phenylketonuria variantHUMAN GENETICS AND GENOMICS ADVANCES, 2024, 5 (01):Brooks, Dominique L.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Cardiovasc Inst, Perelman Sch Med, Philadelphia, PA 19104 USA Univ Penn, Dept Med, Div Cardiovasc Med, Perelman Sch Med, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Genet, Philadelphia, PA 19104 USA Univ Penn, Cardiovasc Inst, Perelman Sch Med, Philadelphia, PA 19104 USAWhittaker, Madelynn N.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Cardiovasc Inst, Perelman Sch Med, Philadelphia, PA 19104 USA Univ Penn, Dept Med, Div Cardiovasc Med, Perelman Sch Med, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Genet, Philadelphia, PA 19104 USA Univ Penn, Dept Bioengn, Philadelphia, PA 19104 USA Univ Penn, Cardiovasc Inst, Perelman Sch Med, Philadelphia, PA 19104 USASaid, Hooda论文数: 0 引用数: 0 h-index: 0机构: George Mason Univ, Dept Bioengn, Fairfax, VA 22030 USA Univ Penn, Cardiovasc Inst, Perelman Sch Med, Philadelphia, PA 19104 USADwivedi, Garima论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Dept Med, Div Infect Dis, Philadelphia, PA 19104 USA Univ Penn, Cardiovasc Inst, Perelman Sch Med, Philadelphia, PA 19104 USAQu, Ping论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Cardiovasc Inst, Perelman Sch Med, Philadelphia, PA 19104 USA Univ Penn, Dept Med, Div Cardiovasc Med, Perelman Sch Med, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Genet, Philadelphia, PA 19104 USA Univ Penn, Cardiovasc Inst, Perelman Sch Med, Philadelphia, PA 19104 USAMusunuru, Kiran论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Cardiovasc Inst, Perelman Sch Med, Philadelphia, PA 19104 USA Univ Penn, Dept Med, Div Cardiovasc Med, Perelman Sch Med, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Genet, Philadelphia, PA 19104 USA Univ Penn, Cardiovasc Inst, Perelman Sch Med, Philadelphia, PA 19104 USAAhrens-Nicklas, Rebecca C.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Cardiovasc Inst, Perelman Sch Med, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Genet, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Dept Pediat, Metab Dis Program, Div Human Genet, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Pediat, Philadelphia, PA 19104 USA Univ Penn, Cardiovasc Inst, Perelman Sch Med, Philadelphia, PA 19104 USAAlameh, Mohamad-Gabriel论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Cardiovasc Inst, Perelman Sch Med, Philadelphia, PA 19104 USA George Mason Univ, Dept Bioengn, Fairfax, VA 22030 USA Childrens Hosp Philadelphia, Dept Pathol & Lab Med, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Pathol & Lab Med, Philadelphia, PA 19104 USA Univ Penn, Cardiovasc Inst, Perelman Sch Med, Philadelphia, PA 19104 USAWang, Xiao论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Cardiovasc Inst, Perelman Sch Med, Philadelphia, PA 19104 USA Univ Penn, Dept Med, Div Cardiovasc Med, Perelman Sch Med, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Genet, Philadelphia, PA 19104 USA Univ Penn, Cardiovasc Inst, Perelman Sch Med, Philadelphia, PA 19104 USA