EFFICACY AND SAFETY OF A SINGLE DOSE OF EXAGAMGLOGENE AUTOTEMCEL FOR TRANSFUSION-DEPENDENT.-THALASSEMIA AND SEVERE SICKLE CELL DISEASE

被引：0

作者：

Locatelli, Franco ^{[1
]}

Frangoul, Haydar ^{[2
]}

Corbacioglu, Selim ^{[3
]}

de la Fuente, Josu ^{[4
]}

Wall, Donna ^{[5
]}

Cappellini, Maria Domenica ^{[6
]}

de Montalembert, Mariane ^{[7
]}

Kattamis, Antonis ^{[8
]}

Lobitz, Stephan ^{[9
]}

Rondelli, Damiano ^{[10
]}

Sheth, Sujit ^{[11
]}

Steinberg, Martin ^{[12
]}

Walters, Mark C. ^{[13
]}

Bobruff, Yael ^{[14
]}

Simard, Chris ^{[14
]}

Song, Yang ^{[14
]}

Zhang, Lanju ^{[14
]}

Sharma, Anjali ^{[15
]}

Imren, Suzan ^{[14
]}

Hobbs, Bill ^{[14
]}

Grupp, Stephan ^{[16
]}

机构：

[1] Osped Pediat Bambino Gesu, Rome, Italy

[2] Childrens Hosp, Sarah Cannon Ctr Blood Canc, Tri Star Centennial, Nashville, TN USA

[3] Univ Regensburg, Regensburg, Germany

[4] Imperial Coll Healthcare NHS Trust, St Marys Hosp, London, England

[5] Univ Toronto, Hosp Sick Children, Toronto, ON, Canada

[6] Univ Milan, Milan, Italy

[7] Univ Paris, Necker Enfants Malades Hosp, Assistance Publ Hop Paris, AP HP, Paris, France

[8] Univ Athens, Athens, Greece

[9] Gemeinschaftsklin Mittelrhein, Koblenz, Germany

[10] Univ Illinois, Chicago, IL USA

[11] Cornell Univ, Joan & Sanford Weill Med Coll, New York, NY USA

[12] Boston Univ, Sch Med, Boston, MA USA

[13] UCSF Benioff Childrens Hosp, Oakland, CA USA

[14] Vertex Pharmaceut Inc, Boston, MA USA

[15] CRISPR Therapeut, Cambridge, England

[16] Univ Penn, Childrens Hosp Philadelphia, Perelman Sch Med, Philadelphia, PA USA

来源：

BONE MARROW TRANSPLANTATION | 2023年 / 58卷 / SUPP1期

关键词：

D O I：

暂无

中图分类号：

Q6 [生物物理学];

学科分类号：

071011 ;

摘要：

O005

引用

页码：16 / 17

页数：2

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