[1] MedStar Georgetown Univ Hosp, Lombardi Comprehens Canc Ctr, Washington, DC USA
[2] Univ Miami, Div Pediat Hematol Oncol, Miller Sch Med, Sylvester Canc Ctr, Miami, FL USA
[3] Univ Miami, Hemophilia Treatment Ctr, Miami, FL USA
[4] IRCCS Ca Granda Fdn, Angelo Bianchi Bonomi Hemophilia & Thrombosis Ctr, Osped Maggiore Policlin, Milan, Italy
[5] Univ Illinois, Bleeding & Clotting Disorders Inst, Coll Med, Peoria, IL USA