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NEW ENGLAND JOURNAL OF MEDICINE, 2021, 384 (03) : 252 - 260Frangoul, H.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USAAltshuler, D.论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut, Boston, MA USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USA论文数: 引用数: h-index:机构:Chen, Y-S论文数: 0 引用数: 0 h-index: 0机构: CRISPR Therapeut, Cambridge, MA USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USADomm, J.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USAEustace, B. K.论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut, Boston, MA USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USAFoell, J.论文数: 0 引用数: 0 h-index: 0机构: Univ Regensburg, Regensburg, Germany Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USAde la Fuente, J.论文数: 0 引用数: 0 h-index: 0机构: Imperial Coll Healthcare NHS Trust, St Marys Hosp, London, England Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USAGrupp, S.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Childrens Hosp Philadelphia, Perelman Sch Med, Philadelphia, PA 19104 USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USAHandgretinger, R.论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Childrens Univ Hosp, Tubingen, Germany Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USAHo, T. W.论文数: 0 引用数: 0 h-index: 0机构: CRISPR Therapeut, Cambridge, MA USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USAKattamis, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Athens, Athens, Greece Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USAKernytsky, A.论文数: 0 引用数: 0 h-index: 0机构: CRISPR Therapeut, Cambridge, MA USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USALekstrom-Himes, J.论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut, Boston, MA USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USALi, A. M.论文数: 0 引用数: 0 h-index: 0机构: Univ British Columbia, BC Childrens Hosp, Vancouver, BC, Canada Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USALocatelli, F.论文数: 0 引用数: 0 h-index: 0机构: Sapienza Univ Rome, Osped Pediat Bambino Gesu Rome, Rome, Italy Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USAMapara, M. Y.论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ, New York, NY 10027 USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USAde Montalembert, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris, AP HP, Necker Enfants Malad Hosp, Paris, France Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USARondelli, D.论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Chicago, IL USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USASharma, A.论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, 332 N Lauderdale St, Memphis, TN 38105 USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USASheth, S.论文数: 0 引用数: 0 h-index: 0机构: Cornell Univ, Joan & Sanford I Weill Med Coll, New York, NY 10021 USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USASoni, S.论文数: 0 引用数: 0 h-index: 0机构: CRISPR Therapeut, Cambridge, MA USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USASteinberg, M. H.论文数: 0 引用数: 0 h-index: 0机构: Boston Univ, Sch Med, Boston, MA USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USAWall, D.论文数: 0 引用数: 0 h-index: 0机构: Univ Toronto, Hosp Sick Children, Toronto, ON, Canada Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USAYen, A.论文数: 0 引用数: 0 h-index: 0机构: Vertex Pharmaceut, Boston, MA USA Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USACorbacioglu, S.论文数: 0 引用数: 0 h-index: 0机构: Univ Regensburg, Regensburg, Germany Childrens Hosp TriStar Centennial, Sarah Cannon Ctr Blood Canc, 330 23rd Ave N,Suite 450, Nashville, TN 37203 USA
- [24] Advancing therapeutic complement inhibition in hematologic diseases: PNH and beyond[J]. BLOOD, 2022, 139 (25) : 3571 - 3582Gavriilaki, Eleni论文数: 0 引用数: 0 h-index: 0机构: G Papanicolaou Hosp, Hematol Dept, Thessaloniki, Greece G Papanicolaou Hosp, Hematol Dept, Thessaloniki, Greecede latour, Egis Peffault论文数: 0 引用数: 0 h-index: 0机构: St Louis Hosp, AP HP, French Reference Ctr Aplast Anemia & Paroxysmal N, Paris, France Univ Paris, BMT Unit, Paris, France European Grp Bone Marrow Transplantat, Severe Aplast Anemia Working Party, Avellino, Italy Azienda Osped Rilievo Nazl San Giuseppe M, Avellino, Italy G Papanicolaou Hosp, Hematol Dept, Thessaloniki, GreeceRisitano, Antonio Maria论文数: 0 引用数: 0 h-index: 0机构: European Grp Bone Marrow Transplantat, Severe Aplast Anemia Working Party, Avellino, Italy Univ Naples Federico II, Dept Clin Med & Surg, Naples, Italy G Papanicolaou Hosp, Hematol Dept, Thessaloniki, Greece
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- [27] Safety and Efficacy of Mitapivat in Pyruvate Kinase Deficiency[J]. NEW ENGLAND JOURNAL OF MEDICINE, 2019, 381 (10) : 933 - 944Grace, Rachael F.论文数: 0 引用数: 0 h-index: 0机构: Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA USA Harvard Med Sch, Boston, MA 02115 USA Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA USARose, Christian论文数: 0 引用数: 0 h-index: 0机构: Hop St Vincent de Paul, Lille, France Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA USALayton, D. Mark论文数: 0 引用数: 0 h-index: 0机构: Imperial Coll Healthcare NHS Trust, Hammersmith Hosp, London, England Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA USAGalacteros, Frederic论文数: 0 引用数: 0 h-index: 0机构: Ctr Hosp Univ Henri Mondor, Unite Malad Genet Globule Rouge, Creteil, France Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA USABarcellini, Wilma论文数: 0 引用数: 0 h-index: 0机构: Fdn IRCCS Ca Granda Osped Maggiore Policlin, Milan, Italy Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA USAMorton, D. Holmes论文数: 0 引用数: 0 h-index: 0机构: Cent Penn Clin, Belleville, PA USA Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA USAvan Beers, Eduard J.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Utrecht, Van Creveldklin, Utrecht, Netherlands Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA USAYaish, Hassan论文数: 0 引用数: 0 h-index: 0机构: Univ Utah, Salt Lake City, UT USA Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA USARavindranath, Yaddanapudi论文数: 0 引用数: 0 h-index: 0机构: Wayne State Univ, Childrens Hosp Michigan, Sch Med, Detroit, MI USA Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA USAKuo, Kevin H. M.论文数: 0 引用数: 0 h-index: 0机构: Univ Toronto, Toronto, ON, Canada Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA USASheth, Sujit论文数: 0 引用数: 0 h-index: 0机构: Weill Cornell Med Coll, New York, NY USA Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA USAKwiatkowski, Janet L.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA USABarbier, Ann J.论文数: 0 引用数: 0 h-index: 0机构: Agios Pharmaceut, Cambridge, MA USA Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA USABodie, Susan论文数: 0 引用数: 0 h-index: 0机构: Agios Pharmaceut, Cambridge, MA USA Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA USASilver, Bruce论文数: 0 引用数: 0 h-index: 0机构: Bruce A Silver Clin Sci & Dev, Dunkirk, MD USA Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA USAHua, Lei论文数: 0 引用数: 0 h-index: 0机构: Agios Pharmaceut, Cambridge, MA USA Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA USAKung, Charles论文数: 0 引用数: 0 h-index: 0机构: Agios Pharmaceut, Cambridge, MA USA Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA USAHawkins, Peter论文数: 0 引用数: 0 h-index: 0机构: Agios Pharmaceut, Cambridge, MA USA Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA USAJouvin, Marie-Helene论文数: 0 引用数: 0 h-index: 0机构: Agios Pharmaceut, Cambridge, MA USA Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA USABowden, Chris论文数: 0 引用数: 0 h-index: 0机构: Agios Pharmaceut, Cambridge, MA USA Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA USAGlader, Bertil论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Sch Med, Palo Alto, CA 94304 USA Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA USA
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