Gene therapies, uncertainty, and decision-making: thinking about the last mile at the first step

被引：2
作者：
Frederix, Gerardus W. J. [1 ]
Ham, Renske M. T. ten [1 ]
机构：
[1] Univ Med Ctr Utrecht, Julius Ctr Hlth Sci & Primary Care, Dept Epidemiol & Hlth Econ, Utrecht, Netherlands
来源：
EXPERT REVIEW OF PHARMACOECONOMICS & OUTCOMES RESEARCH | 2023年 / 23卷 / 08期
关键词：
gene therapy; economics; decision making; uncertainty; drug development; HEALTH TECHNOLOGIES; CHALLENGES;
D O I：
10.1080/14737167.2023.2245138
中图分类号：
R19 [保健组织与事业（卫生事业管理）];
学科分类号：
摘要：
引用
收藏
页码：853 / 856
页数：4
相关论文
共 35 条
  • [1] Amanda Whittal EI., 2022, EXPLORING EC GENE TH, P18
  • [2] Recalibrating Health Technology Assessment Methods for Cell and Gene Therapies
    Angelis, Aris
    Naci, Huseyin
    Hackshaw, Allan
    [J]. PHARMACOECONOMICS, 2020, 38 (12) : 1297 - 1308
  • [3] AMCP Partnership Forum: Designing Benefits and Payment Models for Innovative High-Investment Medications
    Barlow, Jane
    Bens, Cynthia
    Brent, Tim
    Ciarametaro, Michael
    Conway, Collin
    Redell, Jeremy F.
    George, Stephen
    Harman, Matthew
    Henry, Barbara
    Hoffman, Dorothy
    Jauch, Scott
    Jeffrey, Paul
    Keith, Pamela
    Koontz, Laura
    Long, Genia
    Majethia, Sunil
    Martin, Bill
    Martin, Seth
    Miner, Paul
    Moncuso, Donna
    Myers, Jeff
    Powers, Annette
    Reitz, Shirley
    Rogers, William
    Shaul, Bonnie
    Skiermont, Kyle
    Spangler, Jason
    Stojanovska, Ana
    Tharp, Louis
    Trieu, Susan
    Turpin, Robin
    Vandigo, Joe
    Whittington, Melanie
    [J]. JOURNAL OF MANAGED CARE & SPECIALTY PHARMACY, 2019, 25 (02) : 156 - 162
  • [4] Gene therapies: the challenge of super-high-cost treatments and how to pay for them
    Carr, David R.
    Bradshaw, Steven E.
    [J]. REGENERATIVE MEDICINE, 2016, 11 (04) : 381 - 393
  • [5] CfMPfHUC, 2018, GUID SAF EFF FOLL UP
  • [6] A Comprehensive Algorithm for Approval of Health Technologies With, Without, or Only in Research: The Key Principles for Informing Coverage Decisions
    Claxton, Karl
    Palmer, Stephen
    Longworth, Louise
    Bojke, Laura
    Griffin, Susan
    Soares, Marta
    Spackman, Eldon
    Rothery, Claire
    [J]. VALUE IN HEALTH, 2016, 19 (06) : 885 - 891
  • [7] Assessing the potential cost-effectiveness of a gene therapy for the treatment of hemophilia A
    Cook, Keziah
    Forbes, Shaun P.
    Adamski, Kelly
    Ma, Janice J.
    Chawla, Anita
    Garrison, Louis P., Jr.
    [J]. JOURNAL OF MEDICAL ECONOMICS, 2020, 23 (05) : 501 - 512
  • [8] Analytic Considerations in Applying a General Economic Evaluation Reference Case to Gene Therapy
    Drummond, Michael F.
    Neumann, Peter J.
    Sullivan, Sean D.
    Fricke, Frank-Ulrich
    Tunis, Sean
    Dabbous, Omar
    Toumi, Mondher
    [J]. VALUE IN HEALTH, 2019, 22 (06) : 661 - 668
  • [9] Eder Claudia, 2019, J Mark Access Health Policy, V7, P1600939, DOI 10.1080/20016689.2019.1600939
  • [10] Sharing Risk between Payer and Provider by Leasing Health Technologies: An Affordable and Effective Reimbursement Strategy for Innovative Technologies?
    Edlin, Richard
    Hall, Peter
    Wallner, Klemens
    McCabe, Christopher
    [J]. VALUE IN HEALTH, 2014, 17 (04) : 438 - 444
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