ESTIMATING UTILITY VALUES USING THE DUCHENNE MUSCULAR DYSTROPHY-QUALITY OF LIFE MEASURE (DMD-QOL): A NEW PREFERENCE-BASED MEASURE FOR DUCHENNE MUSCULAR DYSTROPHY

被引:0
|
作者
Bever, A. [1 ]
Audhya, I. Filipovic [2 ]
Szabo, S. [1 ]
Jayasinghe, P. [1 ]
Feeny, D. [3 ]
Neumann, P. [4 ]
Malone, D. C. [5 ]
Iannaccone, S. T. [6 ]
Gooch, K. L. [2 ]
机构
[1] Broadst Hlth Econ & Outcomes Res, Vancouver, BC, Canada
[2] Sarepta Therapeut, Cambridge, MA USA
[3] McMaster Univ, Hamilton, ON, Canada
[4] Tufts Med Ctr, Boston, MA USA
[5] Univ Utah, Salt Lake City, UT USA
[6] Univ Texas Southwestern Med Ctr Dallas, Dallas, TX USA
关键词
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中图分类号
F [经济];
学科分类号
02 ;
摘要
PCR230
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收藏
页码:S355 / S355
页数:1
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