Accreditation model of European Haemophilia Centres in the era of novel treatments and gene therapy

被引：9

作者：

Boban, Ana ^{[1
,2
]}

Baghaei, Fariba ^{[3
]}

Karin, Fijnvandraat ^{[4
]}

Klamroth, Robert ^{[5
,6
]}

Miesbach, Wolfgang ^{[7
,8
]}

Stephensen, David ^{[9
]}

Kavanagh, Mary ^{[10
]}

Noone, Declan ^{[11
]}

Crato, Miguel ^{[11
]}

Peyvandi, Flora ^{[12
,13
]}

机构：

[1] Univ Hosp Ctr Zagreb, Haemophilia Ctr, Dept Haematol, Zagreb, Croatia

[2] Univ Zagreb, Sch Med, Zagreb, Croatia

[3] Sahlgrens Univ Hosp, Sect Haematol & Coagulat, Dept Med, Coagulat Ctr, Gothenburg, Sweden

[4] Univ Amsterdam, Emma Childrens Hosp, Amsterdam UMC, Pediat Hematol, Amsterdam, Netherlands

[5] Vivantes Clin Friedrichshain, Haemophilia Treatment Ctr, Dept Internal Med Vasc Med & Haemostaseol, Berlin, Germany

[6] Univ Bonn, Univ Hosp Bonn, Inst Expt Hematol & Transfus Med, Med Fac, Bonn, Germany

[7] Univ Hosp Frankfurt, Inst Transfus Med, Dept Haemostaseol, Med Clin 2, Frankfurt, Germany

[8] Univ Hosp Frankfurt, Inst Transfus Med, Haemophilia Ctr, Med Clin 2, Frankfurt, Germany

[9] East Kent Hosp Univ NHS Trust, Kent Haemophilia & Thrombosis Ctr, Canterbury, England

[10] Childrens Hlth Ireland Crumlin, Paediat Coagulat Ctr, Dublin, Ireland

[11] European Haemophilia Consortium, Brussels, Belgium

[12] Fdn IRCCS Ca Granda Osped Maggiore Policlin, Angelo Bianchi Bonomi Hemophilia & Thrombosis Ctr, Milan, Italy

[13] Univ Milan, Dept Pathophysiol & Transplantat, Milan, Italy

来源：

HAEMOPHILIA | 2023年 / 29卷 / 06期

关键词：

accreditation; certification; gene therapy; haemophilia; haemophilia centres; on-site audit; von Willebrand disease; COMPREHENSIVE CARE; HEALTH-CARE; STANDARDS; CERTIFICATION;

D O I：

10.1111/hae.14887

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

IntroductionThe international certification of haemophilia centres in Europe is run by the European Association of Haemophilia and Allied Disorders (EAHAD) and European Haemophilia Consortium (EHC) since 2013. The centres are designated as European Haemophilia Comprehensive Care Centres (EHCCC) or European Haemophilia Treatment Centres (EHTC), based on the specific requirements which evaluate centres' ability to provide care for patients with haemophilia and allied disorders.AimTo establish the new protocol for accreditation of European Haemophilia Centres.MethodsEAHAD, in collaboration with EHC, established Accreditation Working Group with the aim to define necessary measures to safeguard quality and improvement of bleeding disorders care throughout Europe and to build a novel model for accreditation of European Haemophilia Centres.ResultsThe European guidelines for certification of haemophilia centres have been updated to guidelines for the accreditation and include all the requirements regarding facilities, laboratory and personnel needed for optimal management of novel treatment options, including the introduction of the hub-and-spoke model for delivery of gene therapy. A pilot project for the accreditation of haemophilia centres including on-site audit has been designed.ConclusionImplementation of the novel accreditation protocol of the haemophilia treatment and haemophilia gene therapy centres has been made to further improve the quality of care for patients with haemophilia and other inherited bleeding disorders.

引用

页码：1442 / 1449

页数：8

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