Impact of Nusinersen treatment on quality of life in adult patients with Spinal Muscular Atrophy

被引:0
|
作者
Castanon, Felix Guerra [1 ]
Deardorff, Adam [1 ]
Zhao, Songzhu [2 ]
Severyn, Steven [3 ]
Kelly, Kristrina [1 ]
Tellez, Marco [1 ]
Heintzman, Sarah [1 ]
Sterling, Gary [1 ]
Kolb, Stephen [1 ]
Arnold, David [4 ]
Elsheikh, Bakri [1 ]
机构
[1] Ohio State Univ, Neurol, Columbus, OH USA
[2] Ohio State Univ, Biomed Informat & Ctr Biostat, Columbus, OH USA
[3] Ohio State Univ, Anesthesiol, Columbus, OH USA
[4] Univ Missouri, Neurol, Columbia, MO USA
关键词
D O I
10.1212/WNL.0000000000204221
中图分类号
R74 [神经病学与精神病学];
学科分类号
摘要
P3-8.010
引用
收藏
页数:3
相关论文
共 50 条
  • [31] Neurodegeneration Biomarkers in Adult Spinal Muscular Atrophy (SMA) Patients Treated with Nusinersen
    Andres-Benito, Pol
    Vazquez-Costa, Juan Francisco
    Garzon, Nancy Carolina Nungo
    Colomina, Maria J.
    Marco, Carla
    Gonzalez, Laura
    Terrafeta, Cristina
    Dominguez, Raul
    Ferrer, Isidro
    Povedano, Monica
    INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES, 2024, 25 (07)
  • [32] Treatment with nusinersen in adult patients with spinal muscle atrophy in Slovenia
    Leonardis, L.
    Puksic, P.
    Avbelj, P.
    Petek, K.
    Luksa, M.
    Vucina, M.
    Kranjc, P.
    Klinar, P.
    Koritnik, B.
    EUROPEAN JOURNAL OF NEUROLOGY, 2020, 27 : 868 - 868
  • [33] Respiratory and Nutritional Effects of Nusinersen Treatment in Spinal Muscular Atrophy Patients
    Zver, A.
    Lepej, D.
    Kotnik, Pirs A.
    Praprotnik, M.
    Setina, Smid S.
    Butenko, T.
    Osredkar, D.
    Krivec, U.
    PEDIATRIC PULMONOLOGY, 2021, 56 : S131 - S131
  • [34] Nusinersen in adult patients with spinal muscular atrophy Observations from a single center
    Moshe-Lilie, Orly
    Visser, Amy
    Chahin, Nizar
    Ragole, Thomas
    Dimitrova, Diana
    Karam, Chafic
    NEUROLOGY, 2020, 95 (04) : E413 - E426
  • [35] Nusinersen treatment of spinal muscular atrophy - a systematic review
    Albrechtsen, Simon Sander
    Born, Alfred Peter
    Boesen, Magnus Spangsberg
    DANISH MEDICAL JOURNAL, 2020, 67 (09):
  • [36] The Antisense Oligonucleotide Nusinersen for Treatment of Spinal Muscular Atrophy
    Edinoff, Amber N.
    Nguyen, Long H.
    Odisho, Amira S.
    Maxey, Benjamin S.
    Pruitt, John W.
    Girma, Brook
    Cornett, Elyse M.
    Kaye, Adam M.
    Kaye, Alan D.
    ORTHOPEDIC REVIEWS, 2021, 13 (02)
  • [37] Quality of Life Outcomes According to Differential Nusinersen Exposure in Pediatric Spinal Muscular Atrophy
    Weaver, Meaghann S.
    Yuroff, Alice
    Sund, Sarah
    Hetzel, Scott
    Halanski, Matthew A.
    CHILDREN-BASEL, 2021, 8 (07):
  • [38] NUSINERSEN FOR TREATMENT OF SPINAL MUSCULAR ATROPHY: SCREENING AN ADULT POPULATION FOR CLINICAL TRIAL ELIGIBILITY
    Veloso, Eric
    Avila, J. David
    MUSCLE & NERVE, 2020, 62 : S32 - S32
  • [39] Serum creatine kinase and creatinine in adult spinal muscular atrophy under nusinersen treatment
    Freigang, Maren
    Wurster, Claudia D.
    Hagenacker, Tim
    Stolte, Benjamin
    Weiler, Markus
    Kamm, Christoph
    Schreiber-Katz, Olivia
    Osmanovic, Alma
    Petri, Susanne
    Kowski, Alexander
    Meyer, Thomas
    Koch, Jan C.
    Cordts, Isabell
    Deschauer, Marcus
    Lingor, Paul
    Aust, Elisa
    Petzold, Daniel
    Ludolph, Albert C.
    Falkenburger, Bjoern
    Hermann, Andreas
    Guenther, Rene
    ANNALS OF CLINICAL AND TRANSLATIONAL NEUROLOGY, 2021, 8 (05): : 1049 - 1063
  • [40] Correlates of health related quality of life in adult patients with spinal muscular atrophy
    Kruitwagen-Van Reenen, Esther Th
    Wadman, Renske I.
    Visser-Meily, Johanna Ma
    van den Berg, Leonard H.
    Schroder, Carin
    van der Pol, W. Ludo
    MUSCLE & NERVE, 2016, 54 (05) : 850 - 855