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- [41] Nusinersen (Spinraza) for Spinal Muscular Atrophy MEDICAL LETTER ON DRUGS AND THERAPEUTICS, 2017, 59 (1517): : 50 - 52
- [44] Nusinersen for adults with spinal muscular atrophy Neurological Sciences, 2023, 44 : 2393 - 2400
- [49] Proxy-Reported Quality of Life and Access to Nusinersen Among Patients with Spinal Muscular Atrophy in Saudi Arabia PATIENT PREFERENCE AND ADHERENCE, 2021, 15 : 729 - 739
- [50] Spinal muscular atrophy 5Q-Treatment with nusinersen REVISTA DA ASSOCIACAO MEDICA BRASILEIRA, 2018, 64 (06): : 484 - 491