共 8 条
[1]
Rapid Improvement after Starting Elexacaftor-Tezacaftor-Ivacaftor in Patients with Cystic Fibrosis and Advanced Pulmonary Disease
[J].
Burgel, Pierre-Regis
;
Durieu, Isabelle
;
Chiron, Raphael
;
Ramel, Sophie
;
Danner-Boucher, Isabelle
;
Prevotat, Anne
;
Grenet, Dominique
;
Marguet, Christophe
;
Reynaud-Gaubert, Martine
;
Macey, Julie
;
Mely, Laurent
;
Fenton, Annlyse
;
Quetant, Sebastien
;
Lemonnier, Lydie
;
Paillasseur, Jean-Louis
;
Da Silva, Jennifer
;
Martin, Clemence
.
AMERICAN JOURNAL OF RESPIRATORY AND CRITICAL CARE MEDICINE,
2021, 204 (01)
:64-73

Burgel, Pierre-Regis
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Paris, Inst Cochin, INSERM, Unite 1016, Paris, France
Cochin Hosp, AP HP, Resp Med & Cyst Fibrosis Natl Reference Ctr, Paris, France
European Reference Network Rare Resp Dis, Cyst Fibrosis Network, Frankfurt, Germany Univ Paris, Inst Cochin, INSERM, Unite 1016, Paris, France

Durieu, Isabelle
论文数: 0 引用数: 0
h-index: 0
机构:
European Reference Network Rare Resp Dis, Cyst Fibrosis Network, Frankfurt, Germany
Hosp Civils Lyon, Ctr Reference Adulte Mucoviscidose, Serv Med Interne, Pierre Benite, France
Univ Lyon, Serv Sante & Rech Rendement, Equipe Accueil 7425, Lyon, France Univ Paris, Inst Cochin, INSERM, Unite 1016, Paris, France

Chiron, Raphael
论文数: 0 引用数: 0
h-index: 0
机构:
Ctr Hosp Univ Montpellier, Ctr Mucoviscidose, Hop Arnaud de Villeneuve, Montpellier, France Univ Paris, Inst Cochin, INSERM, Unite 1016, Paris, France

Ramel, Sophie
论文数: 0 引用数: 0
h-index: 0
机构:
Fdn Ildys, Ctr Ressources & Competences Mucoviscidose, Roscoff, France Univ Paris, Inst Cochin, INSERM, Unite 1016, Paris, France

Danner-Boucher, Isabelle
论文数: 0 引用数: 0
h-index: 0
机构:
CHU Nantes, Inst Thorax, Serv Pneumol, Nantes, France Univ Paris, Inst Cochin, INSERM, Unite 1016, Paris, France

Prevotat, Anne
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Lille, CHU Lille, Ctr Mucoviscidose, Serv Pneumol & Immunoallergol,Hop Calmette, Lille, France Univ Paris, Inst Cochin, INSERM, Unite 1016, Paris, France

Grenet, Dominique
论文数: 0 引用数: 0
h-index: 0
机构:
Hop Foch, Serv Pneumol, Suresnes, France Univ Paris, Inst Cochin, INSERM, Unite 1016, Paris, France

论文数: 引用数:
h-index:
机构:

Reynaud-Gaubert, Martine
论文数: 0 引用数: 0
h-index: 0
机构:
Aix Marseille Univ, Nord Hosp, AP HM, Dept Resp Med & Lung Transplantat, Marseille, France Univ Paris, Inst Cochin, INSERM, Unite 1016, Paris, France

Macey, Julie
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Hosp Ctr Bordeaux, Resp Med & Cyst Fibrosis Ctr, Bordeaux, France Univ Paris, Inst Cochin, INSERM, Unite 1016, Paris, France

Mely, Laurent
论文数: 0 引用数: 0
h-index: 0
机构:
Renee Sabran Hosp, Cyst Fibrosis Ctr, Giens, France Univ Paris, Inst Cochin, INSERM, Unite 1016, Paris, France

Fenton, Annlyse
论文数: 0 引用数: 0
h-index: 0
机构:
Dijon Univ Hosp, Cyst Fibrosis Resource & Competence Ctr Adults, Dept Pulm Med, Dijon, France Univ Paris, Inst Cochin, INSERM, Unite 1016, Paris, France

Quetant, Sebastien
论文数: 0 引用数: 0
h-index: 0
机构:
Ctr Hosp Univ Grenoble Alpes, Serv Hosp Univ Pneumol & Physiol, Pole Thorax & Vaisseaux, La Tronche, France Univ Paris, Inst Cochin, INSERM, Unite 1016, Paris, France

Lemonnier, Lydie
论文数: 0 引用数: 0
h-index: 0
机构:
Assoc Vaincre Mucoviscidose, Paris, France Univ Paris, Inst Cochin, INSERM, Unite 1016, Paris, France

Paillasseur, Jean-Louis
论文数: 0 引用数: 0
h-index: 0
机构:
Effi Stat, Paris, France Univ Paris, Inst Cochin, INSERM, Unite 1016, Paris, France

Da Silva, Jennifer
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Paris, Inst Cochin, INSERM, Unite 1016, Paris, France
European Reference Network Rare Resp Dis, Cyst Fibrosis Network, Frankfurt, Germany
Hop Cochin, AP HP, Unite Rech Clin, Ctr Invest Clin Paris Descartes Necker Cochin, Paris, France Univ Paris, Inst Cochin, INSERM, Unite 1016, Paris, France

Martin, Clemence
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Paris, Inst Cochin, INSERM, Unite 1016, Paris, France
Cochin Hosp, AP HP, Resp Med & Cyst Fibrosis Natl Reference Ctr, Paris, France
European Reference Network Rare Resp Dis, Cyst Fibrosis Network, Frankfurt, Germany Univ Paris, Inst Cochin, INSERM, Unite 1016, Paris, France
[2]
Current prices versus minimum costs of production for CFTR modulators
[J].
Guo, Jonathan
;
Wang, Junzheng
;
Zhang, Jingchun
;
Fortunak, Joseph
;
Hill, Andrew
.
JOURNAL OF CYSTIC FIBROSIS,
2022, 21 (05)
:866-872

Guo, Jonathan
论文数: 0 引用数: 0
h-index: 0
机构:
Imperial Coll London, Fac Med, Sch Publ Hlth, London, England Imperial Coll London, Fac Med, Sch Publ Hlth, London, England

Wang, Junzheng
论文数: 0 引用数: 0
h-index: 0
机构:
Imperial Coll London, Fac Med, Sch Publ Hlth, London, England Imperial Coll London, Fac Med, Sch Publ Hlth, London, England

Zhang, Jingchun
论文数: 0 引用数: 0
h-index: 0
机构:
Univ North Dakota, Dept Biomed Engn, Grand Forks, ND USA Imperial Coll London, Fac Med, Sch Publ Hlth, London, England

Fortunak, Joseph
论文数: 0 引用数: 0
h-index: 0
机构:
Howard Univ, Chem & Pharmaceut Sci, Washington, DC USA Imperial Coll London, Fac Med, Sch Publ Hlth, London, England

论文数: 引用数:
h-index:
机构:
[3]
Pregnancy among cystic fibrosis women in the era of CFTR modulators
[J].
Heltshe, Sonya L.
;
Godfrey, Emily M.
;
Josephy, Tatiana
;
Aitken, Moira L.
;
Taylor-Cousar, Jennifer L.
.
JOURNAL OF CYSTIC FIBROSIS,
2017, 16 (06)
:687-694

Heltshe, Sonya L.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Washington, Sch Med, Dept Pediat, Div Pulmonol, 4800 Sand Point Way NE, Seattle, WA 98105 USA
Cyst Fibrosis Fdn, Therapeut Dev Network, Coordinating Ctr, Seattle Childrens Res Inst, POB 5371, Seattle, WA 98145 USA Univ Washington, Sch Med, Dept Pediat, Div Pulmonol, 4800 Sand Point Way NE, Seattle, WA 98105 USA

Godfrey, Emily M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Washington, Sch Med, Dept Family Med, 4311 11th Ave NE, Seattle, WA 98105 USA
Univ Washington, Sch Med, Dept Obstet & Gynecol, 4311 11th Ave NE, Seattle, WA 98105 USA Univ Washington, Sch Med, Dept Pediat, Div Pulmonol, 4800 Sand Point Way NE, Seattle, WA 98105 USA

Josephy, Tatiana
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Washington, Sch Med, Dept Family Med, 4311 11th Ave NE, Seattle, WA 98105 USA
Univ Washington, Sch Med, Dept Obstet & Gynecol, 4311 11th Ave NE, Seattle, WA 98105 USA Univ Washington, Sch Med, Dept Pediat, Div Pulmonol, 4800 Sand Point Way NE, Seattle, WA 98105 USA

Aitken, Moira L.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Washington, Sch Med, Div Pulm & Crit Care Med, 1959 NE Pacific,Campus Box 356522, Seattle, WA 98195 USA Univ Washington, Sch Med, Dept Pediat, Div Pulmonol, 4800 Sand Point Way NE, Seattle, WA 98105 USA

Taylor-Cousar, Jennifer L.
论文数: 0 引用数: 0
h-index: 0
机构:
Natl Jewish Hlth Dept Med, Div Pulm Crit Care & Sleep Med, 1400 Jackson St, Denver, CO 80206 USA
Natl Jewish Hlth Dept Pediat, Div Pulm Crit Care & Sleep Med, 1400 Jackson St, Denver, CO 80206 USA Univ Washington, Sch Med, Dept Pediat, Div Pulmonol, 4800 Sand Point Way NE, Seattle, WA 98105 USA
[4]
Left behind: The potential impact of CFTR modulators on racial and ethnic disparities in cystic fibrosis
[J].
McGarry, Meghan E.
;
Gibb, Elizabeth R.
;
Oates, Gabriela R.
;
Schechter, Michael S.
.
PAEDIATRIC RESPIRATORY REVIEWS,
2022, 42
:35-42

McGarry, Meghan E.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif San Francisco, Dept Pediat, Div Pulm Med, San Francisco, CA 94110 USA Univ Calif San Francisco, Dept Pediat, Div Pulm Med, San Francisco, CA 94110 USA

Gibb, Elizabeth R.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif San Francisco, Dept Pediat, Div Pulm Med, San Francisco, CA 94110 USA Univ Calif San Francisco, Dept Pediat, Div Pulm Med, San Francisco, CA 94110 USA

Oates, Gabriela R.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Alabama Birmingham, Dept Pediat, Div Pulm & Sleep Med, Birmingham, AL USA Univ Calif San Francisco, Dept Pediat, Div Pulm Med, San Francisco, CA 94110 USA

Schechter, Michael S.
论文数: 0 引用数: 0
h-index: 0
机构:
Virginia Commonwealth Univ, Dept Pediat, Div Pulm & Sleep Med, Richmond, VA USA
Childrens Hosp Richmond VCU, Richmond, VA USA Univ Calif San Francisco, Dept Pediat, Div Pulm Med, San Francisco, CA 94110 USA
[5]
Elexacaftor-Tezacaftor-Ivacaftor for Cystic Fibrosis with a Single Phe508del Allele
[J].
Middleton, P. G.
;
Mall, M. A.
;
Drevinek, P.
;
Lands, L. C.
;
McKone, E. F.
;
Polineni, D.
;
Ramsey, B. W.
;
Taylor-Cousar, J. L.
;
Tullis, E.
;
Vermeulen, F.
;
Marigowda, G.
;
Mckee, C. M.
;
Moskowitz, S. M.
;
Nair, N.
;
Savage, J.
;
Simard, C.
;
Tian, S.
;
Waltz, D.
;
Xuan, F.
;
Rowe, S. M.
;
Jain, R.
.
NEW ENGLAND JOURNAL OF MEDICINE,
2019, 381 (19)
:1809-1819

Middleton, P. G.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia
Univ Sydney, Westmead Inst Med Res, Ludwig Engel Ctr Resp Res, CF Res Grp, Westmead, NSW, Australia Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Mall, M. A.
论文数: 0 引用数: 0
h-index: 0
机构:
Charite, Berlin Inst Hlth, Dept Pediat Pulmonol Immunol & Intens Care Med, Berlin, Germany
German Ctr Lung Res, Berlin, Germany Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

论文数: 引用数:
h-index:
机构:

Lands, L. C.
论文数: 0 引用数: 0
h-index: 0
机构:
McGill Univ, Hlth Ctr, Pediat Resp Med & Pediat Cyst Fibrosis Clin, Montreal, PQ, Canada Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

McKone, E. F.
论文数: 0 引用数: 0
h-index: 0
机构:
St Vincents Univ Hosp, Dublin, Ireland
Univ Coll Dublin, Sch Med, Dublin, Ireland Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Polineni, D.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Kansas, Med Ctr, Dept Internal Med, Kansas City, KS 66103 USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Ramsey, B. W.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Washington, Sch Med, Dept Pediat, Seattle, WA 98195 USA
Seattle Childrens Res Inst, Seattle, WA USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Taylor-Cousar, J. L.
论文数: 0 引用数: 0
h-index: 0
机构:
Natl Jewish Hlth, Dept Med, Denver, CO USA
Natl Jewish Hlth, Dept Pediat, Denver, CO USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Tullis, E.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Toronto, St Michaels Hosp, Div Respirol, Toronto, ON, Canada Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Vermeulen, F.
论文数: 0 引用数: 0
h-index: 0
机构:
Katholieke Univ Leuven, Dept Pediat, Cyst Fibrosis Reference Ctr, Leuven, Belgium Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Marigowda, G.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Mckee, C. M.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Moskowitz, S. M.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Nair, N.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Savage, J.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Simard, C.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Tian, S.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Waltz, D.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Xuan, F.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Boston, MA USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Rowe, S. M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Alabama Birmingham, Dept Med, Birmingham, AL 35294 USA
Univ Alabama Birmingham, Dept Pediat, Birmingham, AL USA
Univ Alabama Birmingham, Dept Cell Dev & Integrat Biol, Birmingham, AL USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia

Jain, R.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Dept Internal Med, 5323 Harry Hines Blvd, Dallas, TX 75390 USA Univ Sydney, Westmead Hosp, Dept Resp & Sleep Med, Westmead, NSW, Australia
[6]
Seyoum S., 2020, COST COVERAGE UNDERU
[7]
The effectiveness and value of novel treatments for cystic fibrosis A summary from the Institute for Clinical and Economic Review's California Technology Assessment Forum
[J].
Tice, Jeffrey A.
;
Kuntz, Karen M.
;
Wherry, Kael
;
Seidner, Matt
;
Rind, David M.
;
Pearson, Steven D.
.
JOURNAL OF MANAGED CARE & SPECIALTY PHARMACY,
2021, 27 (02)
:276-280

Tice, Jeffrey A.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif San Francisco, Div Gen Internal Med, San Francisco, CA 94143 USA Univ Calif San Francisco, Div Gen Internal Med, San Francisco, CA 94143 USA

Kuntz, Karen M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Minnesota, Sch Publ Hlth, Minneapolis, MN USA Univ Calif San Francisco, Div Gen Internal Med, San Francisco, CA 94143 USA

Wherry, Kael
论文数: 0 引用数: 0
h-index: 0
机构: Univ Calif San Francisco, Div Gen Internal Med, San Francisco, CA 94143 USA

Seidner, Matt
论文数: 0 引用数: 0
h-index: 0
机构:
Inst Clin & Econ Review, Boston, MA USA Univ Calif San Francisco, Div Gen Internal Med, San Francisco, CA 94143 USA

Rind, David M.
论文数: 0 引用数: 0
h-index: 0
机构:
Inst Clin & Econ Review, Boston, MA USA Univ Calif San Francisco, Div Gen Internal Med, San Francisco, CA 94143 USA

Pearson, Steven D.
论文数: 0 引用数: 0
h-index: 0
机构:
Inst Clin & Econ Review, Boston, MA USA Univ Calif San Francisco, Div Gen Internal Med, San Francisco, CA 94143 USA
[8]
Vertex Pharmaceuticals, 2022, VERT REP 3 QUART 202