共 31 条
- [1] Repeated nebulisation of non-viral CFTR gene therapy in patients with cystic fibrosis: a randomised, double-blind, placebo-controlled, phase 2b trial[J]. LANCET RESPIRATORY MEDICINE, 2015, 3 (09) : 684 - 691Alton, Eric W. F. W.论文数: 0 引用数: 0 h-index: 0机构: Univ London Imperial Coll Sci Technol & Med, London, England Royal Brompton & Harefield NHS Fdn Trust, London, EnglandArmstrong, David K.论文数: 0 引用数: 0 h-index: 0机构: Royal Hosp Sick Children, Edinburgh EH9 1LF, Midlothian, Scotland Royal Brompton & Harefield NHS Fdn Trust, London, EnglandAshby, Deborah论文数: 0 引用数: 0 h-index: 0机构: Univ London Imperial Coll Sci Technol & Med, London, England Royal Brompton & Harefield NHS Fdn Trust, London, EnglandBayfield, Katie J.论文数: 0 引用数: 0 h-index: 0机构: Univ London Imperial Coll Sci Technol & Med, London, England Royal Brompton & Harefield NHS Fdn Trust, London, EnglandBilton, Diana论文数: 0 引用数: 0 h-index: 0机构: Royal Brompton & Harefield NHS Fdn Trust, London, England Royal Brompton & Harefield NHS Fdn Trust, London, EnglandBloomfield, Emily V.论文数: 0 引用数: 0 h-index: 0机构: Univ London Imperial Coll Sci Technol & Med, London, England Royal Brompton & Harefield NHS Fdn Trust, London, EnglandBoyd, A. Christopher论文数: 0 引用数: 0 h-index: 0机构: Univ Edinburgh, Inst Genet & Mol Med, Ctr Genom & Expt Med, Edinburgh, Midlothian, Scotland Royal Brompton & Harefield NHS Fdn Trust, London, EnglandBrand, June论文数: 0 引用数: 0 h-index: 0机构: Univ Edinburgh, Inst Genet & Mol Med, Ctr Genom & Expt Med, Edinburgh, Midlothian, Scotland Royal Brompton & Harefield NHS Fdn Trust, London, EnglandBuchan, Ruaridh论文数: 0 引用数: 0 h-index: 0机构: Western Gen Hosp, Edinburgh EH4 2XU, Midlothian, Scotland Royal Brompton & Harefield NHS Fdn Trust, London, EnglandCalcedo, Roberto论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA USA Royal Brompton & Harefield NHS Fdn Trust, London, EnglandCarvelli, Paula论文数: 0 引用数: 0 h-index: 0机构: Univ London Imperial Coll Sci Technol & Med, London, England Royal Brompton & Harefield NHS Fdn Trust, London, EnglandChan, Mario论文数: 0 引用数: 0 h-index: 0机构: Univ London Imperial Coll Sci Technol & Med, London, England Royal Brompton & Harefield NHS Fdn Trust, London, EnglandCheng, Seng H.论文数: 0 引用数: 0 h-index: 0机构: Genzyme, Framingham, MA USA Royal Brompton & Harefield NHS Fdn Trust, London, EnglandCollie, D. David S.论文数: 0 引用数: 0 h-index: 0机构: Univ Edinburgh, Roslin Inst, Edinburgh, Midlothian, Scotland Univ Edinburgh, R D SVS, Edinburgh, Midlothian, Scotland Royal Brompton & Harefield NHS Fdn Trust, London, EnglandCunningham, Steve论文数: 0 引用数: 0 h-index: 0机构: Royal Hosp Sick Children, Edinburgh EH9 1LF, Midlothian, Scotland Royal Brompton & Harefield NHS Fdn Trust, London, EnglandDavidson, Heather E.论文数: 0 引用数: 0 h-index: 0机构: Univ Edinburgh, Inst Genet & Mol Med, Ctr Genom & Expt Med, Edinburgh, Midlothian, Scotland Royal Brompton & Harefield NHS Fdn Trust, London, EnglandDavies, Gwyneth论文数: 0 引用数: 0 h-index: 0机构: Univ London Imperial Coll Sci Technol & Med, London, England Royal Brompton & Harefield NHS Fdn Trust, London, EnglandDavies, Jane C.论文数: 0 引用数: 0 h-index: 0机构: Univ London Imperial Coll Sci Technol & Med, London, England Royal Brompton & Harefield NHS Fdn Trust, London, EnglandDavies, Lee A.论文数: 0 引用数: 0 h-index: 0机构: Univ Oxford, Radcliff Dept Med, Nuffield Div Clin Lab Sci, Oxford, England Royal Brompton & Harefield NHS Fdn Trust, London, EnglandDewar, Maria H.论文数: 0 引用数: 0 h-index: 0机构: Western Gen Hosp, Edinburgh EH4 2XU, Midlothian, Scotland Royal Brompton & Harefield NHS Fdn Trust, London, EnglandDoherty, Ann论文数: 0 引用数: 0 h-index: 0机构: Univ Edinburgh, Inst Genet & Mol Med, Ctr Genom & Expt Med, Edinburgh, Midlothian, Scotland Royal Brompton & Harefield NHS Fdn Trust, London, EnglandDonovan, Jackie论文数: 0 引用数: 0 h-index: 0机构: Royal Brompton & Harefield NHS Fdn Trust, London, England Royal Brompton & Harefield NHS Fdn Trust, London, EnglandDwyer, Natalie S.论文数: 0 引用数: 0 h-index: 0机构: Univ London Imperial Coll Sci Technol & Med, London, England Royal Brompton & Harefield NHS Fdn Trust, London, EnglandElgmati, Hala I.论文数: 0 引用数: 0 h-index: 0机构: Western Gen Hosp, Edinburgh EH4 2XU, Midlothian, Scotland Royal Brompton & Harefield NHS Fdn Trust, London, EnglandFeatherstone, Rosanna F.论文数: 0 引用数: 0 h-index: 0机构: Univ London Imperial Coll Sci Technol & Med, London, England Royal Brompton & Harefield NHS Fdn Trust, London, EnglandGavino, Jemyr论文数: 0 引用数: 0 h-index: 0机构: Univ London Imperial Coll Sci Technol & Med, London, England Royal Brompton & Harefield NHS Fdn Trust, London, EnglandGea-Sorli, Sabrina论文数: 0 引用数: 0 h-index: 0机构: Univ London Imperial Coll Sci Technol & Med, London, England Royal Brompton & Harefield NHS Fdn Trust, London, EnglandGeddes, Duncan M.论文数: 0 引用数: 0 h-index: 0机构: Royal Brompton & Harefield NHS Fdn Trust, London, England Royal Brompton & Harefield NHS Fdn Trust, London, EnglandGibson, James S. R.论文数: 0 引用数: 0 h-index: 0机构: Univ Edinburgh, Inst Genet & Mol Med, Ctr Genom & Expt Med, Edinburgh, Midlothian, Scotland Royal Brompton & Harefield NHS Fdn Trust, London, EnglandGill, Deborah R.论文数: 0 引用数: 0 h-index: 0机构: Univ Oxford, Radcliff Dept Med, Nuffield Div Clin Lab Sci, Oxford, England Royal Brompton & Harefield NHS Fdn Trust, London, EnglandGreening, Andrew P.论文数: 0 引用数: 0 h-index: 0机构: Western Gen Hosp, Edinburgh EH4 2XU, Midlothian, Scotland Royal Brompton & Harefield NHS Fdn Trust, London, EnglandGriesenbach, Uta论文数: 0 引用数: 0 h-index: 0机构: Univ London Imperial Coll Sci Technol & Med, London, England Royal Brompton & Harefield NHS Fdn Trust, London, EnglandHansell, David M.论文数: 0 引用数: 0 h-index: 0机构: Royal Brompton & Harefield NHS Fdn Trust, London, England Royal Brompton & Harefield NHS Fdn Trust, London, EnglandHarman, Katharine论文数: 0 引用数: 0 h-index: 0机构: Univ London Imperial Coll Sci Technol & Med, London, England Royal Brompton & Harefield NHS Fdn Trust, London, EnglandHiggins, Tracy E.论文数: 0 引用数: 0 h-index: 0机构: Univ London Imperial Coll Sci Technol & Med, London, England Royal Brompton & Harefield NHS Fdn Trust, London, EnglandHodges, Samantha L.论文数: 0 引用数: 0 h-index: 0机构: Royal Brompton & Harefield NHS Fdn Trust, London, EnglandHyde, Stephen C.论文数: 0 引用数: 0 h-index: 0机构: Univ Oxford, Radcliff Dept Med, Nuffield Div Clin Lab Sci, Oxford, England Royal Brompton & Harefield NHS Fdn Trust, London, EnglandHyndman, Laura论文数: 0 引用数: 0 h-index: 0机构: Univ Edinburgh, Inst Genet & Mol Med, Ctr Genom & Expt Med, Edinburgh, Midlothian, Scotland Royal Brompton & Harefield NHS Fdn Trust, London, EnglandInnes, J. Alastair论文数: 0 引用数: 0 h-index: 0机构: Western Gen Hosp, Edinburgh EH4 2XU, Midlothian, Scotland Royal Brompton & Harefield NHS Fdn Trust, London, EnglandJacob, Joseph论文数: 0 引用数: 0 h-index: 0机构: Royal Brompton & Harefield NHS Fdn Trust, London, England Royal Brompton & Harefield NHS Fdn Trust, London, EnglandJones, Nancy论文数: 0 引用数: 0 h-index: 0机构: Royal Brompton & Harefield NHS Fdn Trust, London, England Royal Brompton & Harefield NHS Fdn Trust, London, EnglandKeogh, Brian F.论文数: 0 引用数: 0 h-index: 0机构: Royal Brompton & Harefield NHS Fdn Trust, London, England Royal Brompton & Harefield NHS Fdn Trust, London, EnglandLimberis, Maria P.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Dept Pathol & Lab Med, Gene Therapy Program, Philadelphia, PA USA Royal Brompton & Harefield NHS Fdn Trust, London, EnglandLloyd-Evans, Paul论文数: 0 引用数: 0 h-index: 0机构: NHS Blood & Transplant, Bristol, Avon, England Royal Brompton & Harefield NHS Fdn Trust, London, EnglandMaclean, Alan W.论文数: 0 引用数: 0 h-index: 0机构: Univ Edinburgh, Inst Genet & Mol Med, Ctr Genom & Expt Med, Edinburgh, Midlothian, Scotland Royal Brompton & Harefield NHS Fdn Trust, London, EnglandManvell, Michelle C.论文数: 0 引用数: 0 h-index: 0机构: Univ London Imperial Coll Sci Technol & Med, London, England Royal Brompton & Harefield NHS Fdn Trust, London, EnglandMcCormick, Dominique论文数: 0 引用数: 0 h-index: 0机构: Univ Oxford, Radcliff Dept Med, Nuffield Div Clin Lab Sci, Oxford, England Royal Brompton & Harefield NHS Fdn Trust, London, EnglandMcGovern, Michael论文数: 0 引用数: 0 h-index: 0机构: Western Gen Hosp, Edinburgh EH4 2XU, Midlothian, Scotland Royal Brompton & Harefield NHS Fdn Trust, London, England论文数: 引用数: h-index:机构:Meng, Cuixiang论文数: 0 引用数: 0 h-index: 0机构: Royal Brompton & Harefield NHS Fdn Trust, London, England
- [2] Cationic lipid-mediated CFTR gene transfer to the lungs and nose of patients with cystic fibrosis:: a double-blind placebo-controlled trial[J]. LANCET, 1999, 353 (9157) : 947 - 954Alton, EWFW论文数: 0 引用数: 0 h-index: 0机构: Natl Heart & Lung Inst, Imperial Coll, Dept Gene Therapy, London SW3 6LR, England Natl Heart & Lung Inst, Imperial Coll, Dept Gene Therapy, London SW3 6LR, EnglandStern, M论文数: 0 引用数: 0 h-index: 0机构: Natl Heart & Lung Inst, Imperial Coll, Dept Gene Therapy, London SW3 6LR, EnglandFarley, R论文数: 0 引用数: 0 h-index: 0机构: Natl Heart & Lung Inst, Imperial Coll, Dept Gene Therapy, London SW3 6LR, EnglandJaffe, A论文数: 0 引用数: 0 h-index: 0机构: Natl Heart & Lung Inst, Imperial Coll, Dept Gene Therapy, London SW3 6LR, EnglandChadwick, SL论文数: 0 引用数: 0 h-index: 0机构: Natl Heart & Lung Inst, Imperial Coll, Dept Gene Therapy, London SW3 6LR, EnglandPhillips, J论文数: 0 引用数: 0 h-index: 0机构: Natl Heart & Lung Inst, Imperial Coll, Dept Gene Therapy, London SW3 6LR, EnglandDavies, J论文数: 0 引用数: 0 h-index: 0机构: Natl Heart & Lung Inst, Imperial Coll, Dept Gene Therapy, London SW3 6LR, EnglandSmith, SN论文数: 0 引用数: 0 h-index: 0机构: Natl Heart & Lung Inst, Imperial Coll, Dept Gene Therapy, London SW3 6LR, EnglandBrowning, J论文数: 0 引用数: 0 h-index: 0机构: Natl Heart & Lung Inst, Imperial Coll, Dept Gene Therapy, London SW3 6LR, EnglandDavies, MG论文数: 0 引用数: 0 h-index: 0机构: Natl Heart & Lung Inst, Imperial Coll, Dept Gene Therapy, London SW3 6LR, EnglandHodson, ME论文数: 0 引用数: 0 h-index: 0机构: Natl Heart & Lung Inst, Imperial Coll, Dept Gene Therapy, London SW3 6LR, EnglandDurham, SR论文数: 0 引用数: 0 h-index: 0机构: Natl Heart & Lung Inst, Imperial Coll, Dept Gene Therapy, London SW3 6LR, EnglandLi, D论文数: 0 引用数: 0 h-index: 0机构: Natl Heart & Lung Inst, Imperial Coll, Dept Gene Therapy, London SW3 6LR, EnglandJeffery, PK论文数: 0 引用数: 0 h-index: 0机构: Natl Heart & Lung Inst, Imperial Coll, Dept Gene Therapy, London SW3 6LR, EnglandScallan, M论文数: 0 引用数: 0 h-index: 0机构: Natl Heart & Lung Inst, Imperial Coll, Dept Gene Therapy, London SW3 6LR, EnglandBalfour, R论文数: 0 引用数: 0 h-index: 0机构: Natl Heart & Lung Inst, Imperial Coll, Dept Gene Therapy, London SW3 6LR, EnglandEastman, SJ论文数: 0 引用数: 0 h-index: 0机构: Natl Heart & Lung Inst, Imperial Coll, Dept Gene Therapy, London SW3 6LR, EnglandCheng, SH论文数: 0 引用数: 0 h-index: 0机构: Natl Heart & Lung Inst, Imperial Coll, Dept Gene Therapy, London SW3 6LR, EnglandSmith, AE论文数: 0 引用数: 0 h-index: 0机构: Natl Heart & Lung Inst, Imperial Coll, Dept Gene Therapy, London SW3 6LR, EnglandMeeker, D论文数: 0 引用数: 0 h-index: 0机构: Natl Heart & Lung Inst, Imperial Coll, Dept Gene Therapy, London SW3 6LR, EnglandGeddes, DM论文数: 0 引用数: 0 h-index: 0机构: Natl Heart & Lung Inst, Imperial Coll, Dept Gene Therapy, London SW3 6LR, England
- [3] Systemic Messenger RNA Therapy as a Treatment for Methylmalonic Acidemia[J]. CELL REPORTS, 2017, 21 (12): : 3548 - 3558An, Ding论文数: 0 引用数: 0 h-index: 0机构: Moderna Therapeut, Cambridge, MA 02139 USA Moderna Therapeut, Cambridge, MA 02139 USASchneller, Jessica L.论文数: 0 引用数: 0 h-index: 0机构: NIH, Natl Human Genome Res Inst, Med Genom & Metab Genet Branch, Organ Acid Res Sect, Bethesda, MD 20892 USA Moderna Therapeut, Cambridge, MA 02139 USAFrassetto, Andrea论文数: 0 引用数: 0 h-index: 0机构: Moderna Therapeut, Cambridge, MA 02139 USA Moderna Therapeut, Cambridge, MA 02139 USALiang, Shi论文数: 0 引用数: 0 h-index: 0机构: Moderna Therapeut, Cambridge, MA 02139 USA Moderna Therapeut, Cambridge, MA 02139 USAZhu, Xuling论文数: 0 引用数: 0 h-index: 0机构: Moderna Therapeut, Cambridge, MA 02139 USA Moderna Therapeut, Cambridge, MA 02139 USAPark, Ji-Sun论文数: 0 引用数: 0 h-index: 0机构: Moderna Therapeut, Cambridge, MA 02139 USA Moderna Therapeut, Cambridge, MA 02139 USATheisen, Matt论文数: 0 引用数: 0 h-index: 0机构: Moderna Therapeut, Cambridge, MA 02139 USA Moderna Therapeut, Cambridge, MA 02139 USAHong, Sue-Jean论文数: 0 引用数: 0 h-index: 0机构: Moderna Therapeut, Cambridge, MA 02139 USA Moderna Therapeut, Cambridge, MA 02139 USAZhou, Jenny论文数: 0 引用数: 0 h-index: 0机构: Moderna Therapeut, Cambridge, MA 02139 USA Moderna Therapeut, Cambridge, MA 02139 USARajendran, Raj论文数: 0 引用数: 0 h-index: 0机构: Moderna Therapeut, Cambridge, MA 02139 USA Moderna Therapeut, Cambridge, MA 02139 USALevy, Becca论文数: 0 引用数: 0 h-index: 0机构: Moderna Therapeut, Cambridge, MA 02139 USA Moderna Therapeut, Cambridge, MA 02139 USAHowell, Rebecca论文数: 0 引用数: 0 h-index: 0机构: Moderna Therapeut, Cambridge, MA 02139 USA Moderna Therapeut, Cambridge, MA 02139 USABesin, Gilles论文数: 0 引用数: 0 h-index: 0机构: Moderna Therapeut, Cambridge, MA 02139 USA Moderna Therapeut, Cambridge, MA 02139 USAPresnyak, Vladimir论文数: 0 引用数: 0 h-index: 0机构: Moderna Therapeut, Cambridge, MA 02139 USA Moderna Therapeut, Cambridge, MA 02139 USASabnis, Staci论文数: 0 引用数: 0 h-index: 0机构: Moderna Therapeut, Cambridge, MA 02139 USA Moderna Therapeut, Cambridge, MA 02139 USAMurphy-Benenato, Kerry E.论文数: 0 引用数: 0 h-index: 0机构: Moderna Therapeut, Cambridge, MA 02139 USA Moderna Therapeut, Cambridge, MA 02139 USAKumarasinghe, E. Sathyajith论文数: 0 引用数: 0 h-index: 0机构: Moderna Therapeut, Cambridge, MA 02139 USA Moderna Therapeut, Cambridge, MA 02139 USASalerno, Timothy论文数: 0 引用数: 0 h-index: 0机构: Moderna Therapeut, Cambridge, MA 02139 USA Moderna Therapeut, Cambridge, MA 02139 USAMihai, Cosmin论文数: 0 引用数: 0 h-index: 0机构: Moderna Therapeut, Cambridge, MA 02139 USA Moderna Therapeut, Cambridge, MA 02139 USALukacs, Christine M.论文数: 0 引用数: 0 h-index: 0机构: Moderna Therapeut, Cambridge, MA 02139 USA Moderna Therapeut, Cambridge, MA 02139 USAChandler, Randy J.论文数: 0 引用数: 0 h-index: 0机构: NIH, Natl Human Genome Res Inst, Med Genom & Metab Genet Branch, Organ Acid Res Sect, Bethesda, MD 20892 USA Moderna Therapeut, Cambridge, MA 02139 USAGuey, Lin T.论文数: 0 引用数: 0 h-index: 0机构: Moderna Therapeut, Cambridge, MA 02139 USA Moderna Therapeut, Cambridge, MA 02139 USAVenditti, Charles P.论文数: 0 引用数: 0 h-index: 0机构: NIH, Natl Human Genome Res Inst, Med Genom & Metab Genet Branch, Organ Acid Res Sect, Bethesda, MD 20892 USA Moderna Therapeut, Cambridge, MA 02139 USAMartini, Paolo G. V.论文数: 0 引用数: 0 h-index: 0机构: Moderna Therapeut, Cambridge, MA 02139 USA Moderna Therapeut, Cambridge, MA 02139 USA
- [4] [Anonymous], 2022, Cystic fibrosis foundation patient registry highlights
- [5] Efficacy and Safety of the mRNA-1273 SARS-CoV-2 Vaccine[J]. NEW ENGLAND JOURNAL OF MEDICINE, 2021, 384 (05) : 403 - 416Baden, Lindsey R.论文数: 0 引用数: 0 h-index: 0机构: Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USAEl Sahly, Hana M.论文数: 0 引用数: 0 h-index: 0机构: Baylor Coll Med, Houston, TX 77030 USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USAEssink, Brandon论文数: 0 引用数: 0 h-index: 0机构: Meridian Clin Res, Savannah, GA USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USAKotloff, Karen论文数: 0 引用数: 0 h-index: 0机构: Univ Maryland, Sch Med, Baltimore, MD 21201 USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USAFrey, Sharon论文数: 0 引用数: 0 h-index: 0机构: St Louis Univ, Sch Med, St Louis, MO 63103 USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USANovak, Rick论文数: 0 引用数: 0 h-index: 0机构: Univ Illinois, Chicago, IL USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USA论文数: 引用数: h-index:机构:Spector, Stephen A.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, San Diego, CA 92103 USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USA论文数: 引用数: h-index:机构:Creech, C. Buddy论文数: 0 引用数: 0 h-index: 0机构: Vanderbilt Univ, Sch Med, Nashville, TN 37212 USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USAMcGettigan, John论文数: 0 引用数: 0 h-index: 0机构: Qual Life Med & Res Ctr, Tucson, AZ USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USAKhetan, Shishir论文数: 0 引用数: 0 h-index: 0机构: Meridian Clin Res, Savannah, GA USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USASegall, Nathan论文数: 0 引用数: 0 h-index: 0机构: Atlanta Clin Res Ctr, Atlanta, GA USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USASolis, Joel论文数: 0 引用数: 0 h-index: 0机构: Centex Studies, Houston, TX USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USABrosz, Adam论文数: 0 引用数: 0 h-index: 0机构: Meridian Clin Res, Savannah, GA USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USAFierro, Carlos论文数: 0 引用数: 0 h-index: 0机构: Johnson Cty Clin Trials, Lenexa, KS USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USASchwartz, Howard论文数: 0 引用数: 0 h-index: 0机构: Res Ctr Amer, Hollywood, FL USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USANeuzil, Kathleen论文数: 0 引用数: 0 h-index: 0机构: Univ Maryland, Sch Med, Baltimore, MD 21201 USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USACorey, Larry论文数: 0 引用数: 0 h-index: 0机构: Fred Hutchinson Canc Res Ctr, 1124 Columbia St, Seattle, WA 98104 USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USAGilbert, Peter论文数: 0 引用数: 0 h-index: 0机构: Fred Hutchinson Canc Res Ctr, 1124 Columbia St, Seattle, WA 98104 USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USAJanes, Holly论文数: 0 引用数: 0 h-index: 0机构: Fred Hutchinson Canc Res Ctr, 1124 Columbia St, Seattle, WA 98104 USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USAFollmann, Dean论文数: 0 引用数: 0 h-index: 0机构: NIAID, 9000 Rockville Pike, Bethesda, MD 20892 USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USAMarovich, Mary论文数: 0 引用数: 0 h-index: 0机构: NIAID, 9000 Rockville Pike, Bethesda, MD 20892 USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USAMascola, John论文数: 0 引用数: 0 h-index: 0机构: NIAID, 9000 Rockville Pike, Bethesda, MD 20892 USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USAPolakowski, Laura论文数: 0 引用数: 0 h-index: 0机构: NIAID, 9000 Rockville Pike, Bethesda, MD 20892 USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USALedgerwood, Julie论文数: 0 引用数: 0 h-index: 0机构: NIAID, 9000 Rockville Pike, Bethesda, MD 20892 USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USAGraham, Barney S.论文数: 0 引用数: 0 h-index: 0机构: NIAID, 9000 Rockville Pike, Bethesda, MD 20892 USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USABennett, Hamilton论文数: 0 引用数: 0 h-index: 0机构: Moderna, Cambridge, MA USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USAPajon, Rolando论文数: 0 引用数: 0 h-index: 0机构: Moderna, Cambridge, MA USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USAKnightly, Conor论文数: 0 引用数: 0 h-index: 0机构: Moderna, Cambridge, MA USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USALeav, Brett论文数: 0 引用数: 0 h-index: 0机构: Moderna, Cambridge, MA USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USADeng, Weiping论文数: 0 引用数: 0 h-index: 0机构: Moderna, Cambridge, MA USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USAZhou, Honghong论文数: 0 引用数: 0 h-index: 0机构: Moderna, Cambridge, MA USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USAHan, Shu论文数: 0 引用数: 0 h-index: 0机构: Moderna, Cambridge, MA USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USAIvarsson, Melanie论文数: 0 引用数: 0 h-index: 0机构: Moderna, Cambridge, MA USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USAMiller, Jacqueline论文数: 0 引用数: 0 h-index: 0机构: Moderna, Cambridge, MA USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USAZaks, Tal论文数: 0 引用数: 0 h-index: 0机构: Moderna, Cambridge, MA USA Brigham & Womens Hosp, 75 Francis St, Boston, MA 02115 USA
- [6] Barbier A, 2018, PEDIATR PULM, V53, P253
- [7] Barbier A, 2022, patent application publication, Patent No. 2021021988
- [8] The future of cystic fibrosis care: a global perspective[J]. LANCET RESPIRATORY MEDICINE, 2020, 8 (01) : 65 - 124Bell, Scott C.论文数: 0 引用数: 0 h-index: 0机构: Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, Australia QIMR Berghofer Med Res Inst, Brisbane, Qld, Australia Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, AustraliaMall, Marcus A.论文数: 0 引用数: 0 h-index: 0机构: Charite Univ Med Berlin, Berlin Inst Hlth, Berlin, Germany German Ctr Lung Res, Berlin, Germany Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, AustraliaGutierrez, Hector论文数: 0 引用数: 0 h-index: 0机构: Univ Alabama Birmingham, Birmingham, AL USA Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, AustraliaMacek, Milan论文数: 0 引用数: 0 h-index: 0机构: Charles Univ Prague, Motol Univ Hosp, Fac Med 2, Dept Biol & Med Genet, Prague, Czech Republic Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, AustraliaMadge, Susan论文数: 0 引用数: 0 h-index: 0机构: Royal Brompton & Harefield NHS Fdn Trust, London, England Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, AustraliaDavies, Jane C.论文数: 0 引用数: 0 h-index: 0机构: Royal Brompton & Harefield NHS Fdn Trust, London, England Imperial Coll, Natl Heart & Lung Inst, London, England Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, AustraliaBurgel, Pierre-Regis论文数: 0 引用数: 0 h-index: 0机构: Hop Cochin, AP HP, Paris, France Univ Paris 05, Inst Cochin, Paris, France Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, AustraliaTullis, Elizabeth论文数: 0 引用数: 0 h-index: 0机构: St Michaels Hosp, Toronto, ON, Canada Univ Toronto, Toronto, ON, Canada Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, AustraliaCastaos, Claudio论文数: 0 引用数: 0 h-index: 0机构: Hosp Pediat Juan P Garralian, Buenos Aires, DF, Argentina Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, AustraliaCastellani, Carlo论文数: 0 引用数: 0 h-index: 0机构: IRCCS, Ist Giannina Gaslini, Cyst Fibrosis Ctr, Genoa, Italy Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, AustraliaByrnes, Catherine A.论文数: 0 引用数: 0 h-index: 0机构: Starship Childrens Hosp, Auckland, New Zealand Univ Auckland, Auckland, New Zealand Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, AustraliaCathcart, Fiona论文数: 0 引用数: 0 h-index: 0机构: Royal Brompton & Harefield NHS Fdn Trust, London, England Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, AustraliaChotirmall, Sanjay H.论文数: 0 引用数: 0 h-index: 0机构: Nanyang Technol Univ, Lee Kong Chian Sch Med, Singapore, Singapore Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, AustraliaCosgriff, Rebecca论文数: 0 引用数: 0 h-index: 0机构: Cyst Fibrosis Trust, London, England Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, AustraliaEichler, Irmgard论文数: 0 引用数: 0 h-index: 0机构: European Med Agcy, Amsterdam, Netherlands Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, Australia论文数: 引用数: h-index:机构:Goss, Christopher H.论文数: 0 引用数: 0 h-index: 0机构: Univ Washington, Seattle, WA 98195 USA Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, Australia论文数: 引用数: h-index:机构:Farrell, Philip M.论文数: 0 引用数: 0 h-index: 0机构: Univ Wisconsin, Madison, WI USA Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, AustraliaGravelle, Anna M.论文数: 0 引用数: 0 h-index: 0机构: British Columbia Childrens Hosp, Cyst Fibrosis Clin, Vancouver, BC, Canada Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, AustraliaHavermans, Trudy论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Leuven, Cyst FibrosisCtr, Leuven, Belgium Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, AustraliaMayer-Hamblett, Nicole论文数: 0 引用数: 0 h-index: 0机构: Univ Washington, Seattle, WA 98195 USA Seattle Childrens Res Inst, Seattle, WA USA Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, AustraliaKashirskaya, Nataliya论文数: 0 引用数: 0 h-index: 0机构: Res Ctr Med Genet, Moscow, Russia Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, AustraliaKerem, Eitan论文数: 0 引用数: 0 h-index: 0机构: Hadassah Med Ctr, Jerusalem, Israel Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, AustraliaMathew, Joseph L.论文数: 0 引用数: 0 h-index: 0机构: Post Grad Inst Med Educ & Res, Chandigarh, India Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, AustraliaMcKone, Edward F.论文数: 0 引用数: 0 h-index: 0机构: Univ Coll Dublin, Sch Med, St Vincents Univ Hosp, Dublin, Ireland Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, Australia论文数: 引用数: h-index:机构:Nasr, Samya Z.论文数: 0 引用数: 0 h-index: 0机构: CS Mott Childrens Hosp, Ann Arbor, MI USA Univ Michigan, Ann Arbor, MI 48109 USA Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, AustraliaOates, Gabriela R.论文数: 0 引用数: 0 h-index: 0机构: Univ Alabama Birmingham, Birmingham, AL USA Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, Australia论文数: 引用数: h-index:机构:Pypops, Ulrike论文数: 0 引用数: 0 h-index: 0机构: Jessa Ziekenhuis, Holsbeek, Belgium Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, AustraliaRaraigh, Karen S.论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, Baltimore, MD USA Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, AustraliaRowe, Steven M.论文数: 0 引用数: 0 h-index: 0机构: Univ Alabama Birmingham, Birmingham, AL USA Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, AustraliaSouthern, Kevin W.论文数: 0 引用数: 0 h-index: 0机构: Alder Hey Childrens Hosp, Liverpool, Merseyside, England Univ Liverpool, Liverpool, Merseyside, England Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, AustraliaSivam, Sheila论文数: 0 引用数: 0 h-index: 0机构: Royal Prince Alfred Hosp, Sydney, NSW, Australia Woolcock Inst Med Res, Sydney, NSW, Australia Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, AustraliaStephenson, Anne L.论文数: 0 引用数: 0 h-index: 0机构: St Michaels Hosp, Toronto, ON, Canada Univ Toronto, Toronto, ON, Canada Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, Australia论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:
- [9] Innate antiviral responses by means of TLR7-mediated recognition of single-stranded RNA[J]. SCIENCE, 2004, 303 (5663) : 1529 - 1531Diebold, SS论文数: 0 引用数: 0 h-index: 0机构: London Res Inst, Canc Res UK, Immunobiol Lab, London WC2A 3PX, EnglandKaisho, T论文数: 0 引用数: 0 h-index: 0机构: London Res Inst, Canc Res UK, Immunobiol Lab, London WC2A 3PX, EnglandHemmi, H论文数: 0 引用数: 0 h-index: 0机构: London Res Inst, Canc Res UK, Immunobiol Lab, London WC2A 3PX, EnglandAkira, S论文数: 0 引用数: 0 h-index: 0机构: London Res Inst, Canc Res UK, Immunobiol Lab, London WC2A 3PX, EnglandSousa, CRE论文数: 0 引用数: 0 h-index: 0机构: London Res Inst, Canc Res UK, Immunobiol Lab, London WC2A 3PX, England London Res Inst, Canc Res UK, Immunobiol Lab, London WC2A 3PX, England
- [10] Leveraging Rational Protein Engineering to Improve mRNA Therapeutics[J]. NUCLEIC ACID THERAPEUTICS, 2018, 28 (02) : 74 - 85Farelli, Jeremiah D.论文数: 0 引用数: 0 h-index: 0机构: Alex Pharmaceut Inc, Discovery Res, 75 Sidney St,4th Floor, Cambridge, MA 02139 USA Alex Pharmaceut Inc, Discovery Res, 75 Sidney St,4th Floor, Cambridge, MA 02139 USAAsrani, Kirtika H.论文数: 0 引用数: 0 h-index: 0机构: Alex Pharmaceut Inc, Discovery Res, 75 Sidney St,4th Floor, Cambridge, MA 02139 USA Alex Pharmaceut Inc, Discovery Res, 75 Sidney St,4th Floor, Cambridge, MA 02139 USAIsaacs, Cleo论文数: 0 引用数: 0 h-index: 0机构: Alex Pharmaceut Inc, Discovery Res, 75 Sidney St,4th Floor, Cambridge, MA 02139 USA Alex Pharmaceut Inc, Discovery Res, 75 Sidney St,4th Floor, Cambridge, MA 02139 USAdeBear, Joanna S.论文数: 0 引用数: 0 h-index: 0机构: Alex Pharmaceut Inc, Nucle Acid Technol, New Haven, CT USA Alex Pharmaceut Inc, Discovery Res, 75 Sidney St,4th Floor, Cambridge, MA 02139 USAStahley, Mary R.论文数: 0 引用数: 0 h-index: 0机构: Alex Pharmaceut Inc, Nucle Acid Technol, New Haven, CT USA Alex Pharmaceut Inc, Discovery Res, 75 Sidney St,4th Floor, Cambridge, MA 02139 USAShah, Anumeha论文数: 0 引用数: 0 h-index: 0机构: Alex Pharmaceut Inc, Preclin Pharmacol, New Haven, CT USA Alex Pharmaceut Inc, Discovery Res, 75 Sidney St,4th Floor, Cambridge, MA 02139 USALasaro, Melissa A.论文数: 0 引用数: 0 h-index: 0机构: Alex Pharmaceut Inc, Preclin Pharmacol, New Haven, CT USA Alex Pharmaceut Inc, Discovery Res, 75 Sidney St,4th Floor, Cambridge, MA 02139 USACheng, Christopher J.论文数: 0 引用数: 0 h-index: 0机构: Alex Pharmaceut Inc, Nucle Acid Technol, New Haven, CT USA Alex Pharmaceut Inc, Discovery Res, 75 Sidney St,4th Floor, Cambridge, MA 02139 USASubramanian, Romesh R.论文数: 0 引用数: 0 h-index: 0机构: Alex Pharmaceut Inc, Discovery Res, 75 Sidney St,4th Floor, Cambridge, MA 02139 USA Alex Pharmaceut Inc, Discovery Res, 75 Sidney St,4th Floor, Cambridge, MA 02139 USA