Current and Future Perspective in Hematopoietic Stem Progenitor Cell-gene Therapy for Inborn Errors of Metabolism

被引：4
作者：
Tucci, Francesca [1 ,2 ]
Consiglieri, Giulia [1 ,2 ,3 ]
Cossutta, Matilde [1 ,4 ]
Bernardo, Maria Ester [1 ,2 ,5 ]
机构：
[1] IRCCS San Raffaele Sci Inst, Pediat Immunohematol & Bone Marrow Transplantat, Milan, Italy
[2] San Raffaele Telethon Inst Gene Therapy SR TIGET, Milan, Italy
[3] Univ Roma Tor Vergata, Dept Biomed & Prevent, Rome, Italy
[4] Univ Roma Tor Vergata, Rome, Italy
[5] Univ Vita Salute San Raffaele, Milan, Italy
来源：
HEMASPHERE | 2023年 / 7卷 / 10期
关键词：
ONSET METACHROMATIC LEUKODYSTROPHY; MOUSE MODEL; OPEN-LABEL; TRANSPLANTATION; DISEASE; PHENOTYPE; CORRECTS; TYPE-1; BONE;
D O I：
10.1097/HS9.0000000000000953
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
[No abstract available]
引用
收藏
页数：6
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