Efficacy and safety outcomes with odevixibat treatment: Pooled data from the phase 3 ASSERT and ASSERT-EXT studies in patients with Alagille syndrome

被引:0
作者
Ovchinsky, Nadia [1 ]
Aumar, Madeleine [2 ]
Baker, Alastair [3 ]
Baumann, Ulrich [4 ]
Bufler, Philip [5 ]
Cananzi, Mara [6 ]
Durmaz, Ozlem [7 ]
Fischer, Ryan [8 ]
Indolfi, Giuseppe [9 ]
Karnsakul, Wikrom [10 ]
Lacaille, Florence [11 ]
Lee, Way Seah [12 ]
Maggiore, Giuseppe [13 ]
Rosenthal, Philip [14 ]
Ruiz, Mathias [15 ]
Sokal, Etienne [16 ]
Sturm, Ekkehard [17 ]
van der Woerd, Wendy L. [18 ]
Verkade, Henkjan J. [19 ]
Wehrman, Andrew [20 ]
Clemson, Christine [21 ]
Yu, Qifeng [21 ]
Ni, Quanhong [21 ]
Ruvido, Jessica [21 ]
Manganaro, Susan [21 ]
Mattsson, Jan [21 ]
Czubkowski, Piotr [22 ]
机构
[1] Albert Einstein Coll Med, Childrens Hosp, Div Paediat Gastroenterol Hepatol & Nutr, Bronx, NY USA
[2] Univ Lille, CHU Lille Pole Enfant, Paediat Gastroenterol Hepatol & Nutr, Inserm U1286 Infinite, Lille, France
[3] Kings Coll Hosp London, Paediat Liver Ctr, London, England
[4] Hannover Med Sch, Paediat Gastroenterol & Hepatol, Hannover, Germany
[5] Charite Univ Med Berlin, Dept Paediat Gastroenterol Nephrol & Metab Dis, Berlin, Germany
[6] Univ Hosp Padova, Dept Childrens & Womens Hlth, Paediatr Gastroenterol Digest Endoscopy Hepatol &, Padua, Italy
[7] Istanbul Univ, Istanbul Fac Med, Istanbul, Turkiye
[8] Childrens Mercy Hosp, Div Paediat Gastroenterol Hepatol & Nutr, Kansas City, MO USA
[9] Meyer Childrens Univ Hosp Florence, Paediat & Liver Unit, Florence, Italy
[10] Johns Hopkins Univ, Dept Paediat, Div Paediat Gastroenterol Nutr & Hepatol, Sch Med, Baltimore, MD USA
[11] Hop Univ Necker Enfants Malades, Paediat Gastroenterol Hepatol Nutr Unit, Paris, France
[12] Univ Malaya, Dept Paediat, Fac Med, Kuala Lumpur, Malaysia
[13] Bambino Gesu Childrens Hosp IRCCS, Hepatol Gastroenterol Nutr Digest Endoscopy & Liv, Rome, Italy
[14] Univ Calif San Francisco, Div Gastroenterol Hepatol & Nutr, Dept Paediat, San Francisco, CA USA
[15] Hosp Civils Lyon, Dept Paediat Gastroenterol Hepatol & Nutr, Hop Femme Mere Enfant, Lyon, France
[16] Catholic Univ Louvain, Clin St Luc, Ottignies, Belgium
[17] Univ Childrens Hosp Tubingen, Paediatr Gastroenterol & Hepatol, Tubingen, Germany
[18] Univ Med Ctr Utrecht, Wilhelmina Childrens Hosp, Dept Paediat Gastroenterol, Utrecht, Netherlands
[19] Univ Groningen, Beatrix Childrens Hosp, Dept Paediat, Univ Med Ctr Groningen, Groningen, Netherlands
[20] Boston Childrens Hosp, Div Gastroenterol Hepatol & Nutr, Boston, MA USA
[21] Albireo Pharma Inc, Boston, MA USA
[22] Childrens Mem Hlth Inst, Dept Gastroenterol Hepatol Nutrit Disorders & Pae, Warsaw, Poland
关键词
D O I
暂无
中图分类号
R57 [消化系及腹部疾病];
学科分类号
摘要
THU-284
引用
收藏
页码:S965 / S966
页数:2
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