Safety and Efficacy of Liver-Directed AAV Gene Therapy in Privately Owned Dogs with Severe Hemophilia A

被引：0
|
作者：
Van Gorder, Lucas [1 ]
Doshi, Bhavya S. [1 ]
Willis, Elinor [2 ]
Nichols, Timothy C. [3 ]
Lanza, Matthew [2 ]
Cook, Emma [4 ]
Everett, John [4 ]
Merricks, Elizabeth [3 ]
Arruda, Valder R. [1 ]
Bushman, Frederic [4 ]
Samelson-Jones, Benjamin [1 ]
Callan, Mary Beth [5 ]
机构：
[1] Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapies, Philadelphia, PA USA
[2] Univ Penn, Dept Pathobiol, Sch Vet Med, Philadelphia, PA USA
[3] Univ N Carolina, Dept Pathol & Lab Med, Sch Med, Chapel Hill, NC USA
[4] Univ Penn, Dept Microbiol, Perelman Sch Med, Philadelphia, PA USA
[5] Univ Penn, Sch Vet Med, Dept Clin Sci & Adv Med, Philadelphia, PA USA
来源：
MOLECULAR THERAPY | 2023年 / 31卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
629
引用
收藏
页码：315 / 316
页数：2
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